Frequency and Longitudinal Course of Motor Signs In Genetic Frontotemporal Dementia.


Journal

Neurology
ISSN: 1526-632X
Titre abrégé: Neurology
Pays: United States
ID NLM: 0401060

Informations de publication

Date de publication:
10 Aug 2022
Historique:
received: 12 10 2021
accepted: 21 04 2022
entrez: 10 8 2022
pubmed: 11 8 2022
medline: 11 8 2022
Statut: aheadofprint

Résumé

Frontotemporal dementia (FTD) is a highly heritable disorder. The majority of genetic cases are caused by autosomal dominant pathogenic variants in the We analyzed baseline visit data of known carriers of a pathogenic variant in the 322 pathogenic variant carriers were included in the analysis: 122 These results indicate the presence of multiple natural clusters of motor signs in genetic FTD, each correlated with specific atrophy patterns. Their motor severity depends on time and the affected gene. These clinico-genetic associations can guide diagnostic evaluations and the design of clinical trials for new disease-modifying and preventive treatments.

Sections du résumé

BACKGROUND AND OBJECTIVES OBJECTIVE
Frontotemporal dementia (FTD) is a highly heritable disorder. The majority of genetic cases are caused by autosomal dominant pathogenic variants in the
METHODS METHODS
We analyzed baseline visit data of known carriers of a pathogenic variant in the
RESULTS RESULTS
322 pathogenic variant carriers were included in the analysis: 122
DISCUSSION CONCLUSIONS
These results indicate the presence of multiple natural clusters of motor signs in genetic FTD, each correlated with specific atrophy patterns. Their motor severity depends on time and the affected gene. These clinico-genetic associations can guide diagnostic evaluations and the design of clinical trials for new disease-modifying and preventive treatments.

Identifiants

pubmed: 35948443
pii: WNL.0000000000200828
doi: 10.1212/WNL.0000000000200828
pmc: PMC9519250
pii:
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : Medical Research Council
ID : MC_UU_00005/12
Pays : United Kingdom
Organisme : Medical Research Council
ID : MR/M008525/1
Pays : United Kingdom
Organisme : Medical Research Council
ID : MR/M023664/1
Pays : United Kingdom
Organisme : Medical Research Council
ID : MR/T046015/1
Pays : United Kingdom

Commentaires et corrections

Type : CommentIn

Informations de copyright

Copyright © 2022 The Author(s). Published by Wolters Kluwer Health, Inc. on behalf of the American Academy of Neurology.

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Auteurs

Sonja Schönecker (S)

Department of Neurology, Ludwig-Maximilians-Universität München, Munich, Germany.

Francisco J Martinez-Murcia (FJ)

Department of Signal Theory Networking and Communications, Andalusian Research Institute in Data Science and Computational Intelligence (DaSCI), University of Granada,Granada, Spain.

Boris-Stephan Rauchmann (BS)

Institute for Clinical Radiology, Ludwig-Maximilians-Universität München, Munich, Germany.

Nicolai Franzmeier (N)

Institute for Stroke and Dementia Research, Ludwig-Maximilians-Universität München, Munich, Germany.

Catharina Prix (C)

Department of Neurology, Ludwig-Maximilians-Universität München, Munich, Germany.

Elisabeth Wlasich (E)

Department of Neurology, Ludwig-Maximilians-Universität München, Munich, Germany.

Sandra V Loosli (SV)

Department of Neurology, Ludwig-Maximilians-Universität München, Munich, Germany.

Katja Bochmann (K)

Institute of Neuroradiology, Ludwig-Maximilians-Universität München, Munich, Germany.

Juan-Manuel Gorriz Saez (JM)

Department of Signal Theory Networking and Communications, Andalusian Research Institute in Data Science and Computational Intelligence (DaSCI), University of Granada,Granada, Spain.

Robert Laforce (R)

Clinique Interdisciplinaire de Mémoire (CIME), Département des Sciences Neurologiques, Québec, Canada.

Simon Ducharme (S)

McConnell Brain Imaging Centre, Montreal Neurological Institute, McGill University, Montreal, Quebec, Canada.
Department of Psychiatry, McGill University Health Centre, McGill University, Montreal, Quebec, Canada.

Maria Carmela Tartaglia (MC)

Tanz Centre for Research in Neurodegenerative Diseases, University of Toronto, Toronto Ontario, Canada.

Elizabeth Finger (E)

Department of Clinical Neurological Sciences, University of Western Ontario, London, Ontario, Canada.

