Creation and preclinical evaluation of genetically attenuated malaria parasites arresting growth late in the liver.


Journal

NPJ vaccines
ISSN: 2059-0105
Titre abrégé: NPJ Vaccines
Pays: England
ID NLM: 101699863

Informations de publication

Date de publication:
04 Nov 2022
Historique:
received: 23 03 2022
accepted: 13 10 2022
pubmed: 6 11 2022
medline: 6 11 2022
entrez: 5 11 2022
Statut: epublish

Résumé

Whole-sporozoite (WSp) malaria vaccines induce protective immune responses in animal malaria models and in humans. A recent clinical trial with a WSp vaccine comprising genetically attenuated parasites (GAP) which arrest growth early in the liver (PfSPZ-GA1), showed that GAPs can be safely administered to humans and immunogenicity is comparable to radiation-attenuated PfSPZ Vaccine. GAPs that arrest late in the liver stage (LA-GAP) have potential for increased potency as shown in rodent malaria models. Here we describe the generation of four putative P. falciparum LA-GAPs, generated by CRISPR/Cas9-mediated gene deletion. One out of four gene-deletion mutants produced sporozoites in sufficient numbers for further preclinical evaluation. This mutant, PfΔmei2, lacking the mei2-like RNA gene, showed late liver growth arrest in human liver-chimeric mice with human erythrocytes, absence of unwanted genetic alterations and sensitivity to antimalarial drugs. These features of PfΔmei2 make it a promising vaccine candidate, supporting further clinical evaluation. PfΔmei2 (GA2) has passed regulatory approval for safety and efficacy testing in humans based on the findings reported in this study.

Identifiants

pubmed: 36333336
doi: 10.1038/s41541-022-00558-x
pii: 10.1038/s41541-022-00558-x
pmc: PMC9636417
doi:

Types de publication

Journal Article

Langues

eng

Pagination

139

Informations de copyright

© 2022. The Author(s).

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Auteurs

Blandine Franke-Fayard (B)

Malaria Research Group, Department of Parasitology, Leiden University medical Center, Leiden, The Netherlands. bfranke@lumc.nl.

Catherin Marin-Mogollon (C)

Malaria Research Group, Department of Parasitology, Leiden University medical Center, Leiden, The Netherlands.

Fiona J A Geurten (FJA)

Malaria Research Group, Department of Parasitology, Leiden University medical Center, Leiden, The Netherlands.

Séverine Chevalley-Maurel (S)

Malaria Research Group, Department of Parasitology, Leiden University medical Center, Leiden, The Netherlands.

Jai Ramesar (J)

Malaria Research Group, Department of Parasitology, Leiden University medical Center, Leiden, The Netherlands.

Hans Kroeze (H)

Malaria Research Group, Department of Parasitology, Leiden University medical Center, Leiden, The Netherlands.

Els Baalbergen (E)

Malaria Research Group, Department of Parasitology, Leiden University medical Center, Leiden, The Netherlands.

Els Wessels (E)

Department of Medical Microbiology, Leiden University Medical Center, 2300 RC, Leiden, the Netherlands.

Ludivine Baron (L)

Sorbonne Université, Institut National de la Santé et de la Recherche Médicale (INSERM), Centre National pour la Recherche Scientifique (CNRS), Centre d'Immunologie et des Maladies Infectieuses, CIMI, Paris, France.

Valérie Soulard (V)

Sorbonne Université, Institut National de la Santé et de la Recherche Médicale (INSERM), Centre National pour la Recherche Scientifique (CNRS), Centre d'Immunologie et des Maladies Infectieuses, CIMI, Paris, France.

Thomas Martinson (T)

Vaccine and Gene Therapy Institute, Oregon Health and Science University, Beaverton, OR, 97006, USA.

Maya Aleshnick (M)

Vaccine and Gene Therapy Institute, Oregon Health and Science University, Beaverton, OR, 97006, USA.

Antonius T G Huijs (ATG)

TropIQ Health Sciences, Nijmegen, the Netherlands.

Amit K Subudhi (AK)

Pathogen Genomics Laboratory, Biological and Environmental Sciences and Engineering (BESE) Division, King Abdullah University of Science and Technology (KAUST), Thuwal, Kingdom of Saudi Arabia.

Yukiko Miyazaki (Y)

Malaria Research Group, Department of Parasitology, Leiden University medical Center, Leiden, The Netherlands.
Department of Cellular Architecture Studies, Institute of Tropical Medicine, Nagasaki University, Nagasaki, Japan.

Ahmad Syibli Othman (AS)

Universiti Sultan Zainal Abidin, Faculty of Health Sciences, Terengganu, Malaysia.

Surendra Kumar Kolli (SK)

Malaria Research Group, Department of Parasitology, Leiden University medical Center, Leiden, The Netherlands.
Center for Global Health and Infectious Diseases Research, College of Public Health, University of South Florida, Tampa, FL, USA.

Olivia A C Lamers (OAC)

Malaria Research Group, Department of Parasitology, Leiden University medical Center, Leiden, The Netherlands.

Magali Roques (M)

Institute of Cell Biology, University of Bern, Bern, Switzerland.

Rebecca R Stanway (RR)

Institute of Cell Biology, University of Bern, Bern, Switzerland.
Multidisciplinary Center for Infectious Diseases (MCID), University of Bern, Bern, Switzerland.

Sean C Murphy (SC)

Department of Laboratory Medicine and Pathology, University of Washington, Seattle, WA, USA.

Lander Foquet (L)

Yecuris Corporation, Tualatin, OR, USA.

Diana Moita (D)

Instituto de Medicina Molecular João Lobo Antunes, Faculdade de Medicina, Universidade de Lisboa, Lisboa, Portugal.

António M Mendes (AM)

Instituto de Medicina Molecular João Lobo Antunes, Faculdade de Medicina, Universidade de Lisboa, Lisboa, Portugal.

Miguel Prudêncio (M)

Instituto de Medicina Molecular João Lobo Antunes, Faculdade de Medicina, Universidade de Lisboa, Lisboa, Portugal.

Koen J Dechering (KJ)

TropIQ Health Sciences, Nijmegen, the Netherlands.

Volker T Heussler (VT)

Institute of Cell Biology, University of Bern, Bern, Switzerland.

Arnab Pain (A)

Pathogen Genomics Laboratory, Biological and Environmental Sciences and Engineering (BESE) Division, King Abdullah University of Science and Technology (KAUST), Thuwal, Kingdom of Saudi Arabia.
International Institute for Zoonosis Control, Hokkaido University, N20 W10 Kita-ku, Sapporo, Japan.

Brandon K Wilder (BK)

Vaccine and Gene Therapy Institute, Oregon Health and Science University, Beaverton, OR, 97006, USA.

Meta Roestenberg (M)

Malaria Research Group, Department of Parasitology, Leiden University medical Center, Leiden, The Netherlands. M.Roestenberg@lumc.nl.
Department of Infectious Diseases, Leiden University Medical Center, Leiden, The Netherlands. M.Roestenberg@lumc.nl.

Chris J Janse (CJ)

Malaria Research Group, Department of Parasitology, Leiden University medical Center, Leiden, The Netherlands. c.j.janse@lumc.nl.

Classifications MeSH