Exploiting 4-1BB immune checkpoint to enhance the efficacy of oncolytic virotherapy for diffuse intrinsic pontine gliomas.


Journal

JCI insight
ISSN: 2379-3708
Titre abrégé: JCI Insight
Pays: United States
ID NLM: 101676073

Informations de publication

Date de publication:
08 04 2022
Historique:
received: 14 09 2021
accepted: 25 02 2022
entrez: 8 4 2022
pubmed: 9 4 2022
medline: 12 4 2022
Statut: epublish

Résumé

Diffuse intrinsic pontine gliomas (DIPGs) are aggressive pediatric brain tumors, and patient survival has not changed despite many therapeutic efforts, emphasizing the urgent need for effective treatments. Here, we evaluated the anti-DIPG effect of the oncolytic adenovirus Delta-24-ACT, which was engineered to express the costimulatory ligand 4-1BBL to potentiate the antitumor immune response of the virus. Delta-24-ACT induced the expression of functional 4-1BBL on the membranes of infected DIPG cells, which enhanced the costimulation of CD8+ T lymphocytes. In vivo, Delta-24-ACT treatment of murine DIPG orthotopic tumors significantly improved the survival of treated mice, leading to long-term survivors that developed immunological memory against these tumors. In addition, Delta-24-ACT was safe and caused no local or systemic toxicity. Mechanistic studies showed that Delta-24-ACT modulated the tumor-immune content, not only increasing the number, but also improving the functionality of immune cells. All of these data highlight the safety and potential therapeutic benefit of Delta-24-ACT the treatment of patients with DIPG.

Identifiants

pubmed: 35393952
pii: 154812
doi: 10.1172/jci.insight.154812
pmc: PMC9057625
doi:
pii:

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : NCI NIH HHS
ID : P30 CA016672
Pays : United States
Organisme : NCI NIH HHS
ID : P50 CA127001
Pays : United States

Références

Nat Med. 2007 Jan;13(1):54-61
pubmed: 17187072
J Exp Med. 2017 Feb;214(2):381-400
pubmed: 28115575
Bioinformatics. 2020 Feb 1;36(3):970-971
pubmed: 31504159
Nat Commun. 2019 May 28;10(1):2235
pubmed: 31138805
J Immunother Cancer. 2021 Jul;9(7):
pubmed: 34281988
Neuro Oncol. 2017 Sep 1;19(9):1279-1280
pubmed: 28821206
Clin Cancer Res. 2015 Jul 15;21(14):3113-20
pubmed: 25908780
Nature. 2017 Jan 18;541(7637):321-330
pubmed: 28102259
Nat Rev Immunol. 2018 Aug;18(8):498-513
pubmed: 29743717
Acta Neuropathol Commun. 2019 Apr 29;7(1):64
pubmed: 31036068
Neurosurgery. 2018 Nov 1;83(5):1050-1056
pubmed: 29088386
Cancers (Basel). 2019 May 13;11(5):
pubmed: 31086012
Oncogene. 2000 Jan 6;19(1):2-12
pubmed: 10644974
J Natl Cancer Inst. 2003 May 7;95(9):652-60
pubmed: 12734316
Front Oncol. 2015 Oct 21;5:237
pubmed: 26557503
OMICS. 2012 May;16(5):284-7
pubmed: 22455463
Cell Death Dis. 2020 Nov 26;11(11):1013
pubmed: 33243969
J Clin Oncol. 2018 Jul 1;36(19):1963-1972
pubmed: 29746225
Mol Ther Oncolytics. 2017 May 02;5:75-86
pubmed: 28547002
J Immunother Cancer. 2021 Feb;9(2):
pubmed: 33579736
Nucleic Acids Res. 2015 Apr 20;43(7):e47
pubmed: 25605792
Clin Cancer Res. 2021 Mar 15;27(6):1766-1777
pubmed: 33272983
Blood. 2018 Jan 4;131(1):49-57
pubmed: 29118009
J Immunother Cancer. 2020 Dec;8(2):
pubmed: 33335029
PLoS One. 2017 Jan 20;12(1):e0170501
pubmed: 28107439
Brain. 2021 Feb 12;144(1):53-69
pubmed: 33300045
Front Oncol. 2018 Mar 12;8:61
pubmed: 29594041
Immunol Rev. 2009 May;229(1):192-215
pubmed: 19426223
Nat Rev Immunol. 2003 Aug;3(8):609-20
pubmed: 12974476
Genome Biol. 2004;5(10):R80
pubmed: 15461798
Nat Commun. 2019 Mar 4;10(1):1023
pubmed: 30833574
PLoS One. 2015 Mar 06;10(3):e0118926
pubmed: 25748921
Mod Pathol. 2020 Dec;33(12):2507-2519
pubmed: 32591586
PLoS One. 2013 Oct 02;8(10):e77639
pubmed: 24098593
J Neurooncol. 2019 Oct;145(1):177-184
pubmed: 31522324
Mol Cancer Res. 2017 Sep;15(9):1243-1254
pubmed: 28522693
Nat Rev Immunol. 2018 Nov;18(11):671-688
pubmed: 30209347
Proc Natl Acad Sci U S A. 2015 Jun 16;112(24):7551-6
pubmed: 26034288
Nature. 2011 Dec 21;480(7378):480-9
pubmed: 22193102
Viruses. 2016 May 19;8(5):
pubmed: 27213425
J Clin Oncol. 2018 May 10;36(14):1419-1427
pubmed: 29432077
J Clin Invest. 2002 Mar;109(5):651-9
pubmed: 11877473
Acta Neuropathol Commun. 2018 Jun 28;6(1):51
pubmed: 29954445
Nat Rev Cancer. 2016 Jan;16(1):7-19
pubmed: 26694935
Ann Neurol. 2019 Oct;86(4):539-551
pubmed: 31376172
Cancer Genet. 2015 Jul-Aug;208(7-8):367-73
pubmed: 26206682
Nat Med. 2015 Jun;21(6):555-9
pubmed: 25939062
Neuro Oncol. 2019 Jan 1;21(1):83-94
pubmed: 30169876

