Platelet-targeted thrombolysis for treatment of acute ischemic stroke.


Journal

Blood advances
ISSN: 2473-9537
Titre abrégé: Blood Adv
Pays: United States
ID NLM: 101698425

Informations de publication

Date de publication:
28 02 2023
Historique:
accepted: 09 04 2022
received: 29 11 2021
pubmed: 29 4 2022
medline: 25 2 2023
entrez: 28 4 2022
Statut: ppublish

Résumé

Thrombolysis with tissue-type plasminogen activator (tPA) remains the main treatment for acute ischemic stroke. Nevertheless, tPA intervention is limited by a short therapeutic window, low recanalization rates, and a risk of intracranial hemorrhage (ICH), highlighting the clinical demand for improved thrombolytic drugs. We examined a novel thrombolytic agent termed "SCE5-scuPA," comprising a single-chain urokinase plasminogen activator (scuPA) fused with a single-chain antibody (SCE5) that targets the activated glycoprotein IIb/IIIa platelet receptor, for its effects in experimental stroke. SCE5-scuPA was first tested in a whole blood clot degradation assay to show the benefit of platelet-targeted thrombolysis. The tail bleeding time, blood clearance, and biodistribution were then determined to inform the use of SCE5-scuPA in mouse models of photothrombotic stroke and middle cerebral artery occlusion against tenecteplase. The impacts of SCE5-scuPA on motor function, ICH, blood-brain barrier (BBB) integrity, and immunosuppression were evaluated. Infarct size was measured by computed tomography imaging and magnetic resonance imaging. SCE5-scuPA enhanced clot degradation ex vivo compared with its nonplatelet-targeting control. The maximal SCE5-scuPA dose that maintained hemostasis and a rapid blood clearance was determined. SCE5-scuPA administration both before and 2 hours after photothrombotic stroke reduced the infarct volume. SCE5-scuPA also improved neurologic deficit, decreased intracerebral blood deposits, preserved the BBB, and alleviated immunosuppression poststroke. In middle cerebral artery occlusion, SCE5-scuPA did not worsen stroke outcomes or cause ICH, and it protected the BBB. Our findings support the ongoing development of platelet-targeted thrombolysis with SCE5-scuPA as a novel emergency treatment for acute ischemic stroke with a promising safety profile.

Identifiants

pubmed: 35482909
pii: 485108
doi: 10.1182/bloodadvances.2021006691
pmc: PMC9984306
doi:

Substances chimiques

Fibrinolytic Agents 0
Urokinase-Type Plasminogen Activator EC 3.4.21.73
Platelet Glycoprotein GPIIb-IIIa Complex 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

561-574

Informations de copyright

© 2023 by The American Society of Hematology. Licensed under Creative Commons Attribution-NonCommercial-NoDerivatives 4.0 International (CC BY-NC-ND 4.0), permitting only noncommercial, nonderivative use with attribution. All other rights reserved.

