Development of a core outcome set for basal cell carcinoma.


Journal

Journal of the American Academy of Dermatology
ISSN: 1097-6787
Titre abrégé: J Am Acad Dermatol
Pays: United States
ID NLM: 7907132

Informations de publication

Date de publication:
09 2022
Historique:
received: 11 02 2020
revised: 18 04 2022
accepted: 23 04 2022
pubmed: 14 5 2022
medline: 24 8 2022
entrez: 13 5 2022
Statut: ppublish

Résumé

There is variation in the outcomes reported in clinical studies of basal cell carcinoma. This can prevent effective meta-analyses from answering important clinical questions. To identify a recommended minimum set of core outcomes for basal cell carcinoma clinical trials. Patient and professional Delphi process to cull a long list, culminating in a consensus meeting. To be provisionally accepted, outcomes needed to be deemed important (score, 7-9, with 9 being the maximum) by 70% of each stakeholder group. Two hundred thirty-five candidate outcomes identified via a systematic literature review and survey of key stakeholders were reduced to 74 that were rated by 100 health care professionals and patients in 2 Delphi rounds. Twenty-seven outcomes were provisionally accepted. The final core set of 5 agreed-upon outcomes after the consensus meeting included complete response; persistent or serious adverse events; recurrence-free survival; quality of life; and patient satisfaction, including cosmetic outcome. English-speaking patients and professionals rated outcomes extracted from English language studies. A core outcome set for basal cell carcinoma has been developed. The use of relevant measures may improve the utility of clinical research and the quality of therapeutic guidance available to clinicians.

Sections du résumé

BACKGROUND
There is variation in the outcomes reported in clinical studies of basal cell carcinoma. This can prevent effective meta-analyses from answering important clinical questions.
OBJECTIVE
To identify a recommended minimum set of core outcomes for basal cell carcinoma clinical trials.
METHODS
Patient and professional Delphi process to cull a long list, culminating in a consensus meeting. To be provisionally accepted, outcomes needed to be deemed important (score, 7-9, with 9 being the maximum) by 70% of each stakeholder group.
RESULTS
Two hundred thirty-five candidate outcomes identified via a systematic literature review and survey of key stakeholders were reduced to 74 that were rated by 100 health care professionals and patients in 2 Delphi rounds. Twenty-seven outcomes were provisionally accepted. The final core set of 5 agreed-upon outcomes after the consensus meeting included complete response; persistent or serious adverse events; recurrence-free survival; quality of life; and patient satisfaction, including cosmetic outcome.
LIMITATIONS
English-speaking patients and professionals rated outcomes extracted from English language studies.
CONCLUSION
A core outcome set for basal cell carcinoma has been developed. The use of relevant measures may improve the utility of clinical research and the quality of therapeutic guidance available to clinicians.

Identifiants

pubmed: 35551965
pii: S0190-9622(22)00789-7
doi: 10.1016/j.jaad.2022.04.059
pii:
doi:

Types de publication

Journal Article Systematic Review Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

573-581

Informations de copyright

Copyright © 2022 American Academy of Dermatology, Inc. Published by Elsevier Inc. All rights reserved.

Déclaration de conflit d'intérêts

Conflicts of interest Dr Kirkham is involved with the COMET and CS-COUSIN Methods groups. Drs Schmitt and Alam are involved with the CS-COUSIN Methods group. Dr Armstrong has served as a research investigator and/or scientific advisor to AbbVie, Almirall, Arcutis, ASLAN, Beiersdorf, BI, BMS, EPI, Incyte, Leo, UCB, Janssen, Lilly, Nimbus, Novartis, Ortho Dermatologics, Sun, Dermavant, Dermira, Sanofi, Regeneron, Pfizer, and Modmed. The remaining authors have no relevant conflicts to disclose.

Auteurs

Daniel I Schlessinger (DI)

Department of Dermatology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois; Division of Dermatology, Department of Internal Medicine, Washington University, St. Louis, Missouri.

Kelly A Reynolds (KA)

Department of Dermatology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois; University of Cincinnati College of Medicine, Cincinnati, Ohio.

McKenzie A Dirr (MA)

Department of Dermatology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois.

Sarah A Ibrahim (SA)

Department of Dermatology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois.

Arianna F Yanes (AF)

Department of Dermatology, Perelman Center for Advanced Medicine, Hospital of the University of Pennsylvania, Philadelphia, Pennsylvania.

Jake M Lazaroff (JM)

Department of Dermatology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois.

Victoria Godinez-Puig (V)

Department of Dermatology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois.