Alexandre de Mendonça (A)

Department of Neurology and Laboratory of Neurosciences, Faculty of Medicine, University of Lisbon, Lisbon, Portugal.

Isabel Santana (I)

Center for Neuroscience and Cell Biology, Faculty of Medicine, Centro Hospitalar e Universitário de Coimbra, Portugal.
Center for Neuroscience and Cell Biology, Faculty of Medicine, University of Coimbra, Coimbra, Portugal.

Raquel Sanchez-Valle (R)

Alzheimer's Disease and Other Cognitive Disorders Unit, Neurology Service, Hospital Clinic, Institut d'Investigacions Biomediques August Pi I Sunyer, Barcelona, Spain.
Institut d'Investigació Biomèdica August Pi I Sunyer, Barcelona, Spain.

Fermin Moreno (F)

Department of Neurology, Donostio University Hospital, San Sebastian, Gipuzkoa, Spain.
Neuroscience Area, Biodonostia Health Research Institute, San Sebastian, Gipuzkoa, Spain.

Sandro Sorbi (S)

Department of Neuroscience, Psychology, Drug Research and Child Health, University of Florence, Florence, Italy.
IRCCS Fondazione Don Carlo Gnocchi, Florence, Italy.

Fabrizio Tagliavini (F)

Fondazione Istituto di Ricovero e Cura a Carattere Scientifico Istituto Neurologica Carlo Besta, Milano, Italy.

Barbara Borroni (B)

Centre for Neurodegenerative Disorders, Neurology Unit, Department of Clinical and Experimental Sciences, University of Brescia, Brescia, Italy.

Markus Otto (M)

Department of Neurology, University Hospital Ulm, Ulm, Germany.

Matthis Synofzik (M)

Department of Neurodegenerative Diseases, Hertie-Institute for Clinical Brain Research and Center of Neurology, University of Tübingen, Tübingen, Germany.
Center for Neurodegenerative Diseases, Tübingen, Germany.

Daniela Galimberti (D)

Fondazione IRCCS Ospediale Policlinico, Milan, Italy.
University of Milan, Centro Dino Ferrari, Milan, Italy.

Rik Vandenberghe (R)

Leuven Brain Institute (LBI), KU Leuven, Leuven, Belgium.
Laboratory for Cognitive Neurology, Department of Neurosciences, KU Leuven, Leuven, Belgium.
Neurology Department, UZ Leuven, Leuven, Belgium.

John van Swieten (J)

Department of Neurology, Erasmus Medical Centre, Rotterdam, the Netherlands.

Christopher Butler (C)

Nuffield Department of Clinical Neurosciences, Medical Sciences Division, University of Oxford, Oxford, UK.
Department of Brain Sciences, Imperial College London, UK.

Alexander Gerhard (A)

Wolfson Molecular Imaging Centre, Faculty of Medicine, Biology and Health, University of Manchester, Manchester, United Kingdom.
Departments of Geriatric Medicine and Nuclear Medicine, Essen University Hospital, Essen, Germany.

Caroline Graff (C)

Swedish FTD Initiative, Stockholm, Sweden.
Division of Neurogeriatrics, Centre for Alzheimer Research, Department of Neurobiology, Care Sciences and Society, Karolinska Institutet Solna, Sweden.
Unit for hereditary dementias, Theme Aging, Karolinska University Hospital, Stockholm, Sweden.

Adrian Danek (A)

Department of Neurology, Ludwig-Maximilians-Universität München, Munich, Germany.

Jonathan D Rohrer (JD)

Dementia Research Centre, University College London, London, United Kingdom.

Mario Masellis (M)

Hurvitz Brain Sciences Program, Sunnybrook Research Institute, University of Toronto, Toronto, Canada.
Division of Neurology, Department of Medicine, University of Toronto, Toronto, Canada.
Cognitive and Movement Disorders Clinic, Sunnybrook Health Sciences Centre, Toronto, Canada.

James Rowe (J)

Medical Research Council, Cognition and Brain Sciences Unit, Cambridge, United Kingdom.
Department of Clinical Neurosciences, University of Cambridge, Cambridge, United Kingdom.
Cambridge University Hospitals NHS Trust, Cambridge, United Kingdom.

Johannes Levin (J)

Department of Neurology, Ludwig-Maximilians-Universität München, Munich, Germany 46465jlevin@med.uni-muenchen.de.
German Center for Neurodegenerative Diseases (DZNE), Munich, Germany.
Munich Cluster for Systems Neurology (SyNergy), Munich, Germany.
European Reference Network for Rare Neurological Diseases (ERN-RND), Munich, Germany.

Classifications MeSH