Detection and evolutionary dynamics of somatic FAS variants in autoimmune lymphoproliferative syndrome: Diagnostic implications.

FAS autoimmune lymphoproliferative syndrome genetics inborn errors of immunity next-generation sequencing primary immunodeficiencies somatic mutation

Journal

Frontiers in immunology
ISSN: 1664-3224
Titre abrégé: Front Immunol
Pays: Switzerland
ID NLM: 101560960

Informations de publication

Date de publication:
2022
Historique:
received: 09 08 2022
accepted: 24 10 2022
entrez: 5 12 2022
pubmed: 6 12 2022
medline: 7 12 2022
Statut: epublish

Résumé

Autoimmune lymphoproliferative syndrome (ALPS) is a rare primary immune disorder characterized by impaired apoptotic homeostasis. The clinical characteristics include lymphoproliferation, autoimmunity (mainly cytopenia), and an increased risk of lymphoma. A distinctive biological feature is accumulation (>2.5%) of an abnormal cell subset composed of TCRαβ

Identifiants

pubmed: 36466883
doi: 10.3389/fimmu.2022.1014984
pmc: PMC9716137
doi:

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

1014984

Informations de copyright

Copyright © 2022 Batlle-Masó, Garcia-Prat, Parra-Martínez, Franco-Jarava, Aguiló-Cucurull, Velasco, Antolín, Rivière, Martín-Nalda, Soler-Palacín, Martínez-Gallo and Colobran.

Déclaration de conflit d'intérêts

The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.

Références

Ann Hematol. 2022 Mar;101(3):469-484
pubmed: 35059842
Am J Hum Genet. 2010 Dec 10;87(6):873-81
pubmed: 21109225
Cell. 1995 Jun 16;81(6):935-46
pubmed: 7540117
Blood. 2011 Nov 3;118(18):4798-807
pubmed: 21885602
Immunobiology. 2016 Jan;221(1):40-7
pubmed: 26323380
Blood. 2006 Aug 15;108(4):1306-12
pubmed: 16627752
J Clin Immunol. 2018 Jul;38(5):558-568
pubmed: 29911256
Nature. 2009 Feb 19;457(7232):1019-22
pubmed: 19118384
Blood. 2010 Jun 24;115(25):5164-9
pubmed: 20360470
N Engl J Med. 2004 Sep 30;351(14):1409-18
pubmed: 15459302
Sci Rep. 2017 Feb 24;7:43169
pubmed: 28233799
Nature. 2002 Sep 26;419(6905):395-9
pubmed: 12353035
Clin Immunol. 2021 Sep;230:108812
pubmed: 34329798
J Clin Immunol. 2021 May;41(4):718-728
pubmed: 33864184
Proc Natl Acad Sci U S A. 2007 May 22;104(21):8953-8
pubmed: 17517660
PLoS One. 2016 Mar 22;11(3):e0151664
pubmed: 27002637
F1000Res. 2017 Nov 1;6:1928
pubmed: 29123652
Haematologica. 2013 Mar;98(3):389-92
pubmed: 22983577
Blood. 1997 Feb 1;89(3):902-9
pubmed: 9028321
Trends Genet. 2019 Dec;35(12):935-947
pubmed: 31668909
N Engl J Med. 2020 Dec 31;383(27):2628-2638
pubmed: 33108101
Blood. 2021 May 6;137(18):2450-2462
pubmed: 33512449
J Pediatr. 2005 Nov;147(5):691-4
pubmed: 16291365
J Allergy Clin Immunol. 2019 Jan;143(1):359-368
pubmed: 30273710
Cell. 1999 Jul 9;98(1):47-58
pubmed: 10412980
Curr Opin Pediatr. 2013 Dec;25(6):722-9
pubmed: 24240292
Science. 1995 Jun 2;268(5215):1347-9
pubmed: 7539157
Curr Opin Immunol. 2017 Dec;49:79-86
pubmed: 29073495
Haematologica. 2017 Feb;102(2):e52-e56
pubmed: 27789675
J Clin Invest. 2011 Jan;121(1):106-12
pubmed: 21183795
Blood. 2016 Jan 7;127(1):17-28
pubmed: 26504182
Nat Genet. 2016 Jan;48(1):4-6
pubmed: 26711108
Sci Rep. 2021 Jun 21;11(1):12940
pubmed: 34155260
Front Immunol. 2021 Apr 29;12:656356
pubmed: 33995372
Comput Struct Biotechnol J. 2018 Feb 06;16:15-24
pubmed: 29552334
Am J Hum Genet. 1999 Apr;64(4):1002-14
pubmed: 10090885
Rheumatology (Oxford). 2022 Aug 3;61(8):3149-3160
pubmed: 34888629
Blood. 2011 Nov 24;118(22):5741-51
pubmed: 21885601
Blood. 2010 Oct 7;116(14):e35-40
pubmed: 20538792

