Assessment of mitochondrial toxicity in newborns and infants with congenital cytomegalovirus infection treated with valganciclovir.


Journal

Archives of disease in childhood
ISSN: 1468-2044
Titre abrégé: Arch Dis Child
Pays: England
ID NLM: 0372434

Informations de publication

Date de publication:
07 2022
Historique:
received: 20 09 2021
accepted: 17 02 2022
pubmed: 16 3 2022
medline: 22 6 2022
entrez: 15 3 2022
Statut: ppublish

Résumé

Ganciclovir/valganciclovir is currently indicated during the first 6 months of life in symptomatic children with congenital cytomegalovirus (CMV) infection. However, this treatment may have the potential to induce mitochondrial toxicity due to off-target inhibition of DNA-polymerases. Similar anti-HIV drugs have been associated with mitochondrial toxicity but this has never been explored in CMV. To determine the potential mitochondrial toxicity profile at the genetic, functional and biogenesis level in peripheral blood mononuclear cells from a cohort of newborns and infants with symptomatic congenital CMV infection (treated with valganciclovir, untreated and uninfected controls). Longitudinal, observational and controlled study. Subjects were recruited at the tertiary referral Hospital Sant Joan de Déu and experiments were conducted at IDIBAPS-Hospital Clínic of Barcelona, Spain. CMV-infected newborns underwent comprehensive monthly clinical follow-up. Mitochondrial parameters, audiometry and neurological assessment were measured at baseline, 3-6 and 12 months after inclusion in the study. The Kruskal-Wallis test for k-independent samples and Friedman tests for repeated measurements were applied. Complex IV, citrate synthase enzymatic activities and mtDNA remained preserved in congenital CMV-infected infants treated with valganciclovir compared with controls (p>0.05 in all cases). No evidence of mitochondrial toxicity was found in infants treated with valganciclovir for congenital CMV.

Sections du résumé

BACKGROUND
Ganciclovir/valganciclovir is currently indicated during the first 6 months of life in symptomatic children with congenital cytomegalovirus (CMV) infection. However, this treatment may have the potential to induce mitochondrial toxicity due to off-target inhibition of DNA-polymerases. Similar anti-HIV drugs have been associated with mitochondrial toxicity but this has never been explored in CMV.
OBJECTIVE
To determine the potential mitochondrial toxicity profile at the genetic, functional and biogenesis level in peripheral blood mononuclear cells from a cohort of newborns and infants with symptomatic congenital CMV infection (treated with valganciclovir, untreated and uninfected controls).
DESIGN
Longitudinal, observational and controlled study.
SETTING AND PATIENTS
Subjects were recruited at the tertiary referral Hospital Sant Joan de Déu and experiments were conducted at IDIBAPS-Hospital Clínic of Barcelona, Spain. CMV-infected newborns underwent comprehensive monthly clinical follow-up.
METHODS
Mitochondrial parameters, audiometry and neurological assessment were measured at baseline, 3-6 and 12 months after inclusion in the study. The Kruskal-Wallis test for k-independent samples and Friedman tests for repeated measurements were applied.
RESULTS
Complex IV, citrate synthase enzymatic activities and mtDNA remained preserved in congenital CMV-infected infants treated with valganciclovir compared with controls (p>0.05 in all cases).
CONCLUSIONS
No evidence of mitochondrial toxicity was found in infants treated with valganciclovir for congenital CMV.

Identifiants

pubmed: 35288419
pii: archdischild-2021-322996
doi: 10.1136/archdischild-2021-322996
pmc: PMC9209682
doi:

Substances chimiques

Anti-HIV Agents 0
Antiviral Agents 0
Valganciclovir GCU97FKN3R
Ganciclovir P9G3CKZ4P5

Types de publication

Controlled Clinical Trial Journal Article Observational Study Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

686-691

Informations de copyright

© Author(s) (or their employer(s)) 2022. Re-use permitted under CC BY-NC. No commercial re-use. See rights and permissions. Published by BMJ.

Déclaration de conflit d'intérêts

Competing interests: None declared.

Références

AIDS Res Hum Retroviruses. 2010 Sep;26(9):1015-8
pubmed: 20707732
J Acquir Immune Defic Syndr. 2012 Jun 1;60(2):111-6
pubmed: 22362155
Lab Delo. 1990;(2):20-3
pubmed: 1692359
J Antimicrob Chemother. 2015 Aug;70(8):2330-6
pubmed: 25921514
Pediatr Infect Dis J. 2016 Aug;35(8):924-6
pubmed: 27195603
Clin Infect Dis. 2013 Dec;57 Suppl 4:S178-81
pubmed: 24257422
J Clin Virol. 2012 Sep;55(1):72-4
pubmed: 22750017
Pediatr Infect Dis J. 2003 Sep;22(9):778-82
pubmed: 14506367
Ital J Pediatr. 2017 Apr 17;43(1):38
pubmed: 28416012
J Cell Mol Med. 2017 Feb;21(2):402-409
pubmed: 27758070
Front Genet. 2020 May 26;11:497
pubmed: 32528527
Rev Med Virol. 2014 Nov;24(6):420-33
pubmed: 25316174
Pediatr Infect Dis J. 2015 Dec;34(12):1349-54
pubmed: 26372453
N Engl J Med. 2015 Mar 5;372(10):933-43
pubmed: 25738669
Expert Rev Anti Infect Ther. 2016;14(5):479-88
pubmed: 27043943
Lancet Infect Dis. 2017 Jun;17(6):e177-e188
pubmed: 28291720
Int J Infect Dis. 2014 May;22:44-8
pubmed: 24631522
An Pediatr (Barc). 2009 Dec;71(6):535-47
pubmed: 19815469
Drug Chem Toxicol. 2013 Oct;36(4):496-500
pubmed: 23534415
AIDS. 2015 Jan 2;29(1):5-12
pubmed: 25268887
J Pediatr. 2003 Jul;143(1):16-25
pubmed: 12915819
Rev Med Virol. 2021 Nov;31(6):e2232
pubmed: 33792105
Pediatr Infect Dis J. 2017 Dec;36(12):1205-1213
pubmed: 29140947

