Comprehensive genetic testing approaches as the basis for personalized management of growth disturbances: current status and perspectives.

genetic testing genome medicine growth disturbances growth retardation interdisciplinary clinical management overgrowth

Journal

Endocrine connections
ISSN: 2049-3614
Titre abrégé: Endocr Connect
Pays: England
ID NLM: 101598413

Informations de publication

Date de publication:
01 Nov 2022
Historique:
received: 30 08 2022
accepted: 05 09 2022
pubmed: 6 9 2022
medline: 6 9 2022
entrez: 5 9 2022
Statut: epublish

Résumé

The implementation of high-throughput and deep sequencing methods in routine genetic diagnostics has significantly improved the diagnostic yield in patient cohorts with growth disturbances and becomes increasingly important as the prerequisite of personalized medicine. They provide considerable chances to identify even rare and unexpected situations; nevertheless, we must be aware of their limitations. A simple genetic test in the beginning of a testing cascade might also help to identify the genetic cause of specific growth disorders. However, the clinical picture of genetically caused growth disturbance phenotypes can vary widely, and there is a broad clinical overlap between different growth disturbance disorders. As a consequence, the clinical diagnosis and therewith connected the decision on the appropriate genetic test is often a challenge. In fact, the clinician asking for genetic testing has to weigh different aspects in this decision process, including appropriateness (single gene test, stepwise procedure, comprehensive testing), turnaround time as the basis for rapid intervention, and economic considerations. Therefore, a frequent question in that context is 'what to test when'. In this review, we aim to review genetic testing strategies and their strengths and limitations and to raise awareness for the future implementation of interdisciplinary genome medicine in diagnoses, treatment, and counselling of growth disturbances.

Identifiants

pubmed: 36064195
doi: 10.1530/EC-22-0277
pii: e220277
pmc: PMC9578069
doi:
pii:

Types de publication

Journal Article Review

Langues

eng

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Auteurs

Danielle Christine Maria van der Kaay (DCM)

Erasmus University Medical Center, Department of Pediatrics, Subdivision of Endocrinology, Rotterdam, Netherlands.

Anne Rochtus (A)

Department of Pediatric Endocrinology, University Hospitals Leuven, Leuven, Belgium.

Gerhard Binder (G)

University Children's Hospital, Pediatric Endocrinology, University of Tübingen, Tübingen, Germany.

Ingo Kurth (I)

Institute of Human Genetics, Medical Faculty, RWTH Aachen University, Aachen, Germany.

Dirk Prawitt (D)

Center for Paediatrics and Adolescent Medicine, University Medical Center, Mainz, Germany.

Irène Netchine (I)

Sorbonne Université, Centre de Recherche Saint-Antoine, INSERM, Assistance Publique-Hôpitaux de Paris (AP-HP), Paris, France.

Gudmundur Johannsson (G)

Department of Internal Medicine and Clinical Nutrition, Institute of Medicine, Sahlgrenska Academy, University of Gothenburg, Gothenburg, Sweden.
Department of Endocrinology at Sahlgrenska University Hospital, Gothenburg, Sweden.

Anita C S Hokken-Koelega (ACS)

Erasmus University Medical Center, Department of Pediatrics, Subdivision of Endocrinology, Rotterdam, Netherlands.

Miriam Elbracht (M)

Institute of Human Genetics, Medical Faculty, RWTH Aachen University, Aachen, Germany.

Thomas Eggermann (T)

Institute of Human Genetics, Medical Faculty, RWTH Aachen University, Aachen, Germany.

Classifications MeSH