Leber Hereditary Optic Neuropathy: Molecular Pathophysiology and Updates on Gene Therapy.
gene therapy
leber hereditary optic neuropathy
molecular pathophysiology
Journal
Biomedicines
ISSN: 2227-9059
Titre abrégé: Biomedicines
Pays: Switzerland
ID NLM: 101691304
Informations de publication
Date de publication:
09 Aug 2022
09 Aug 2022
Historique:
received:
24
06
2022
revised:
29
07
2022
accepted:
04
08
2022
entrez:
26
8
2022
pubmed:
27
8
2022
medline:
27
8
2022
Statut:
epublish
Résumé
Molecular pathophysiology of LHON was reviewed and the current status of gene therapy for LHON is updated.
Identifiants
pubmed: 36009477
pii: biomedicines10081930
doi: 10.3390/biomedicines10081930
pmc: PMC9405679
pii:
doi:
Types de publication
Journal Article
Review
Langues
eng
Déclaration de conflit d'intérêts
A.G.W was the PI of the REFLECT trial. H.C.C was the co-PI of the REFLECT trial.
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