Brian R Chen (BR)

Department of Dermatology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois.

Anastasia O Kurta (AO)

Department of Dermatology, Saint Louis University, St. Louis, Missouri.

Jill K Cotseones (JK)

Medical & Cosmetic Dermatology Service, Northwestern Medicine Regional Medical Group, Naperville, Illinois.

Sarah G Chiren (SG)

Department of Dermatology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois.

Karina C Furlan (KC)

Department of Pathology, Rush University Medical Center, Chicago, Illinois.

Sanjana Iyengar (S)

Department of Dermatology, West Virginia University, Morgantown, West Virginia.

Ramona Behshad (R)

Department of Dermatology, Saint Louis University, St. Louis, Missouri.

Danielle M DeHoratius (DM)

Department of Dermatology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, Pennsylvania.

Pablo Denes (P)

Division of Cardiology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois.

Aaron M Drucker (AM)

Division of Dermatology, Department of Medicine, University of Toronto, Toronto, Ontario, Canada; Division of Dermatology, Department of Medicine and Women's College Research Institute, Women's College Hospital, Toronto, Ontario, Canada.

Leonard M Dzubow (LM)

Private Practice, Media, Pennsylvania.

Jeremy R Etzkorn (JR)

Department of Dermatology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, Pennsylvania.

Catherine A Harwood (CA)

Department of Dermatology, Royal London Hospital, Barts Health NHS Trust, London, United Kingdom; Centre for Cell Biology and Cutaneous Research, Blizard Institute, Barts and the London School of Medicine and Dentistry, Queen Mary University of London, London, United Kingdom.

John Y S Kim (JYS)

Division of Plastic and Reconstructive Surgery, Feinberg School of Medicine, Northwestern University, Chicago, Illinois.

Naomi Lawrence (N)

Division of Dermatologic Surgery, Department of Dermatology, Cooper University Hospital, Camden, New Jersey.

Erica H Lee (EH)

Dermatology Service, Memorial Sloan Kettering Cancer Center, New York, New York.

Gary S Lissner (GS)

Department of Ophthalmology, Northwestern University, Feinberg School of Medicine, Chicago, Illinois.

Ashfaq A Marghoob (AA)

Department of Dermatology, Memorial Sloan Kettering Cancer Center, New York, New York.

Rubeta N Matin (RN)

Department of Dermatology, Churchill Hospital, Oxford, United Kingdom.

Adam R Mattox (AR)

Department of Dermatology, University of Minnesota, Minneapolis, Minnesota.

Bharat B Mittal (BB)

Department of Radiation Oncology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois.

J Regan Thomas (JR)

Department of Otolaryngology - Head and Neck Surgery, Feinberg School of Medicine, Northwestern University, Chicago, Illinois.

Xiaolong Alan Zhou (XA)

Department of Dermatology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois.

David Zloty (D)

Department of Dermatology & Skin Science, University of British Columbia, Vancouver, British Columbia, Canada.

Jochen Schmitt (J)

Center for Evidence-based Healthcare, Medical Faculty Carl Gustav Carus, TU Dresden, Dresden, Germany.

Jamie J Kirkham (JJ)

Centre for Biostatistics, The University of Manchester, Manchester Academic Health Science Centre, Manchester, United Kingdom.

April W Armstrong (AW)

Keck School of Medicine, Department of Dermatology, University of Southern California, Los Angeles, California.

Nicole Basset-Seguin (N)

Universite de Paris, Hospital Saint Louis, Paris, France.

Elizabeth M Billingsley (EM)

Department of Dermatology, Penn State Hershey Medical Center, Hershey, Pennsylvania.

Jeremy S Bordeaux (JS)

Department of Dermatology, University Hospitals of Cleveland, Case Western Reserve University, Cleveland, Ohio.

Jerry Brewer (J)

Mayo Clinic, Rochester, Minnesota.

Marc Brown (M)

Department of Dermatology and Oncology, University of Rochester, Rochester, Minnesota.

Mariah Brown (M)

Department of Dermatology, University of Colorado Hospital and School of Medicine, Aurora, Colorado.

Scott A B Collins (SAB)

Private Practice, Dermatology Associates, Tigard, Oregon.

Maria Concetta Fargnoli (MC)

Dermatology, Department of Biotechnological and Applied Clinical Sciences, University of L'Aquila, L'Aquila, Italy.

Sergio Jobim De Azevedo (SJ)

Department of Medicine, Chief of Medical Oncology at Hospital de Clinicas de Porto Alegre, Porto Alegre, Brazil.

