A Phase II Trial of a Personalized, Dose-Intense Administration Schedule of

177Lu-DOTATATE PRRT high-risk neuroblastoma radiopharmaceutical refractory relapse therapy

Journal

Frontiers in pediatrics
ISSN: 2296-2360
Titre abrégé: Front Pediatr
Pays: Switzerland
ID NLM: 101615492

Informations de publication

Date de publication:
2022
Historique:
received: 15 12 2021
accepted: 31 01 2022
entrez: 1 4 2022
pubmed: 2 4 2022
medline: 2 4 2022
Statut: epublish

Résumé

Half the children with high-risk neuroblastoma die with widespread metastases. Molecular radiotherapy is an attractive systemic treatment for this relatively radiosensitive tumor. The LuDO-N trial is a phase II, open label, multi-center, single arm, two stage design clinical trial. Children aged 18 months to 18 years are eligible. The trial is conducted by the Nordic Society for Pediatric Hematology and Oncology (NOPHO) and it has been endorsed by SIOPEN (https://www.siopen.net). The Karolinska University Hospital, is the sponsor of the LuDO-N trial, which is conducted in collaboration with Advanced Accelerator Applications, a Novartis company. All Scandinavian countries, Lithuania and the Netherlands participate in the trial and the UK has voiced an interest in joining in 2022. The pediatric use of the Investigational Medicinal Product (IMP) In this paper we present the protocol of the LuDO-N Trial. The rationale and design of the trial are discussed in relation to other ongoing, or planned trials with similar objectives. Further, we discuss the rapid development of targeted radiopharmaceutical therapy and the future perspectives for developing novel therapies for high-risk neuroblastoma and other pediatric solid tumors.

Sections du résumé

Background UNASSIGNED
Half the children with high-risk neuroblastoma die with widespread metastases. Molecular radiotherapy is an attractive systemic treatment for this relatively radiosensitive tumor.
Methods UNASSIGNED
The LuDO-N trial is a phase II, open label, multi-center, single arm, two stage design clinical trial. Children aged 18 months to 18 years are eligible. The trial is conducted by the Nordic Society for Pediatric Hematology and Oncology (NOPHO) and it has been endorsed by SIOPEN (https://www.siopen.net). The Karolinska University Hospital, is the sponsor of the LuDO-N trial, which is conducted in collaboration with Advanced Accelerator Applications, a Novartis company. All Scandinavian countries, Lithuania and the Netherlands participate in the trial and the UK has voiced an interest in joining in 2022.
Results UNASSIGNED
The pediatric use of the Investigational Medicinal Product (IMP)
Discussion UNASSIGNED
In this paper we present the protocol of the LuDO-N Trial. The rationale and design of the trial are discussed in relation to other ongoing, or planned trials with similar objectives. Further, we discuss the rapid development of targeted radiopharmaceutical therapy and the future perspectives for developing novel therapies for high-risk neuroblastoma and other pediatric solid tumors.

Identifiants

pubmed: 35359899
doi: 10.3389/fped.2022.836230
pmc: PMC8960300
doi:

Banques de données

ClinicalTrials.gov
['NCT04903899']

Types de publication

Journal Article

Langues

eng

Pagination

836230

Informations de copyright

Copyright © 2022 Sundquist, Georgantzi, Jarvis, Brok, Koskenvuo, Rascon, van Noesel, Grybäck, Nilsson, Braat, Sundin, Wessman, Herold, Hjorth, Kogner, Granberg, Gaze and Stenman.

Déclaration de conflit d'intérêts

This study received funding from Applied Accelerator Applications, a Novartis company. The funder had the following involvement with the study: Advice on trial design, provision of all investigational and non-investigational products, free of charge for the LuDO-N trial and review of the final manuscript. The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.

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Auteurs

Fredrik Sundquist (F)

Department of Women's and Children's Health, Karolinska Institutet, Stockholm, Sweden.

Kleopatra Georgantzi (K)

Department of Women's and Children's Health, Karolinska Institutet, Stockholm, Sweden.
Pediatric Oncology, Astrid Lindgren Children's Hospital, Karolinska University Hospital, Stockholm, Sweden.

Kirsten Brunsvig Jarvis (KB)

Department of Paediatric Haematology and Oncology, Oslo University Hospital, Rikshospitalet, Oslo, Norway.

Jesper Brok (J)

Department of Paediatrics and Adolescent Medicine, Rigshospitalet, Copenhagen, Denmark.

Minna Koskenvuo (M)

Helsinki University Central Hospital, University of Helsinki, Helsinki, Finland.

Jelena Rascon (J)

Center for Pediatric Oncology and Hematology, Vilnius University Hospital Santaros Klinikos, Vilnius, Lithuania.

Max van Noesel (M)

Solid Tumor Department, Princess Máxima Center for Pediatric Oncology, Utrecht, Netherlands.

Per Grybäck (P)

Department of Medical Radiation Physics and Nuclear Medicine, Karolinska University Hospital, Stockholm, Sweden.

Joachim Nilsson (J)

Department of Medical Radiation Physics and Nuclear Medicine, Karolinska University Hospital, Stockholm, Sweden.

Arthur Braat (A)

Department of Nuclear Medicine, Princess Máxima Center for Pediatric Oncology, Utrecht, Netherlands.

Mikael Sundin (M)

Division of Pediatrics, Department of Pediatric Hematology, Immunology and HCT, Department of Clinical Science, Intervention and Technology (CLINTEC), Karolinska University Hospital, Karolinska Institutet, Stockholm, Sweden.

Sandra Wessman (S)

Department of Pathology, Department of Oncology-Pathology, Karolinska University Hospital, Karolinska Institutet, Stockholm, Sweden.

Nikolas Herold (N)

Department of Women's and Children's Health, Karolinska Institutet, Stockholm, Sweden.
Pediatric Oncology, Astrid Lindgren Children's Hospital, Karolinska University Hospital, Stockholm, Sweden.

Lars Hjorth (L)

Department of Clinical Sciences Lund, Paediatrics, Lund University, Skane University Hospital, Lund, Sweden.

Per Kogner (P)

Department of Women's and Children's Health, Karolinska Institutet, Stockholm, Sweden.

Dan Granberg (D)

Department of Breast, Endocrine Tumors and Sarcomas, Department of Molecular Medicine and Surgery, Karolinska University Hospital, Karolinska Institutet, Stockholm, Sweden.

Mark Gaze (M)

Department of Oncology, University College London Hospitals NHS Foundation Trust, London, United Kingdom.

Jakob Stenman (J)

Department of Women's and Children's Health, Karolinska Institutet, Stockholm, Sweden.
Department of Pediatric Surgery, Karolinska University Hospital, Stockholm, Sweden.

Classifications MeSH