An
Angelman Syndrome (AS)
artificial transcription factor (ATF)
cell-based delivery
mesenchymal stem/stromal cell
zinc finger
Journal
Frontiers in molecular neuroscience
ISSN: 1662-5099
Titre abrégé: Front Mol Neurosci
Pays: Switzerland
ID NLM: 101477914
Informations de publication
Date de publication:
2021
2021
Historique:
received:
05
10
2021
accepted:
01
12
2021
entrez:
14
2
2022
pubmed:
15
2
2022
medline:
15
2
2022
Statut:
epublish
Résumé
Zinc finger (ZF), transcription activator-like effectors (TALE), and CRISPR/Cas9 therapies to regulate gene expression are becoming viable strategies to treat genetic disorders, although effective
Identifiants
pubmed: 35153670
doi: 10.3389/fnmol.2021.789913
pmc: PMC8829036
doi:
Types de publication
Journal Article
Langues
eng
Pagination
789913Subventions
Organisme : NCATS NIH HHS
ID : KL2 TR001859
Pays : United States
Organisme : NIMH NIH HHS
ID : T32 MH112507
Pays : United States
Organisme : NCATS NIH HHS
ID : TL1 TR001861
Pays : United States
Organisme : NCATS NIH HHS
ID : UL1 TR001860
Pays : United States
Informations de copyright
Copyright © 2022 Deng, Halmai, Beitnere, Cameron, Martinez, Lee, Waldo, Thongphanh, Adhikari, Copping, Petkova, Lee, Lock, Palomares, O’Geen, Carter, Gonzalez, Buchanan, Anderson, Fierro, Nolta, Tarantal, Silverman, Segal and Fink.
Déclaration de conflit d'intérêts
The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.
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