Reinhard Dummer (R)

University Hospital, Skin Cancer Center, Zurich, Switzerland.

Alexander Eggermont (A)

University Medical Center Utrecht, The Netherlands.

Glenn D Goldman (GD)

University of Vermont Medical Center, Burlington, Vermont.

Merete Haedersdal (M)

Copenhagen University Hospital, Bispebjerg and Frederiksberg, Copenhagen, Denmark.

Elizabeth K Hale (EK)

The Ronald O. Perelman Department of Dermatology, New York University School of Medicine, New York, New York.

Allison Hanlon (A)

Vanderbilt Department of Dermatology, Nashville, Tennessee.

Kelly L Harms (KL)

Department of Dermatology, University of Michigan Medical School, Michigan Medicine, Ann Arbor, Michigan.

Conway C Huang (CC)

Department of Dermatology, University of Alabama at Birmingham, Birmingham, Alabama.

Eva A Hurst (EA)

Distinctive Dermatology, Fairview Heights, Illinois.

Gino K In (GK)

Division of Medical Oncology, Norris Comprehensive Cancer Center, University of Southern California, Los Angeles, California.

Nicole Kelleners-Smeets (N)

Maastricht University Medical Centre, Maastricht, The Netherlands.

Meenal Kheterpal (M)

Duke University, Durham, North Carolina.

Barry Leshin (B)

Skin Surgery Center, Winston-Salem, North Carolina.

Michel Mcdonald (M)

Vanderbilt University Medical Center, Nashville, Tennessee.

Stanley J Miller (SJ)

Johns Hopkins Hospital, Baltimore, Maryland.

Alexander Miller (A)

Department of Dermatology, University of California Irvine, Irvine, California.

Eliot N Mostow (EN)

Northeast Ohio Medical University (NEOMED), Rootstown, Ohio.

Myrto Trakatelli (M)

Department of Dermatology, Papageorgiou Hospital, Aristotle University Department of Medicine, Thessaloniki, Greece.

Kishwer S Nehal (KS)

Dermatology Service, Memorial Sloan Kettering Cancer Center, New York, New York.

Desiree Ratner (D)

Dermatology, NYU Grossman School of Medicine, New York, New York.

Howard Rogers (H)

Advanced Dermatology, Norwich, Connecticut.

Kavita Y Sarin (KY)

Department of Dermatology, Stanford University School of Medicine, Stanford, California.

Seaver L Soon (SL)

The Skin Clinic MD (private practice), San Diego, California.

Thomas Stasko (T)

Department of Dermatology, The University of Oklahoma, Oklahoma City, Oklahoma.

Paul A Storrs (PA)

Department of Dermatology, University of Illinois Chicago, Chicago, Illinois.

Luca Tagliaferri (L)

Fondazione Policlinico Universitario Agostino Gemelli, IRCCS, Rome, Italy.

Allison T Vidimos (AT)

Department of Dermatology, Cleveland Clinic, Cleveland, Ohio.

Sandra L Wong (SL)

Department of Surgery, Dartmouth Health, Lebanon, New Hampshire.

Siegrid S Yu (SS)

Department of Dermatology, University of California San Francisco, California.

Iris Zalaudek (I)

Department of Dermatology and Venereology, University of Trieste, Trieste, Italy.

Nathalie C Zeitouni (NC)

Medical Dermatology Specialists, Phoenix, Arizona.

John A Zitelli (JA)

Dermatology, Otolaryngology, and Plastic Surgery, University of Pittsburgh Medical Center, Pittsburgh, Pennsylvania.

Emily Poon (E)

Department of Dermatology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois.

Joseph F Sobanko (JF)

Department of Dermatology, Perelman Center for Advanced Medicine, Hospital of the University of Pennsylvania, Philadelphia, Pennsylvania; Division of Dermatologic Surgery, Department of Dermatology, Hospital of the University of Pennsylvania, Philadelphia, Pennsylvania.

Todd V Cartee (TV)

Department of Dermatology, Penn State Health, Milton S. Hershey Medical Center, Hershey, Pennsylvania.

Ian A Maher (IA)

Department of Dermatology, University of Minnesota, Minneapolis, Minnesota.

Murad Alam (M)

Department of Dermatology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois; Department of Otolaryngology - Head and Neck Surgery, Feinberg School of Medicine, Northwestern University, Chicago, Illinois; Department of Surgery, Feinberg School of Medicine, Northwestern University, Chicago, Illinois. Electronic address: m-alam@northwestern.edu.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH