Urine-Derived Kidney Progenitor Cells in Cystinosis.
cell model
cystinosis
gene therapy
kidney progenitors
Journal
Cells
ISSN: 2073-4409
Titre abrégé: Cells
Pays: Switzerland
ID NLM: 101600052
Informations de publication
Date de publication:
06 04 2022
06 04 2022
Historique:
received:
31
01
2022
revised:
14
03
2022
accepted:
31
03
2022
entrez:
12
4
2022
pubmed:
13
4
2022
medline:
14
4
2022
Statut:
epublish
Résumé
Nephropathic cystinosis is an inherited lysosomal storage disorder caused by pathogenic variants in the cystinosin (
Identifiants
pubmed: 35406807
pii: cells11071245
doi: 10.3390/cells11071245
pmc: PMC8997687
pii:
doi:
Substances chimiques
Cystine
48TCX9A1VT
Types de publication
Journal Article
Research Support, Non-U.S. Gov't
Langues
eng
Sous-ensembles de citation
IM
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