Novel large deletion involving EVC and EVC2 in Ellis-van Creveld syndrome.


Journal

Human genome variation
ISSN: 2054-345X
Titre abrégé: Hum Genome Var
Pays: England
ID NLM: 101652445

Informations de publication

Date de publication:
17 May 2022
Historique:
received: 03 02 2022
accepted: 17 03 2022
revised: 17 03 2022
entrez: 17 5 2022
pubmed: 18 5 2022
medline: 18 5 2022
Statut: epublish

Résumé

Ellis-van Creveld syndrome is an autosomal recessive skeletal dysplasia that is characterized by thoracic hypoplasia, polydactyly, oral abnormalities, and congenital heart disease. It is caused by pathogenic variants in the EVC or EVC2 genes. We report a case of a newborn with a compound heterozygous variant comprising NM_147127.5: c.1991dup:[p.Lys665Glufs*10] in the EVC2 gene and a novel large deletion involving exon 1 in EVC and exons 1-7 in EVC2.

Identifiants

pubmed: 35581188
doi: 10.1038/s41439-022-00190-0
pii: 10.1038/s41439-022-00190-0
pmc: PMC9114401
doi:

Types de publication

Journal Article

Langues

eng

Pagination

15

Informations de copyright

© 2022. The Author(s).

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Auteurs

Hiroki Sato (H)

Department of Pediatrics, Tokushima University Hospital, Kuramotocho, Tokushima, Japan.

Kenichi Suga (K)

Department of Pediatrics, Tokushima University Hospital, Kuramotocho, Tokushima, Japan. suga.kenichi.1@tokushima-u.ac.jp.

Masashi Suzue (M)

Department of Pediatrics, Tokushima University Hospital, Kuramotocho, Tokushima, Japan.

Yukako Honma (Y)

Department of Pediatrics, Tokushima University Hospital, Kuramotocho, Tokushima, Japan.

Yasunobu Hayabuchi (Y)

Department of Pediatrics, Tokushima University Hospital, Kuramotocho, Tokushima, Japan.

Shunsuke Miyai (S)

Division of Molecular Genetics, Institute for Comprehensive Medical Science, Fujita Health University, Toyoake, Japan.

Hiroki Kurahashi (H)

Division of Molecular Genetics, Institute for Comprehensive Medical Science, Fujita Health University, Toyoake, Japan.

Ryuji Nakagawa (R)

Department of Pediatrics, Tokushima University Hospital, Kuramotocho, Tokushima, Japan.

Classifications MeSH