Neurofibromatosis Type 1 and Hypospadias in a Male 46, XY with a Mutation in the

Colombia cafe-au-lait macules external genitalia development tumor predisposition syndrome

Journal

Pharmacogenomics and personalized medicine
ISSN: 1178-7066
Titre abrégé: Pharmgenomics Pers Med
Pays: New Zealand
ID NLM: 101514107

Informations de publication

Date de publication:
2022
Historique:
received: 01 07 2022
accepted: 22 09 2022
entrez: 1 11 2022
pubmed: 2 11 2022
medline: 2 11 2022
Statut: epublish

Résumé

Neurofibromatosis type 1 is one of the most common genetic autosomal dominant disorders described, with a prevalence of 1 in 2000 to 1 in 3000 individuals. It is characterized by skin, nerves, and bone abnormalities. Non-related to NF1, hypospadias is a displacement in the urethral opening which in the majority of patients has an idiopathic cause. Here, we describe a patient with neurofibromatosis type 1, hypospadias, and unilateral cryptorchidism. The heterozygous variants c.6789_6792delTTAC, p.(Tyr2264Thrfs*5) and c.140A>G, p.(Tyr47Cys) were found in the

Identifiants

pubmed: 36317063
doi: 10.2147/PGPM.S380796
pii: 380796
pmc: PMC9617560
doi:

Types de publication

Case Reports

Langues

eng

Pagination

873-878

Informations de copyright

© 2022 Perafan-Valdes et al.

Déclaration de conflit d'intérêts

The authors have no conflicts of interest in relation to this work to declare.

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Auteurs

Lina Perafan-Valdes (L)

Universidad Libre, Programa de Maestría en Epidemiología, Cali, Colombia.
Fundación Valle del Lili, Genetics Division, Cali, Colombia.

Sebastian Giraldo-Ocampo (S)

Universidad del Valle, Departamento de Microbiología, Cali, Colombia.

Juliana Lores (J)

Fundación Valle del Lili, Genetics Division, Cali, Colombia.

Harry Pachajoa (H)

Fundación Valle del Lili, Genetics Division, Cali, Colombia.
Universidad Icesi, Centro de Investigaciones en Anomalías Congénitas y Enfermedades Raras (CIACER), Cali, Colombia.

Classifications MeSH