Complement inhibitor eculizumab in thrombotic microangiopathy: Single-center case series.

atypical hemolytic uremic syndrome complement eculizumab nephrology thrombotic microangiopathy

Journal

Clinical case reports
ISSN: 2050-0904
Titre abrégé: Clin Case Rep
Pays: England
ID NLM: 101620385

Informations de publication

Date de publication:
Mar 2022
Historique:
received: 24 09 2021
revised: 16 01 2022
accepted: 16 02 2022
entrez: 23 3 2022
pubmed: 24 3 2022
medline: 24 3 2022
Statut: epublish

Résumé

Our case series showed that eculizumab is efficacious and safe in treating thrombotic microangiopathy, as well as it has positive effects on quality of life. Further extensive studies are required to develop unified treatment guidelines.

Identifiants

pubmed: 35317070
doi: 10.1002/ccr3.5573
pii: CCR35573
pmc: PMC8922540
doi:

Types de publication

Case Reports

Langues

eng

Pagination

e05573

Informations de copyright

© 2022 The Authors. Clinical Case Reports published by John Wiley & Sons Ltd.

Déclaration de conflit d'intérêts

None.

Références

Pediatr Nephrol. 2014 Mar;29(3):333-42
pubmed: 23475077
Clin J Am Soc Nephrol. 2013 Apr;8(4):554-62
pubmed: 23307876
Front Immunol. 2021 Nov 10;12:780107
pubmed: 34858436
Pediatr Nephrol. 1998 Feb;12(2):101-4
pubmed: 9543364
Pediatr Nephrol. 2019 May;34(5):943-949
pubmed: 30693384
Pediatr Nephrol. 2011 Jan;26(1):41-57
pubmed: 20556434
Am J Kidney Dis. 2014 Oct;64(4):633-7
pubmed: 24656451
Blood. 2006 Aug 15;108(4):1267-79
pubmed: 16621965
Neuromolecular Med. 2010 Jun;12(2):179-92
pubmed: 19763906
Blood. 2015 Jan 22;125(4):616-8
pubmed: 25414441
Pediatr Nephrol. 2008 Oct;23(10):1761-7
pubmed: 17906963
Semin Thromb Hemost. 2010 Sep;36(6):673-81
pubmed: 20865645
J Immunol Methods. 2018 Oct;461:15-22
pubmed: 30031798
Pediatr Nephrol. 2011 Aug;26(8):1325-9
pubmed: 21556717
Lancet. 2017 Aug 12;390(10095):681-696
pubmed: 28242109
Clin J Am Soc Nephrol. 2017 Jan 6;12(1):50-59
pubmed: 27799617
Orphanet J Rare Dis. 2011 Sep 08;6:60
pubmed: 21902819
Medicine (Baltimore). 2016 May;95(18):e3595
pubmed: 27149490
J Nephrol. 2022 Mar;35(2):451-461
pubmed: 33599971
Clin Kidney J. 2020 Jun 22;14(4):1126-1135
pubmed: 33841858
Ther Apher Dial. 2019 Feb;23(1):4-21
pubmed: 30294946
Semin Arthritis Rheum. 2019 Aug;49(1):74-83
pubmed: 30598332
Nephrol Dial Transplant. 2014 Sep;29 Suppl 4:iv1-8
pubmed: 25165174
Nefrologia. 2015;35(5):421-47
pubmed: 26456110
Ren Fail. 2010 Jul;32(6):753-6
pubmed: 20540647
Am J Pathol. 2009 Mar;174(3):797-807
pubmed: 19164508
N Engl J Med. 1991 Aug 8;325(6):398-403
pubmed: 2062331
Eur J Immunol. 1999 Mar;29(3):815-22
pubmed: 10092084
Nat Rev Nephrol. 2012 Nov;8(11):643-57
pubmed: 23026949
Pediatr Nephrol. 2013 May;28(5):827-30
pubmed: 23389237
Clin J Am Soc Nephrol. 2010 Oct;5(10):1844-59
pubmed: 20595690
Kidney Int Rep. 2019 Aug 02;4(11):1568-1576
pubmed: 31890998
Semin Nephrol. 2013 Nov;33(6):508-30
pubmed: 24161037
Pediatr Nephrol. 2019 Aug;34(8):1337-1348
pubmed: 30109445
Clin Exp Nephrol. 2010 Oct;14(5):487-91
pubmed: 20535626
N Engl J Med. 2006 Sep 21;355(12):1233-43
pubmed: 16990386
J Am Soc Nephrol. 2004 Feb;15(2):241-50
pubmed: 14747370
Kidney Int. 2015 May;87(5):1061-73
pubmed: 25651368
N Engl J Med. 2001 Apr 5;344(14):1058-66
pubmed: 11287977
Medicine (Baltimore). 2016 Aug;95(31):e4330
pubmed: 27495036
Clin Pharmacokinet. 2019 Jul;58(7):859-874
pubmed: 30758736
BMJ Open. 2013 Nov 04;3(11):e003573
pubmed: 24189082
Arthritis Rheum. 1997 Sep;40(9):1725
pubmed: 9324032
Nat Biotechnol. 2007 Nov;25(11):1256-64
pubmed: 17989688
Am J Kidney Dis. 2013 Sep;62(3):403-41
pubmed: 23871408
Intern Med. 2017 Nov 1;56(21):2937-2941
pubmed: 28943538
Clin Epidemiol. 2020 Mar 12;12:295-305
pubmed: 32210633
Korean J Pediatr. 2018 Feb;61(2):37-42
pubmed: 29563942
Arch Intern Med. 1984 May;144(5):1074-6
pubmed: 6712399
N Engl J Med. 2009 Oct 22;361(17):1676-87
pubmed: 19846853
MMWR Morb Mortal Wkly Rep. 2017 Jul 14;66(27):734-737
pubmed: 28704351
Pediatr Nephrol. 2008 Nov;23(11):1957-72
pubmed: 18594873
Kidney Int Rep. 2018 Dec 03;4(3):434-446
pubmed: 30899871
Cochrane Database Syst Rev. 2009 Jan 21;(1):CD003595
pubmed: 19160220
J Pediatr. 2007 Aug;151(2):140-4
pubmed: 17643764
BMC Nephrol. 2019 Apr 10;20(1):125
pubmed: 30971227
F1000Prime Rep. 2014 Dec 01;6:119
pubmed: 25580273
Semin Hematol. 2018 Jul;55(3):150-158
pubmed: 30032752
Am J Transplant. 2013 Mar;13(3):663-75
pubmed: 23356914
N Engl J Med. 2013 Jun 6;368(23):2169-81
pubmed: 23738544
Pediatr Nephrol. 2016 Jan;31(1):15-39
pubmed: 25859752
Mol Immunol. 2015 Sep;67(1):31-42
pubmed: 25843230

