A Chemical Strategy toward Novel Brain-Penetrant EZH2 Inhibitors.


Journal

ACS medicinal chemistry letters
ISSN: 1948-5875
Titre abrégé: ACS Med Chem Lett
Pays: United States
ID NLM: 101521073

Informations de publication

Date de publication:
10 Mar 2022
Historique:
received: 18 08 2021
accepted: 24 01 2022
entrez: 18 3 2022
pubmed: 19 3 2022
medline: 19 3 2022
Statut: epublish

Résumé

Aberrant gene-silencing through dysregulation of polycomb protein activity has emerged as an important oncogenic mechanism in cancer, implicating polycomb proteins as important therapeutic targets. Recently, an inhibitor targeting EZH2, the methyltransferase component of PRC2, received U.S. Food and Drug Administration approval following promising clinical responses in cancer patients. However, the current array of EZH2 inhibitors have poor brain penetrance, limiting their use in patients with central nervous system malignancies, a number of which have been shown to be sensitive to EZH2 inhibition. To address this need, we have identified a chemical strategy, based on computational modeling of pyridone-containing EZH2 inhibitor scaffolds, to minimize P-glycoprotein activity, and here we report the first brain-penetrant EZH2 inhibitor, TDI-6118 (compound

Identifiants

pubmed: 35300079
doi: 10.1021/acsmedchemlett.1c00448
pmc: PMC8919293
doi:

Types de publication

Journal Article

Langues

eng

Pagination

377-387

Subventions

Organisme : NCI NIH HHS
ID : P30 CA008748
Pays : United States

Informations de copyright

© 2022 American Chemical Society.

Déclaration de conflit d'intérêts

The authors declare no competing financial interest.

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Auteurs

Rui Liang (R)

Tri-Institutional Therapeutics Discovery Institute, 413 East 69th Street, New York, New York 10021, United States.

Daisuke Tomita (D)

Tri-Institutional Therapeutics Discovery Institute, 413 East 69th Street, New York, New York 10021, United States.

Yusuke Sasaki (Y)

Tri-Institutional Therapeutics Discovery Institute, 413 East 69th Street, New York, New York 10021, United States.

John Ginn (J)

Tri-Institutional Therapeutics Discovery Institute, 413 East 69th Street, New York, New York 10021, United States.

Mayako Michino (M)

Tri-Institutional Therapeutics Discovery Institute, 413 East 69th Street, New York, New York 10021, United States.

David J Huggins (DJ)

Tri-Institutional Therapeutics Discovery Institute, 413 East 69th Street, New York, New York 10021, United States.
Department of Physiology and Biophysics, Weill Cornell Medical College, New York, New York 10021, United States.

Leigh Baxt (L)

Tri-Institutional Therapeutics Discovery Institute, 413 East 69th Street, New York, New York 10021, United States.

Stacia Kargman (S)

Tri-Institutional Therapeutics Discovery Institute, 413 East 69th Street, New York, New York 10021, United States.

Maaz Shahid (M)

Department of Neurology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, Pennsylvania 19104, United States.
Epigenetics Program, Perelman School of Medicine, Philadelphia, Pennsylvania 19104, United States.
Abramson Cancer Center, Perelman School of Medicine, Philadelphia, Pennsylvania 19104, United States.

Kazuyoshi Aso (K)

Tri-Institutional Therapeutics Discovery Institute, 413 East 69th Street, New York, New York 10021, United States.

Mark Duggan (M)

LifeSci Consulting, LLC., 18243 SE Ridgeview Drive, Tequesta, Florida 33469, United States.

Andrew W Stamford (AW)

Tri-Institutional Therapeutics Discovery Institute, 413 East 69th Street, New York, New York 10021, United States.

Elisa DeStanchina (E)

Molecular Pharmacology Program, Memorial Sloan Kettering Cancer Center, New York, New York 10065, United States.

Nigel Liverton (N)

Tri-Institutional Therapeutics Discovery Institute, 413 East 69th Street, New York, New York 10021, United States.

Peter T Meinke (PT)

Tri-Institutional Therapeutics Discovery Institute, 413 East 69th Street, New York, New York 10021, United States.
Department of Pharmacology, Weill Cornell Medical College, New York, New York 10021, United States.

Michael A Foley (MA)

Tri-Institutional Therapeutics Discovery Institute, 413 East 69th Street, New York, New York 10021, United States.

Richard E Phillips (RE)

Department of Neurology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, Pennsylvania 19104, United States.
Epigenetics Program, Perelman School of Medicine, Philadelphia, Pennsylvania 19104, United States.
Abramson Cancer Center, Perelman School of Medicine, Philadelphia, Pennsylvania 19104, United States.

Classifications MeSH