Adult-onset KMT2B-related dystonia.

DYT28 KMT2B dystonia genetics hearing loss

Journal

Brain communications
ISSN: 2632-1297
Titre abrégé: Brain Commun
Pays: England
ID NLM: 101755125

Informations de publication

Date de publication:
2022
Historique:
received: 14 02 2022
revised: 30 08 2022
accepted: 24 10 2022
entrez: 9 12 2022
pubmed: 10 12 2022
medline: 10 12 2022
Statut: epublish

Résumé

KMT2B-related dystonia (DYT-KMT2B, also known as DYT28) is an autosomal dominant neurological disorder characterized by varying combinations of generalized dystonia, psychomotor developmental delay, mild-to-moderate intellectual disability and short stature. Disease onset occurs typically before 10 years of age. We report the clinical and genetic findings of a series of subjects affected by adult-onset dystonia, hearing loss or intellectual disability carrying rare heterozygous

Identifiants

pubmed: 36483457
doi: 10.1093/braincomms/fcac276
pii: fcac276
pmc: PMC9724767
doi:

Types de publication

Journal Article

Langues

eng

Pagination

fcac276

Informations de copyright

© The Author(s) 2022. Published by Oxford University Press on behalf of the Guarantors of Brain.

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Auteurs

Edoardo Monfrini (E)

Dino Ferrari Center, Neuroscience Section, Department of Pathophysiology and Transplantation, University of Milan, Milan 20122, Italy.
Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Neurology Unit, Milan 20122, Italy.

Andrea Ciolfi (A)

Genetics and Rare Diseases Research Division, Ospedale Pediatrico Bambino Gesù, IRCCS, Rome 00146, Italy.

Francesco Cavallieri (F)

Neurology Unit, Neuromotor & Rehabilitation Department, Azienda USL-IRCCS di Reggio Emilia, Reggio Emilia 42124, Italy.
Clinical and Experimental Medicine PhD Program, University of Modena and Reggio Emilia, Reggio Emilia 42124, Italy.

Marco Ferilli (M)

Genetics and Rare Diseases Research Division, Ospedale Pediatrico Bambino Gesù, IRCCS, Rome 00146, Italy.

Paola Soliveri (P)

Parkinson Institute, ASST G. Pini-CTO, Milan 20126, Italy.
Fondazione Grigioni per il Morbo di Parkinson, Milan 20125, Italy.

Lucia Pedace (L)

Department of Onco-Hematology, Cell Therapy, Gene Therapy and Hemopoietic Transplant, Ospedale Pediatrico Bambino Gesù, IRCCS, Rome 00165, Italy.

Roberto Erro (R)

Department of Medicine, Surgery and Dentistry 'Scuola Medica Salernitana', Neuroscience Section, University of Salerno, Baronissi, SA 84081, Italy.

Francesca Del Sorbo (F)

Parkinson Institute, ASST G. Pini-CTO, Milan 20126, Italy.
Fondazione Grigioni per il Morbo di Parkinson, Milan 20125, Italy.

Franco Valzania (F)

Neurology Unit, Neuromotor & Rehabilitation Department, Azienda USL-IRCCS di Reggio Emilia, Reggio Emilia 42124, Italy.

Valentina Fioravanti (V)

Neurology Unit, Neuromotor & Rehabilitation Department, Azienda USL-IRCCS di Reggio Emilia, Reggio Emilia 42124, Italy.

Giovanni Cossu (G)

Department of Neuroscience, Brotzu Hospital, Cagliari 09047, Italy.

Maria Pellegrini (M)

Neurology Unit, Trento Hospital, Azienda Provinciale per i Servizi Sanitari (APSS) di Trento, Trento 38122, Italy.

Leonardo Salviati (L)

Clinical Genetics Unit, Department of Woman and Child Health, University of Padova, Padova 35131, Italy.

Federica Invernizzi (F)

Medical Genetics and Neurogenetics Unit, Fondazione IRCCS Istituto Neurologico C. Besta, Milano 20126, Italy.

Valentina Oppo (V)

Department of Neuroscience, Brotzu Hospital, Cagliari 09047, Italy.

Daniela Murgia (D)

Department of Neuroscience, Brotzu Hospital, Cagliari 09047, Italy.

Bruno Giometto (B)

Neurology Unit, Trento Hospital, Azienda Provinciale per i Servizi Sanitari (APSS) di Trento, Trento 38122, Italy.

Marina Picillo (M)

Department of Medicine, Surgery and Dentistry 'Scuola Medica Salernitana', Neuroscience Section, University of Salerno, Baronissi, SA 84081, Italy.

Barbara Garavaglia (B)

Medical Genetics and Neurogenetics Unit, Fondazione IRCCS Istituto Neurologico C. Besta, Milano 20126, Italy.

Francesca Morgante (F)

Neurosciences Research Centre, Molecular and Clinical Sciences Research Institute, St George's, University of London, London SW170RE, United Kingdom.
Department of Experimental and Clinical Medicine, University of Messina, Messina 98122, Italy.

Marco Tartaglia (M)

Genetics and Rare Diseases Research Division, Ospedale Pediatrico Bambino Gesù, IRCCS, Rome 00146, Italy.

Miryam Carecchio (M)

Parkinson disease and Movement Disorders Unit, Department of Neuroscience, University of Padua, Padua 35131, Italy.
Study Center for Neurodegeneration (CESNE), University of Padua, Padua 35131, Italy.

Alessio Di Fonzo (A)

Foundation IRCCS Ca' Granda Ospedale Maggiore Policlinico, Neurology Unit, Milan 20122, Italy.

Classifications MeSH