HER2DX ERBB2 mRNA expression in advanced HER2-positive breast cancer treated with T-DM1.


Journal

Journal of the National Cancer Institute
ISSN: 1460-2105
Titre abrégé: J Natl Cancer Inst
Pays: United States
ID NLM: 7503089

Informations de publication

Date de publication:
09 03 2023
Historique:
accepted: 27 10 2022
received: 26 07 2022
revised: 21 09 2022
pmc-release: 28 12 2023
pubmed: 29 12 2022
medline: 11 3 2023
entrez: 28 12 2022
Statut: ppublish

Résumé

In advanced HER2-positive (HER2+) breast cancer, the new antibody-drug conjugate trastuzumab deruxtecan is more effective compared with trastuzumab emtansine (T-DM1). However, trastuzumab deruxtecan can have considerable toxicities, and the right treatment sequence is unknown. Biomarkers to guide the use of anti-HER2 therapies beyond HER2 status are needed. Here, we evaluated if preestablished levels of ERBB2 mRNA expression according to the HER2DX standardized assay are associated with response and survival following T-DM1. In ERBB2 low, medium, and high groups, the overall response rate was 0%, 29%, and 56%, respectively (P < .001). ERBB2 mRNA was statistically significantly associated with better progression-free survival (P = .002) and overall survival (OS; P = .02). These findings were independent of HER2 immunohistochemistry (IHC) levels, hormone receptor, age, brain metastasis, and line of therapy. The HER2DX risk score (P = .04) and immunoglobulin signature (P = .04) were statistically significantly associated with overall survival since diagnosis. HER2DX provides prognostic and predictive information following T-DM1 in advanced HER2+ breast cancer.

Identifiants

pubmed: 36576009
pii: 6964385
doi: 10.1093/jnci/djac227
pmc: PMC9996199
doi:

Substances chimiques

Ado-Trastuzumab Emtansine SE2KH7T06F
Maytansine 14083FR882
Antibodies, Monoclonal, Humanized 0
Trastuzumab P188ANX8CK
Receptor, ErbB-2 EC 2.7.10.1
RNA, Messenger 0
ERBB2 protein, human EC 2.7.10.1

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

332-336

Commentaires et corrections

Type : CommentIn
Type : CommentIn

Informations de copyright

© The Author(s) 2022. Published by Oxford University Press. All rights reserved. For permissions, please email: journals.permissions@oup.com.

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Auteurs

Fara Brasó-Maristany (F)

Translational Genomics and Targeted Therapies in Solid Tumors group, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.

Gaia Griguolo (G)

Department of Surgery, Oncology and Gastroenterology, University of Padova, Padova, Italy.
Division of Oncology 2, Istituto Oncologico Veneto, IRCCS, Padova, Italy.

Nuria Chic (N)

Translational Genomics and Targeted Therapies in Solid Tumors group, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Spain.

Tomás Pascual (T)

Department of Medical Oncology, Hospital Clinic of Barcelona, Spain.
SOLTI Cooperative Group, Barcelona, Spain.

Laia Paré (L)

Reveal Genomics, Barcelona, Spain.

Julia Maues (J)

GRASP, Baltimore, MD, USA.

Patricia Galván (P)

Translational Genomics and Targeted Therapies in Solid Tumors group, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.

Maria Vittoria Dieci (MV)

Department of Surgery, Oncology and Gastroenterology, University of Padova, Padova, Italy.
Division of Oncology 2, Istituto Oncologico Veneto, IRCCS, Padova, Italy.

Federica Miglietta (F)

Department of Surgery, Oncology and Gastroenterology, University of Padova, Padova, Italy.
Division of Oncology 2, Istituto Oncologico Veneto, IRCCS, Padova, Italy.

Tommaso Giarratano (T)

Department of Surgery, Oncology and Gastroenterology, University of Padova, Padova, Italy.
Division of Oncology 2, Istituto Oncologico Veneto, IRCCS, Padova, Italy.

Olga Martínez-Sáez (O)

Translational Genomics and Targeted Therapies in Solid Tumors group, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Spain.
Department of Medicine, University of Barcelona, Barcelona, Spain.

Mercedes Marín-Aguilera (M)

Reveal Genomics, Barcelona, Spain.

Francesco Schettini (F)

Translational Genomics and Targeted Therapies in Solid Tumors group, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Spain.

Benedetta Conte (B)

Translational Genomics and Targeted Therapies in Solid Tumors group, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Spain.

Laura Angelats (L)

Translational Genomics and Targeted Therapies in Solid Tumors group, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Spain.

Maria Vidal (M)

Translational Genomics and Targeted Therapies in Solid Tumors group, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Spain.
SOLTI Cooperative Group, Barcelona, Spain.
Department of Medicine, University of Barcelona, Barcelona, Spain.
Institute of Oncology (IOB)-Hospital Quirónsalud, Barcelona, Spain.

Barbara Adamo (B)

Translational Genomics and Targeted Therapies in Solid Tumors group, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Spain.
GRASP, Baltimore, MD, USA.

Montserrat Muñoz (M)

Translational Genomics and Targeted Therapies in Solid Tumors group, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Spain.
SOLTI Cooperative Group, Barcelona, Spain.
Department of Medicine, University of Barcelona, Barcelona, Spain.

Esther Sanfeliu (E)

Department of Pathology, Hospital Clinic de Barcelona, Barcelona, Spain.

Blanca González (B)

Department of Pathology, Hospital Clinic de Barcelona, Barcelona, Spain.

Ana Vivancos (A)

Vall d'Hebron Institute of Oncology (VHIO), Cancer Genomics Group, Barcelona, Spain.

Patricia Villagrasa (P)

Reveal Genomics, Barcelona, Spain.

Joel S Parker (JS)

Department of Genetics, University of North Carolina, Chapel Hill, NC, USA.

Charles M Perou (CM)

Lineberger Comprehensive Cancer Center, University of North Carolina, Chapel Hill, NC, USA.

PierFranco Conte (P)

Department of Surgery, Oncology and Gastroenterology, University of Padova, Padova, Italy.
Division of Oncology 2, Istituto Oncologico Veneto, IRCCS, Padova, Italy.

Aleix Prat (A)

Translational Genomics and Targeted Therapies in Solid Tumors group, August Pi i Sunyer Biomedical Research Institute (IDIBAPS), Barcelona, Spain.
Department of Medical Oncology, Hospital Clinic of Barcelona, Spain.
SOLTI Cooperative Group, Barcelona, Spain.
Reveal Genomics, Barcelona, Spain.
Department of Medicine, University of Barcelona, Barcelona, Spain.
Institute of Oncology (IOB)-Hospital Quirónsalud, Barcelona, Spain.

Valentina Guarneri (V)

Department of Surgery, Oncology and Gastroenterology, University of Padova, Padova, Italy.
Division of Oncology 2, Istituto Oncologico Veneto, IRCCS, Padova, Italy.

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Classifications MeSH