AAV-monoclonal antibody expression protects mice from Ebola virus without impeding the endogenous antibody response to heterologous challenge.

AAV6.2FF Ebola adeno-associated virus (AAV) filovirus immunotherapy monoclonal antibody vectored immunoprophylaxis

Journal

Molecular therapy. Methods & clinical development
ISSN: 2329-0501
Titre abrégé: Mol Ther Methods Clin Dev
Pays: United States
ID NLM: 101624857

Informations de publication

Date de publication:
08 Sep 2022
Historique:
received: 26 01 2022
accepted: 09 08 2022
entrez: 12 9 2022
pubmed: 13 9 2022
medline: 13 9 2022
Statut: epublish

Résumé

Filoviruses cause severe hemorrhagic fever with case fatality rates as high as 90%. Filovirus-specific monoclonal antibodies (mAbs) confer protection in nonhuman primates as late as 5 days after challenge, and FDA-approved mAbs REGN-EB3 and mAb114 have demonstrated efficacy against Ebola virus (EBOV) infection in humans. Vectorized antibody expression mediated by adeno-associated virus (AAV) can generate protective and sustained concentrations of therapeutic mAbs in animal models for a variety of infectious diseases, including EBOV. Here we demonstrate that AAV6.2FF-mediated expression of murine IgG2a EBOV mAbs, 2G4 and 5D2, protects from mouse-adapted (MA)-EBOV infection with none of the surviving mice developing anti-VP40 antibodies above background. Protective serum concentrations of AAV6.2FF-2G4/AAV6.2FF-5D2 did not alter endogenous antibody responses to heterologous virus infection. AAV-mediated expression of EBOV mAbs 100 and 114, and pan-ebolavirus mAbs, FVM04, ADI-15878, and CA45, as human IgG1 antibodies conferred protection against MA-EBOV at low serum concentrations, with minimum protective serum levels as low as 2 μg/mL. Vectorized expression of murine IgG2a or human IgG1 mAbs led to sustained expression in the serum of mice for >400 days or for the lifetime of the animal, respectively. AAV6.2FF-mediated mAb expression offers an alternative to recombinant antibody administration in scenarios where long-term protection is preferable to passive immunization.

Identifiants

pubmed: 36092367
doi: 10.1016/j.omtm.2022.08.003
pii: S2329-0501(22)00113-9
pmc: PMC9436706
doi:

Types de publication

Journal Article

Langues

eng

Pagination

505-518

Informations de copyright

© 2022 The Author(s).

Déclaration de conflit d'intérêts

L.P.L. and S.K.W. are inventors on a US patent for the AAV6.2FF capsid. This patent (US20190216949) is licensed to Avamab Pharma Inc., where B.T., L.P.L., and S.K.W. are co-founders and B.T. serves as an executive. The funders had no role in the design of the study; in the collection, analyses, or interpretation of data; in the writing of the manuscript; nor in the decision to publish the results.

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Auteurs

Laura P van Lieshout (LP)

Department of Pathobiology, University of Guelph, Guelph, ON N1G 2W1, Canada.

Amira D Rghei (AD)

Department of Pathobiology, University of Guelph, Guelph, ON N1G 2W1, Canada.

Wenguang Cao (W)

Special Pathogens Program, National Microbiology Laboratory, Public Health Agency of Canada, 1015 Arlington Street, Winnipeg, MB R3E 3R2, Canada.

Shihua He (S)

Special Pathogens Program, National Microbiology Laboratory, Public Health Agency of Canada, 1015 Arlington Street, Winnipeg, MB R3E 3R2, Canada.

Geoff Soule (G)

Special Pathogens Program, National Microbiology Laboratory, Public Health Agency of Canada, 1015 Arlington Street, Winnipeg, MB R3E 3R2, Canada.

Wenjun Zhu (W)

Special Pathogens Program, National Microbiology Laboratory, Public Health Agency of Canada, 1015 Arlington Street, Winnipeg, MB R3E 3R2, Canada.

Sylvia P Thomas (SP)

Department of Pathobiology, University of Guelph, Guelph, ON N1G 2W1, Canada.

Debra Sorensen (D)

Molecular Pathobiology, National Microbiology Laboratory, Public Health Agency of Canada, 1015 Arlington Street, Winnipeg, MB R3E 3R2, Canada.

Kathy Frost (K)

Molecular Pathobiology, National Microbiology Laboratory, Public Health Agency of Canada, 1015 Arlington Street, Winnipeg, MB R3E 3R2, Canada.

Kevin Tierney (K)

Special Pathogens Program, National Microbiology Laboratory, Public Health Agency of Canada, 1015 Arlington Street, Winnipeg, MB R3E 3R2, Canada.

Brad Thompson (B)

Avamab Pharma Inc., 1646 Acton Avenue SW, Calgary, AB T2T 2P9, Canada.

Stephanie Booth (S)

Molecular Pathobiology, National Microbiology Laboratory, Public Health Agency of Canada, 1015 Arlington Street, Winnipeg, MB R3E 3R2, Canada.
Department of Medical Microbiology, University of Manitoba, Winnipeg, MB R3T 2N2, Canada.

David Safronetz (D)

Special Pathogens Program, National Microbiology Laboratory, Public Health Agency of Canada, 1015 Arlington Street, Winnipeg, MB R3E 3R2, Canada.
Department of Medical Microbiology, University of Manitoba, Winnipeg, MB R3T 2N2, Canada.

Raveendra R Kulkarni (RR)

Department of Pathobiology, University of Guelph, Guelph, ON N1G 2W1, Canada.
Department of Pathobiology and Population Health, North Carolina State University, Raleigh, NC 27695, USA.

Byram W Bridle (BW)

Department of Pathobiology, University of Guelph, Guelph, ON N1G 2W1, Canada.

Xiangguo Qiu (X)

Special Pathogens Program, National Microbiology Laboratory, Public Health Agency of Canada, 1015 Arlington Street, Winnipeg, MB R3E 3R2, Canada.

Logan Banadyga (L)

Special Pathogens Program, National Microbiology Laboratory, Public Health Agency of Canada, 1015 Arlington Street, Winnipeg, MB R3E 3R2, Canada.

Sarah K Wootton (SK)

Department of Pathobiology, University of Guelph, Guelph, ON N1G 2W1, Canada.

Classifications MeSH