Auteurs

Alba Ortiz-Gracia (A)

Pompeu Fabra University, Barcelona, Spain.
Universitat Autònoma de Barcelona, Barcelona, Spain.

María Ríos (M)

Malalties Infeccioses i Resposta Inflamatòria Sistèmica en Pediatria, Unitat d'Infeccions, Servei de Pediatria, Institut de Recerca Sant Joan de Déu, Barcelona, Spain.

Ester Tobías (E)

Faculty of Medicine and Health Sciences, University of Barcelona, Barcelona, Spain.
Cellex, Institut d'Investigacions Biomèdiques August Pi i Sunyer, IDIBAPS, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Enfermedades Raras, CIBERER, Madrid, Spain.
Internal Medicine Department, Hospital Clínic of Barcelona HCB, Barcelona, Spain.

Antoni Noguera-Julian (A)

Malalties Infeccioses i Resposta Inflamatòria Sistèmica en Pediatria, Unitat d'Infeccions, Servei de Pediatria, Institut de Recerca Sant Joan de Déu, Barcelona, Spain.
Faculty of Medicine and Health Sciences, University of Barcelona, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Epidemiología y Salud Pública, CIBERESP, Madrid, Spain.
Red de Investigación Translacional en Infectología Pediátrica RITIP, Madrid, Spain.

Francesc Josep García-García (FJ)

Faculty of Medicine and Health Sciences, University of Barcelona, Barcelona, Spain.
Cellex, Institut d'Investigacions Biomèdiques August Pi i Sunyer, IDIBAPS, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Enfermedades Raras, CIBERER, Madrid, Spain.
Internal Medicine Department, Hospital Clínic of Barcelona HCB, Barcelona, Spain.

Judith Cantó-Santos (J)

Faculty of Medicine and Health Sciences, University of Barcelona, Barcelona, Spain.
Cellex, Institut d'Investigacions Biomèdiques August Pi i Sunyer, IDIBAPS, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Enfermedades Raras, CIBERER, Madrid, Spain.
Internal Medicine Department, Hospital Clínic of Barcelona HCB, Barcelona, Spain.

Laura Valls-Roca (L)

Faculty of Medicine and Health Sciences, University of Barcelona, Barcelona, Spain.
Cellex, Institut d'Investigacions Biomèdiques August Pi i Sunyer, IDIBAPS, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Enfermedades Raras, CIBERER, Madrid, Spain.
Internal Medicine Department, Hospital Clínic of Barcelona HCB, Barcelona, Spain.

Glòria Garrabou (G)

Faculty of Medicine and Health Sciences, University of Barcelona, Barcelona, Spain.
Cellex, Institut d'Investigacions Biomèdiques August Pi i Sunyer, IDIBAPS, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Enfermedades Raras, CIBERER, Madrid, Spain.
Internal Medicine Department, Hospital Clínic of Barcelona HCB, Barcelona, Spain.

Josep Maria Grau (JM)

Faculty of Medicine and Health Sciences, University of Barcelona, Barcelona, Spain.
Cellex, Institut d'Investigacions Biomèdiques August Pi i Sunyer, IDIBAPS, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Enfermedades Raras, CIBERER, Madrid, Spain.
Internal Medicine Department, Hospital Clínic of Barcelona HCB, Barcelona, Spain.

Francesc Cardellach (F)

Faculty of Medicine and Health Sciences, University of Barcelona, Barcelona, Spain.
Cellex, Institut d'Investigacions Biomèdiques August Pi i Sunyer, IDIBAPS, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Enfermedades Raras, CIBERER, Madrid, Spain.
Internal Medicine Department, Hospital Clínic of Barcelona HCB, Barcelona, Spain.

Emilia Sánchez (E)

Blanquerna School of Health Science, Ramon Llull University, Barcelona, Spain.

Constanza Morén (C)

Faculty of Medicine and Health Sciences, University of Barcelona, Barcelona, Spain cmoren1@clinic.cat.
Cellex, Institut d'Investigacions Biomèdiques August Pi i Sunyer, IDIBAPS, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Enfermedades Raras, CIBERER, Madrid, Spain.
Internal Medicine Department, Hospital Clínic of Barcelona HCB, Barcelona, Spain.

Clàudia Fortuny (C)

Malalties Infeccioses i Resposta Inflamatòria Sistèmica en Pediatria, Unitat d'Infeccions, Servei de Pediatria, Institut de Recerca Sant Joan de Déu, Barcelona, Spain.
Faculty of Medicine and Health Sciences, University of Barcelona, Barcelona, Spain.
Centro de Investigación Biomédica en Red de Epidemiología y Salud Pública, CIBERESP, Madrid, Spain.
Red de Investigación Translacional en Infectología Pediátrica RITIP, Madrid, Spain.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH