Natural history of propionic acidemia in the Amish population.

Amish Cardiomyopathy Newborn screen Propionic Acidemia Seizures Treatment

Journal

Molecular genetics and metabolism reports
ISSN: 2214-4269
Titre abrégé: Mol Genet Metab Rep
Pays: United States
ID NLM: 101624422

Informations de publication

Date de publication:
Dec 2022
Historique:
received: 13 07 2022
revised: 25 10 2022
accepted: 30 10 2022
entrez: 17 11 2022
pubmed: 18 11 2022
medline: 18 11 2022
Statut: epublish

Résumé

Propionic acidemia (PA) in the Amish is caused by a homozygous pathogenic variant (c.1606A>G; p.Asn536Asp) in the

Identifiants

pubmed: 36393899
doi: 10.1016/j.ymgmr.2022.100936
pii: S2214-4269(22)00096-9
pmc: PMC9647228
doi:

Types de publication

Journal Article

Langues

eng

Pagination

100936

Subventions

Organisme : NHGRI NIH HHS
ID : K08 HG010490
Pays : United States

Informations de copyright

© 2022 The Authors.

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Auteurs

Sarah Ehrenberg (S)

University of Pittsburgh, School of Medicine, Pittsburgh, PA, USA.
Division of Genetic and Genomic Medicine, Department of Pediatrics, University of Pittsburgh, PA, USA.

Catherine Walsh Vockley (C)

Division of Genetic and Genomic Medicine, Department of Pediatrics, University of Pittsburgh, PA, USA.
Department of Human Genetics, Graduate School of Public Health, University of Pittsburgh, PA, USA.

Paige Heiman (P)

Division of Genetic and Genomic Medicine, Department of Pediatrics, University of Pittsburgh, PA, USA.

Zineb Ammous (Z)

The Community Health Clinic, Topeka, IN, USA.

Olivia Wenger (O)

New Leaf Center, Mount Eaton, OH, USA.
Department of Pediatrics, Akron Children's Hospital, 214 West Bowery Street, Akron, OH 44308, USA.

Jerry Vockley (J)

Division of Genetic and Genomic Medicine, Department of Pediatrics, University of Pittsburgh, PA, USA.
Department of Human Genetics, Graduate School of Public Health, University of Pittsburgh, PA, USA.

Lina Ghaloul-Gonzalez (L)

Division of Genetic and Genomic Medicine, Department of Pediatrics, University of Pittsburgh, PA, USA.
Department of Human Genetics, Graduate School of Public Health, University of Pittsburgh, PA, USA.

Classifications MeSH