Nanodelivery of nucleic acids.
Journal
Nature reviews. Methods primers
ISSN: 2662-8449
Titre abrégé: Nat Rev Methods Primers
Pays: England
ID NLM: 101778010
Informations de publication
Date de publication:
2022
2022
Historique:
entrez:
28
4
2022
pubmed:
29
4
2022
medline:
29
4
2022
Statut:
ppublish
Résumé
There is growing need for a safe, efficient, specific and non-pathogenic means for delivery of gene therapy materials. Nanomaterials for nucleic acid delivery offer an unprecedented opportunity to overcome these drawbacks; owing to their tunability with diverse physico-chemical properties, they can readily be functionalized with any type of biomolecules/moieties for selective targeting. Nucleic acid therapeutics such as antisense DNA, mRNA, small interfering RNA (siRNA) or microRNA (miRNA) have been widely explored to modulate DNA or RNA expression Strikingly, gene therapies combined with nanoscale delivery systems have broadened the therapeutic and biomedical applications of these molecules, such as bioanalysis, gene silencing, protein replacement and vaccines. Here, we overview how to design smart nucleic acid delivery methods, which provide functionality and efficacy in the layout of molecular diagnostics and therapeutic systems. It is crucial to outline some of the general design considerations of nucleic acid delivery nanoparticles, their extraordinary properties and the structure-function relationships of these nanomaterials with biological systems and diseased cells and tissues.
Identifiants
pubmed: 35480987
doi: 10.1038/s43586-022-00104-y
pmc: PMC9038125
mid: NIHMS1799023
pii:
doi:
Types de publication
Journal Article
Langues
eng
Subventions
Organisme : NHLBI NIH HHS
ID : R01 HL158097
Pays : United States
Organisme : NHLBI NIH HHS
ID : R01 HL156362
Pays : United States
Organisme : NHLBI NIH HHS
ID : R01 HL162367
Pays : United States
Organisme : NHLBI NIH HHS
ID : R01 HL159012
Pays : United States
Organisme : NCI NIH HHS
ID : R01 CA200900
Pays : United States
Organisme : NHLBI NIH HHS
ID : R01 HL137229
Pays : United States
Déclaration de conflit d'intérêts
Competing interests J. Conde is a co-founder and shareholder of TargTex S.A. The other authors declare no competing interests.
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