Abnormal B-Cell Maturation and Increased Transitional B Cells in CBL Syndrome.

ALPS BENTA CARD11 CBL RALD RASopathies lymphocytosis splenomegaly

Journal

Frontiers in pediatrics
ISSN: 2296-2360
Titre abrégé: Front Pediatr
Pays: Switzerland
ID NLM: 101615492

Informations de publication

Date de publication:
2022
Historique:
received: 04 05 2022
accepted: 17 06 2022
entrez: 15 8 2022
pubmed: 16 8 2022
medline: 16 8 2022
Statut: epublish

Résumé

CBL syndrome is a Noonan-like RASopathy with heterogeneous clinical phenotype and predisposition to juvenile myelomonocytic leukemia (JMML). Here we describe two patients with identical germline

Identifiants

pubmed: 35967575
doi: 10.3389/fped.2022.935951
pmc: PMC9366004
doi:

Types de publication

Case Reports

Langues

eng

Pagination

935951

Informations de copyright

Copyright © 2022 Saettini, Coliva, Vendemini, Galbiati, Bugarin, Masetti, Moratto, Chiarini, Guerra, Iascone, Badolato, Cazzaniga, Niemeyer, Flotho and Biondi.

Déclaration de conflit d'intérêts

The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.

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Auteurs

Francesco Saettini (F)

Department of Pediatric Hematology, Fondazione Monza e Brianza per il Bambino e la sua Mamma (MBBM), University of Milano Bicocca, Monza, Italy.

Tiziana Angela Coliva (TA)

Department of Pediatric Hematology, Fondazione Monza e Brianza per il Bambino e la sua Mamma (MBBM), University of Milano Bicocca, Monza, Italy.

Francesca Vendemini (F)

Department of Pediatric Hematology, Fondazione Monza e Brianza per il Bambino e la sua Mamma (MBBM), University of Milano Bicocca, Monza, Italy.

Marta Galbiati (M)

Centro Ricerca Tettamanti, University of Milano Bicocca, Monza, Italy.

Cristina Bugarin (C)

Centro Ricerca Tettamanti, University of Milano Bicocca, Monza, Italy.

Riccardo Masetti (R)

Pediatric Hematology-Oncology Unit, Department of Medical and Surgical Sciences (DIMEC), University of Bologna, Bologna, Italy.

Daniele Moratto (D)

Flow Cytometry, Clinical Chemistry Laboratory, Brescia, Italy.

Marco Chiarini (M)

Flow Cytometry, Clinical Chemistry Laboratory, Brescia, Italy.

Fabiola Guerra (F)

Department of Pediatric Hematology, Fondazione Monza e Brianza per il Bambino e la sua Mamma (MBBM), University of Milano Bicocca, Monza, Italy.
Centro Ricerca Tettamanti, University of Milano Bicocca, Monza, Italy.

Maria Iascone (M)

Laboratorio di Genetica Medica, Azienda Socio Sanitaria Territoriale (ASST) Papa Giovanni XXIII, Bergamo, Italy.

Raffaele Badolato (R)

Department of Clinical and Experimental Sciences, Pediatrics Clinic and Institute for Molecular Medicine A. Nocivelli, University of Brescia and ASST-Spedali Civili of Brescia, Brescia, Italy.

Giovanni Cazzaniga (G)

Centro Ricerca Tettamanti, University of Milano Bicocca, Monza, Italy.

Charlotte Niemeyer (C)

Department of Pediatrics and Adolescent Medicine, University Children's Hospital, University of Freiburg, Freiburg, Germany.

Christian Flotho (C)

Department of Pediatrics and Adolescent Medicine, University Children's Hospital, University of Freiburg, Freiburg, Germany.

Andrea Biondi (A)

Pediatric Department and Centro Tettamanti-European Reference Network PaedCan, EuroBloodNet, MetabERN-University of Milano-Bicocca-Fondazione Monza e Brianza per il Bambino e la sua Mamma (MBBM)-Ospedale, San Gerardo, Monza, Italy.

Classifications MeSH