Auteurs

Monika Vitkauskaitė (M)

Faculty of Medicine Vilnius University Vilnius Lithuania.

Artūras Vinikovas (A)

Faculty of Medicine Vilnius University Vilnius Lithuania.
Clinic of Gastroenterology, Nephro-Urology and Surgery Faculty of Medicine Institute of Clinical Medicine Vilnius University Vilnius Lithuania.

Marius Miglinas (M)

Faculty of Medicine Vilnius University Vilnius Lithuania.
Clinic of Gastroenterology, Nephro-Urology and Surgery Faculty of Medicine Institute of Clinical Medicine Vilnius University Vilnius Lithuania.

Laurynas Rimševičius (L)

Faculty of Medicine Vilnius University Vilnius Lithuania.
Clinic of Gastroenterology, Nephro-Urology and Surgery Faculty of Medicine Institute of Clinical Medicine Vilnius University Vilnius Lithuania.

Agnė Čerkauskaitė (A)

Faculty of Medicine Vilnius University Vilnius Lithuania.
Clinic of Gastroenterology, Nephro-Urology and Surgery Faculty of Medicine Institute of Clinical Medicine Vilnius University Vilnius Lithuania.

Ernesta Mačionienė (E)

Faculty of Medicine Vilnius University Vilnius Lithuania.
Clinic of Gastroenterology, Nephro-Urology and Surgery Faculty of Medicine Institute of Clinical Medicine Vilnius University Vilnius Lithuania.

Eglė Ašakienė (E)

Faculty of Medicine Vilnius University Vilnius Lithuania.
Clinic of Gastroenterology, Nephro-Urology and Surgery Faculty of Medicine Institute of Clinical Medicine Vilnius University Vilnius Lithuania.

Classifications MeSH