Références

Circ Res. 2014 Mar 28;114(7):1083-93
pubmed: 24508759
Exp Transl Stroke Med. 2015 Jan 27;7:2
pubmed: 25657829
Front Immunol. 2019 Mar 27;10:591
pubmed: 30972077
Int J Emerg Med. 2022 Jan 4;15(1):1
pubmed: 34983359
JAMA. 1999 Dec 1;282(21):2003-11
pubmed: 10591382
Exp Neurobiol. 2016 Oct;25(5):241-251
pubmed: 27790058
N Engl J Med. 1995 Dec 14;333(24):1581-7
pubmed: 7477192
Stroke. 2004 Jul;35(7):1683-7
pubmed: 15155956
Nat Med. 2001 Jan;7(1):59-64
pubmed: 11135617
Bull World Health Organ. 2016 Sep 1;94(9):634-634A
pubmed: 27708464
West J Emerg Med. 2020 Feb 24;21(2):199-202
pubmed: 32191176
Curr Pharm Des. 2010;16(37):4119-33
pubmed: 21247395
Sci Rep. 2017 May 24;7(1):2346
pubmed: 28539608
Hemasphere. 2021 Jun 01;5(6):e570
pubmed: 34095754
Circ Res. 2006 Jul 7;99(1):25-33
pubmed: 16778135
Arterioscler Thromb Vasc Biol. 2001 Jan;21(1):142-8
pubmed: 11145946
Lancet. 2018 Oct 6;392(10154):1247-1256
pubmed: 30319112
Thromb Haemost. 2009 Jun;101(6):1012-9
pubmed: 19492141
Front Neurol. 2021 May 14;12:661955
pubmed: 34054705
Stroke. 2004 Sep;35(9):2128-33
pubmed: 15272127
Blood Adv. 2020 Apr 14;4(7):1222-1231
pubmed: 32227212
PLoS One. 2020 May 11;15(5):e0232497
pubmed: 32392257
Circulation. 1999 Jun 15;99(23):3050-5
pubmed: 10368124
Stroke. 2010 Oct;41(10):2254-8
pubmed: 20829513
Ann Transl Med. 2014 Aug;2(8):81
pubmed: 25333056
J Vis Exp. 2013 Jun 09;(76):
pubmed: 23770844
Biochem J. 1990 May 1;267(3):647-52
pubmed: 2160232
J Cereb Blood Flow Metab. 2017 Jul;37(7):2539-2554
pubmed: 27683449
Arterioscler Thromb. 1994 Sep;14(9):1452-8
pubmed: 8068607
Indian J Crit Care Med. 2015 May;19(5):265-9
pubmed: 25983432
Arzneimittelforschung. 1991 Dec;41(12):1310-9
pubmed: 1815534
Sports Med. 2003;33(3):231-43
pubmed: 12656642
JAMA. 2020 Apr 7;323(13):1257-1265
pubmed: 32078683
Lancet Neurol. 2017 Oct;16(10):781-788
pubmed: 28780236
Cerebrovasc Dis. 2016;42(5-6):361-369
pubmed: 27336314
Front Neurol. 2020 Nov 03;11:589628
pubmed: 33224099
Heart. 2003 Nov;89(11):1358-62
pubmed: 14594904
Stroke. 2018 Mar;49(3):700-709
pubmed: 29382802
J Neurochem. 2008 Nov;107(4):1091-101
pubmed: 18796005
Stroke. 2020 Dec;51(12):3681-3689
pubmed: 33023423
J Cereb Blood Flow Metab. 2014 Aug;34(8):1283-96
pubmed: 24896566
Blood. 1989 May 15;73(7):1842-50
pubmed: 2496774
Curr Opin Hematol. 2010 Nov;17(6):585-9
pubmed: 20729731
Stroke. 2013 Jun;44(6 Suppl 1):S84-6
pubmed: 23709741
Eur J Neurol. 2014 Feb;21(2):215-22
pubmed: 23848934
Cerebrovasc Dis. 2021;50(4):375-382
pubmed: 33849042
Circulation. 1995 Nov 15;92(10):3032-40
pubmed: 7586274
Blood. 2010 Jun 24;115(25):5241-8
pubmed: 20410503
Thromb Haemost. 1984 Aug 31;52(1):24-6
pubmed: 6495260

Auteurs

Jason S Palazzolo (JS)

NanoBiotechnology Laboratory, Monash University, Melbourne, VIC, Australia.

Anukreity Ale (A)

NanoBiotechnology Laboratory, Monash University, Melbourne, VIC, Australia.

Heidi Ho (H)

Molecular Neurotrauma and Haemostasis, Australian Centre for Blood Diseases, Central Clinical School, Monash University, Melbourne, VIC, Australia.

Shweta Jagdale (S)

NanoBiotechnology Laboratory, Monash University, Melbourne, VIC, Australia.

Brad R S Broughton (BRS)

Department of Pharmacology, Monash Biomedicine Discovery Institute, Monash University, Melbourne, VIC, Australia.

Robert L Medcalf (RL)

Molecular Neurotrauma and Haemostasis, Australian Centre for Blood Diseases, Central Clinical School, Monash University, Melbourne, VIC, Australia.

David K Wright (DK)

Department of Neuroscience, Central Clinical School, Monash University, Melbourne, VIC, Australia.

Karen Alt (K)

NanoTheranostics Laboratory, Australian Centre for Blood Diseases, Central Clinical School, Monash University, Melbourne, VIC, Australia.

Christoph E Hagemeyer (CE)

NanoBiotechnology Laboratory, Monash University, Melbourne, VIC, Australia.

Be'eri Niego (B)

NanoBiotechnology Laboratory, Monash University, Melbourne, VIC, Australia.

Articles similaires

Robotic Surgical Procedures Animals Humans Telemedicine Models, Animal

Odour generalisation and detection dog training.

Lyn Caldicott, Thomas W Pike, Helen E Zulch et al.
1.00
Animals Odorants Dogs Generalization, Psychological Smell
Animals TOR Serine-Threonine Kinases Colorectal Neoplasms Colitis Mice
Animals Tail Swine Behavior, Animal Animal Husbandry

Classifications MeSH