Targeted Gene Insertion for Functional CFTR Restoration in Airway Epithelium.
CFTR
basal cells
cystic fibrosis
gene editing
gene insertion
Journal
Frontiers in genome editing
ISSN: 2673-3439
Titre abrégé: Front Genome Ed
Pays: Switzerland
ID NLM: 101775540
Informations de publication
Date de publication:
2022
2022
Historique:
received:
03
01
2022
accepted:
21
02
2022
entrez:
25
3
2022
pubmed:
26
3
2022
medline:
26
3
2022
Statut:
epublish
Résumé
Cystic Fibrosis (CF) is caused by a diverse set of mutations distributed across the approximately 250 thousand base pairs of the
Identifiants
pubmed: 35330693
doi: 10.3389/fgeed.2022.847645
pii: 847645
pmc: PMC8940244
doi:
Types de publication
Journal Article
Langues
eng
Pagination
847645Subventions
Organisme : NIDDK NIH HHS
ID : P30 DK054759
Pays : United States
Informations de copyright
Copyright © 2022 Barillà, Suzuki, Rab, Sorscher and Davis.
Déclaration de conflit d'intérêts
The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.
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