Case Report: Novel Biallelic Variants in

DNAJC21 gene Shwachman–Diamond syndrome bone marrow failure syndrome ribosomopathy telomeres

Journal

Frontiers in genetics
ISSN: 1664-8021
Titre abrégé: Front Genet
Pays: Switzerland
ID NLM: 101560621

Informations de publication

Date de publication:
2022
Historique:
received: 06 02 2022
accepted: 28 02 2022
entrez: 25 4 2022
pubmed: 26 4 2022
medline: 26 4 2022
Statut: epublish

Résumé

Bone marrow failure represents an umbrella diagnosis for several life-threatening disorders. In many people, the etiology remains unknown for a long time, leading to an odyssey to diagnosis, with numerous tests performed and sometimes inappropriate treatment. Biallelic pathogenic variants in the

Identifiants

pubmed: 35464845
doi: 10.3389/fgene.2022.870233
pii: 870233
pmc: PMC9023866
doi:

Types de publication

Case Reports

Langues

eng

Pagination

870233

Commentaires et corrections

Type : ErratumIn

Informations de copyright

Copyright © 2022 Chirita-Emandi, Petrescu, Zimbru, Stoica, Marian, Ciubotaru, Bataneant and Puiu.

Déclaration de conflit d'intérêts

The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.

Références

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Blood. 2018 Feb 15;131(7):717-732
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Acta Ophthalmol. 2018 May;96(3):301-309
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Blood. 2017 Mar 16;129(11):1413-1414
pubmed: 28302692

Auteurs

Adela Chirita-Emandi (A)

Department of Genetics, Center of Genomic Medicine, "Victor Babes" University of Medicine and Pharmacy, Timisoara, Romania.
Regional Center of Medical Genetics Timis, Clinical Emergency Hospital for Children "Louis Turcanu", Timisoara, Romania.

Carmen-Angela-Maria Petrescu (CA)

Department of Pediatrics, "Victor Babes" University of Medicine and Pharmacy, Timisoara, Romania.
Department of Oncology and Hematology, Clinical Emergency Hospital for Children "Louis Turcanu", Timisoara, Romania.

Cristian G Zimbru (CG)

Department of Genetics, Center of Genomic Medicine, "Victor Babes" University of Medicine and Pharmacy, Timisoara, Romania.
Department of Automation and Applied Informatics, Politehnica University of Timisoara, Timisoara, Romania.

Florina Stoica (F)

Department of Ophthalmology, Municipal Clinical Emergency Hospital of Timisoara, Timisoara, Romania.

Catalin Marian (C)

Department of Biochemistry, "Victor Babes" University of Medicine and Pharmacy, Timisoara, Romania.
Center for Complex Networks Science, "Victor Babes" University of Medicine and Pharmacy, Timisoara, Romania.

Andreea Ciubotaru (A)

INFOSAN Ophthalmology Hospital, Bucharest, Romania.

Mihaela Bataneant (M)

Department of Pediatrics, "Victor Babes" University of Medicine and Pharmacy, Timisoara, Romania.
Department of Oncology and Hematology, Clinical Emergency Hospital for Children "Louis Turcanu", Timisoara, Romania.

Maria Puiu (M)

Department of Genetics, Center of Genomic Medicine, "Victor Babes" University of Medicine and Pharmacy, Timisoara, Romania.
Regional Center of Medical Genetics Timis, Clinical Emergency Hospital for Children "Louis Turcanu", Timisoara, Romania.

Classifications MeSH