Auteurs

Laura Batlle-Masó (L)

Infection in Immunocompromised Pediatric Patients Research Group, Vall d'Hebron Research Institute (VHIR), Barcelona, Spain.
Pediatric Infectious Diseases and Immunodeficiencies Unit, Vall d'Hebron University Hospital (HUVH), Barcelona, Spain.
Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.

Marina Garcia-Prat (M)

Infection in Immunocompromised Pediatric Patients Research Group, Vall d'Hebron Research Institute (VHIR), Barcelona, Spain.
Pediatric Infectious Diseases and Immunodeficiencies Unit, Vall d'Hebron University Hospital (HUVH), Barcelona, Spain.
Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.

Alba Parra-Martínez (A)

Infection in Immunocompromised Pediatric Patients Research Group, Vall d'Hebron Research Institute (VHIR), Barcelona, Spain.
Pediatric Infectious Diseases and Immunodeficiencies Unit, Vall d'Hebron University Hospital (HUVH), Barcelona, Spain.
Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.

Clara Franco-Jarava (C)

Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.
Translational Immunology Group, Vall d'Hebron Research Institute (VHIR), Barcelona, Spain.
Immunology Division, Vall d'Hebron University Hospital (HUVH), Barcelona, Spain.

Aina Aguiló-Cucurull (A)

Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.
Translational Immunology Group, Vall d'Hebron Research Institute (VHIR), Barcelona, Spain.
Immunology Division, Vall d'Hebron University Hospital (HUVH), Barcelona, Spain.

Pablo Velasco (P)

Pediatric Oncology and Hematology Department, Vall d'Hebron University Hospital (HUVH), Barcelona, Spain.

María Antolín (M)

Department of Clinical and Molecular Genetics, Vall d'Hebron University Hospital (HUVH), Barcelona, Spain.

Jacques G Rivière (JG)

Infection in Immunocompromised Pediatric Patients Research Group, Vall d'Hebron Research Institute (VHIR), Barcelona, Spain.
Pediatric Infectious Diseases and Immunodeficiencies Unit, Vall d'Hebron University Hospital (HUVH), Barcelona, Spain.
Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.

Andrea Martín-Nalda (A)

Infection in Immunocompromised Pediatric Patients Research Group, Vall d'Hebron Research Institute (VHIR), Barcelona, Spain.
Pediatric Infectious Diseases and Immunodeficiencies Unit, Vall d'Hebron University Hospital (HUVH), Barcelona, Spain.
Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.

Pere Soler-Palacín (P)

Infection in Immunocompromised Pediatric Patients Research Group, Vall d'Hebron Research Institute (VHIR), Barcelona, Spain.
Pediatric Infectious Diseases and Immunodeficiencies Unit, Vall d'Hebron University Hospital (HUVH), Barcelona, Spain.
Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.

Mónica Martínez-Gallo (M)

Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.
Translational Immunology Group, Vall d'Hebron Research Institute (VHIR), Barcelona, Spain.
Immunology Division, Vall d'Hebron University Hospital (HUVH), Barcelona, Spain.
Department of Cell Biology, Autonomous University of Barcelona (UAB), Physiology and Immunology, Bellaterra, Spain.

Roger Colobran (R)

Jeffrey Modell Diagnostic and Research Center for Primary Immunodeficiencies, Barcelona, Spain.
Translational Immunology Group, Vall d'Hebron Research Institute (VHIR), Barcelona, Spain.
Immunology Division, Vall d'Hebron University Hospital (HUVH), Barcelona, Spain.
Department of Clinical and Molecular Genetics, Vall d'Hebron University Hospital (HUVH), Barcelona, Spain.
Department of Cell Biology, Autonomous University of Barcelona (UAB), Physiology and Immunology, Bellaterra, Spain.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH