Treatment Pathways and Health Outcomes of German Patients with Chronic Graft-Versus-Host Disease After Allogeneic Hematopoietic Cell Transplantation: A Retrospective Health Claims Data Analysis.


Journal

Drugs - real world outcomes
ISSN: 2199-1154
Titre abrégé: Drugs Real World Outcomes
Pays: Switzerland
ID NLM: 101658456

Informations de publication

Date de publication:
Dec 2022
Historique:
accepted: 06 06 2022
pubmed: 3 7 2022
medline: 3 7 2022
entrez: 2 7 2022
Statut: ppublish

Résumé

Although chronic graft-versus-host-disease (cGvHD) is an important long-term complication after allogenic hematopoietic cell transplantation (allo-HCT) and is associated with increased healthcare resource utilization, real-world evidence is scarce. The aim of the study was to evaluate survival of patients with cGvHD in Germany and to analyze hospitalization and treatment patterns. Based on a German claims database with 4.9 million enrollees, a retrospective longitudinal analysis covering a 6-year period between 2013 and 2018 was conducted. Patients with allo-HCT in 2014 or 2015 (index date) and no record of transplantation or documentation of GvHD 365 days prior to index were included. Patients who subsequently developed a cGVHD were compared with those who did not develop a cGVHD within 3 years after index date. cGVHD cases were identified based on documented International Classification of Diseases, Tenth Revision (ICD-10) diagnosis and treatment algorithms. Since the onset of cGvHD is defined at 100 days after allo-HCT, only those alive beyond day 100 were considered in the survival analysis. Patients who did not survive the first 100 days after allo-HCT were censored to prevent a selection bias due to early mortality within patients without GvHD. Survival rates were plotted using the Kaplan-Meier estimator. The number of hospitalizations and average lengths of stay as well as treatment patterns were descriptively examined. Overall, 165 cGvHD patients were identified and compared with 43 patients without cGVHD. Short-term survival rates were better for patients with cGvHD; the 6-month survival probability was 95.8% for patients with cGVHD and 83.7% for patients without cGVHD. However, long-term survival was better in patients without GvHD; The 30-month survival probability was 65.5% for patients with cGVHD and 76.7% for patients without cGVHD. While overall 90% of cGvHD patients were hospitalized at least once, the share was only half for patients without GvHD (44%). 78.2% of patients with cGVHD received corticosteroids in combination with other predefined immunosuppressants. Findings from this study reveal a high disease burden associated with cGvHD. This underlines the high medical need for new interventional strategies to improve survival and morbidity after allo-HCT.

Sections du résumé

BACKGROUND BACKGROUND
Although chronic graft-versus-host-disease (cGvHD) is an important long-term complication after allogenic hematopoietic cell transplantation (allo-HCT) and is associated with increased healthcare resource utilization, real-world evidence is scarce.
OBJECTIVES OBJECTIVE
The aim of the study was to evaluate survival of patients with cGvHD in Germany and to analyze hospitalization and treatment patterns.
PATIENTS AND METHODS METHODS
Based on a German claims database with 4.9 million enrollees, a retrospective longitudinal analysis covering a 6-year period between 2013 and 2018 was conducted. Patients with allo-HCT in 2014 or 2015 (index date) and no record of transplantation or documentation of GvHD 365 days prior to index were included. Patients who subsequently developed a cGVHD were compared with those who did not develop a cGVHD within 3 years after index date. cGVHD cases were identified based on documented International Classification of Diseases, Tenth Revision (ICD-10) diagnosis and treatment algorithms. Since the onset of cGvHD is defined at 100 days after allo-HCT, only those alive beyond day 100 were considered in the survival analysis. Patients who did not survive the first 100 days after allo-HCT were censored to prevent a selection bias due to early mortality within patients without GvHD. Survival rates were plotted using the Kaplan-Meier estimator. The number of hospitalizations and average lengths of stay as well as treatment patterns were descriptively examined.
RESULTS RESULTS
Overall, 165 cGvHD patients were identified and compared with 43 patients without cGVHD. Short-term survival rates were better for patients with cGvHD; the 6-month survival probability was 95.8% for patients with cGVHD and 83.7% for patients without cGVHD. However, long-term survival was better in patients without GvHD; The 30-month survival probability was 65.5% for patients with cGVHD and 76.7% for patients without cGVHD. While overall 90% of cGvHD patients were hospitalized at least once, the share was only half for patients without GvHD (44%). 78.2% of patients with cGVHD received corticosteroids in combination with other predefined immunosuppressants.
CONCLUSION CONCLUSIONS
Findings from this study reveal a high disease burden associated with cGvHD. This underlines the high medical need for new interventional strategies to improve survival and morbidity after allo-HCT.

Identifiants

pubmed: 35779205
doi: 10.1007/s40801-022-00320-8
pii: 10.1007/s40801-022-00320-8
pmc: PMC9712900
doi:

Types de publication

Journal Article

Langues

eng

Pagination

577-588

Informations de copyright

© 2022. The Author(s).

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Auteurs

Christof Scheid (C)

Universitätsklinikum Köln (AöR), Kerpener Str. 62, 50937, Cologne, Germany.

Robert Kudernatsch (R)

Janssen-Cilag GmbH, Johnson & Johnson Platz 1, 41470, Neuss, Germany.

Marie Eckart (M)

Janssen-Cilag GmbH, Johnson & Johnson Platz 1, 41470, Neuss, Germany.

Chiara Feig (C)

HGC Healthcare Consultants GmbH, Graf-Adolf-Platz 15, 40213, Dusseldorf, Germany.

Vincent Straub (V)

HGC Healthcare Consultants GmbH, Graf-Adolf-Platz 15, 40213, Dusseldorf, Germany.

Berit Libutzki (B)

HGC Healthcare Consultants GmbH, Graf-Adolf-Platz 15, 40213, Dusseldorf, Germany.
Department of Psychiatry, Interdisciplinary Center Psychopathology and Emotion regulation (ICPE), University of Groningen, University Medical Center Groningen, Groningen, Groningen, The Netherlands.

Jörg Mahlich (J)

DICE, Heinrich-Heine-University Düsseldorf, Universitätsstraße 1, 40225, Dusseldorf, Germany. Joerg.mahlich@gmail.com.
Miltenyi Biomedicine, Friedrich-Ebert-Straße 68, 51429, Bergisch Gladbach, Germany. Joerg.mahlich@gmail.com.

Classifications MeSH