Auteurs

Virginia Laspidea (V)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Pediatrics, Navarra University Clinic, Pamplona, Spain.

Montserrat Puigdelloses (M)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Pediatrics, Navarra University Clinic, Pamplona, Spain.

Sara Labiano (S)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Pediatrics, Navarra University Clinic, Pamplona, Spain.

Lucía Marrodán (L)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Pediatrics, Navarra University Clinic, Pamplona, Spain.

Marc Garcia-Moure (M)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Pediatrics, Navarra University Clinic, Pamplona, Spain.

Marta Zalacain (M)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Pediatrics, Navarra University Clinic, Pamplona, Spain.

Marisol Gonzalez-Huarriz (M)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Pediatrics, Navarra University Clinic, Pamplona, Spain.

Naiara Martínez-Vélez (N)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Pediatrics, Navarra University Clinic, Pamplona, Spain.

Iker Ausejo-Mauleon (I)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Pediatrics, Navarra University Clinic, Pamplona, Spain.

Daniel de la Nava (D)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Pediatrics, Navarra University Clinic, Pamplona, Spain.

Guillermo Herrador-Cañete (G)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Gene Therapy and Regulation of Gene Expression Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.

Javier Marco-Sanz (J)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Pediatrics, Navarra University Clinic, Pamplona, Spain.

Elisabeth Guruceaga (E)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Bioinformatics Platform, El Centro de Investigación Médica Aplicada (CIMA), University of Navarra, Pamplona, Spain.

Carlos E de Andrea (CE)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Department of Pathology, Navarra University Clinic, Pamplona, Spain.

María Villalba (M)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Department of Pathology, Navarra University Clinic, Pamplona, Spain.

Oren Becher (O)

Department of Pediatrics.
Department of Biochemistry and Molecular Genetics, and.
Lurie Comprehensive Cancer Center, Northwestern University, Chicago, Illinois, USA.
Division of Hematology Oncology and Stem Cell Transplant, Ann & Robert H. Lurie Children's Hospital, Chicago, Illinois, USA.

Massimo Squatrito (M)

Seve Ballesteros Foundation Brain Tumor Group, Molecular Oncology Programme, Spanish National Cancer Research Center, Madrid, Spain.

Verónica Matía (V)

Seve Ballesteros Foundation Brain Tumor Group, Molecular Oncology Programme, Spanish National Cancer Research Center, Madrid, Spain.

Jaime Gállego Pérez-Larraya (J)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Neurology, Navarra University Clinic, Pamplona, Spain.

Ana Patiño-García (A)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Pediatrics, Navarra University Clinic, Pamplona, Spain.

Sumit Gupta (S)

Department of Neuro-Oncology, The University of Texas MD Anderson Cancer Center, Houston, Texas, USA.

Candelaria Gomez-Manzano (C)

Department of Neuro-Oncology, The University of Texas MD Anderson Cancer Center, Houston, Texas, USA.

Juan Fueyo (J)

Department of Neuro-Oncology, The University of Texas MD Anderson Cancer Center, Houston, Texas, USA.

Marta M Alonso (MM)

Health Research Institute of Navarra, Pamplona, Navarra, Spain.
Solid Tumor Program, Center for the Applied Medical Research, Pamplona, Navarra, Spain.
Department of Pediatrics, Navarra University Clinic, Pamplona, Spain.

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