Novel


Journal

Neurology. Genetics
ISSN: 2376-7839
Titre abrégé: Neurol Genet
Pays: United States
ID NLM: 101671068

Informations de publication

Date de publication:
Apr 2022
Historique:
received: 13 10 2021
accepted: 24 01 2022
entrez: 7 3 2022
pubmed: 8 3 2022
medline: 8 3 2022
Statut: epublish

Résumé

To report a novel association between pathogenic variants in the Clinical exome sequencing was performed in an adult patient with a genetically unsolved neurodegenerative disorder. The main clinical, neuroimaging, and genetic data were described. The c.865C > T (p.P289S) and c.1297T > C (p.Y433H) missense variants in This case represents a novel form of early-onset pyramidal syndrome with optic nerve hypoplasia, which slowly evolved to extrapyramidal syndrome featuring dystonia-parkinsonism, associated with TCC, caused by

Identifiants

pubmed: 35252561
doi: 10.1212/NXG.0000000000000661
pii: NG2021017244
pmc: PMC8893591
doi:

Types de publication

Journal Article

Langues

eng

Pagination

e661

Informations de copyright

Copyright © 2022 The Author(s). Published by Wolters Kluwer Health, Inc. on behalf of the American Academy of Neurology.

Références

Eur J Paediatr Neurol. 2016 May;20(3):483-8
pubmed: 26805434
J Hum Genet. 2016 Jun;61(6):527-31
pubmed: 26888482
Neurology. 2015 Jul 28;85(4):306-15
pubmed: 26115735
J Inherit Metab Dis. 2018 Sep;41(5):897-898
pubmed: 29464431
Am J Hum Genet. 2010 Oct 8;87(4):538-44
pubmed: 20920667
Antioxid Redox Signal. 2020 Sep 1;33(7):481-497
pubmed: 32295391
Parkinsonism Relat Disord. 2017 Jun;39:4-16
pubmed: 28256436
Genet Med. 2015 May;17(5):405-24
pubmed: 25741868

Auteurs

Francesco Nicita (F)

Genetics and Rare Diseases Research Division (N.D.F., L.T., M.T., E.B., A.D.A.), Unit of Neuromuscular and Neurodegenerative Disorders, Department of Neurosciences, Bambino Gesù Children's Hospital, IRCCS; Studio Neurologico Laterano (F.B.); and Neurophysiology Unit (S.P.), Department of Neuroscience, Bambino Gesù Children's Hospital, IRCCS, Rome, Italy.

Lorena Travaglini (L)

Genetics and Rare Diseases Research Division (N.D.F., L.T., M.T., E.B., A.D.A.), Unit of Neuromuscular and Neurodegenerative Disorders, Department of Neurosciences, Bambino Gesù Children's Hospital, IRCCS; Studio Neurologico Laterano (F.B.); and Neurophysiology Unit (S.P.), Department of Neuroscience, Bambino Gesù Children's Hospital, IRCCS, Rome, Italy.

Francesco Bombelli (F)

Genetics and Rare Diseases Research Division (N.D.F., L.T., M.T., E.B., A.D.A.), Unit of Neuromuscular and Neurodegenerative Disorders, Department of Neurosciences, Bambino Gesù Children's Hospital, IRCCS; Studio Neurologico Laterano (F.B.); and Neurophysiology Unit (S.P.), Department of Neuroscience, Bambino Gesù Children's Hospital, IRCCS, Rome, Italy.

Michele Tosi (M)

Genetics and Rare Diseases Research Division (N.D.F., L.T., M.T., E.B., A.D.A.), Unit of Neuromuscular and Neurodegenerative Disorders, Department of Neurosciences, Bambino Gesù Children's Hospital, IRCCS; Studio Neurologico Laterano (F.B.); and Neurophysiology Unit (S.P.), Department of Neuroscience, Bambino Gesù Children's Hospital, IRCCS, Rome, Italy.

Stefano Pro (S)

Genetics and Rare Diseases Research Division (N.D.F., L.T., M.T., E.B., A.D.A.), Unit of Neuromuscular and Neurodegenerative Disorders, Department of Neurosciences, Bambino Gesù Children's Hospital, IRCCS; Studio Neurologico Laterano (F.B.); and Neurophysiology Unit (S.P.), Department of Neuroscience, Bambino Gesù Children's Hospital, IRCCS, Rome, Italy.

Enrico Bertini (E)

Genetics and Rare Diseases Research Division (N.D.F., L.T., M.T., E.B., A.D.A.), Unit of Neuromuscular and Neurodegenerative Disorders, Department of Neurosciences, Bambino Gesù Children's Hospital, IRCCS; Studio Neurologico Laterano (F.B.); and Neurophysiology Unit (S.P.), Department of Neuroscience, Bambino Gesù Children's Hospital, IRCCS, Rome, Italy.

Adele D'Amico (A)

Genetics and Rare Diseases Research Division (N.D.F., L.T., M.T., E.B., A.D.A.), Unit of Neuromuscular and Neurodegenerative Disorders, Department of Neurosciences, Bambino Gesù Children's Hospital, IRCCS; Studio Neurologico Laterano (F.B.); and Neurophysiology Unit (S.P.), Department of Neuroscience, Bambino Gesù Children's Hospital, IRCCS, Rome, Italy.

Classifications MeSH