Surrogate Endpoints as Predictors of Overall Survival in Metastatic Urothelial Cancer: A Trial-level Analysis.

Bladder cancer Clinical trials Surrogate endpoints

Journal

European urology open science
ISSN: 2666-1683
Titre abrégé: Eur Urol Open Sci
Pays: Netherlands
ID NLM: 101771568

Informations de publication

Date de publication:
Jan 2023
Historique:
accepted: 04 11 2022
entrez: 5 1 2023
pubmed: 6 1 2023
medline: 6 1 2023
Statut: epublish

Résumé

Surrogate endpoints (SEs), such as progression-free survival (PFS) and objective response rate (ORR), are frequently used in clinical trials. The relationship between SEs and overall survival (OS) has not been well described in metastatic urothelial cancer (MUC). We evaluated trial-level data to assess the relationship between SEs and OS. We hypothesize a moderate surrogacy relationship between both PFS and ORR with OS. We systematically reviewed phase 2/3 trials in MUC with two or more treatment arms, and report PFS and/or ORR, and OS. Linear regression was performed, and the coefficient of determination (R Of 3791 search results, 59 trials and 62 comparisons met the inclusion criteria. Of the 53 trials that reported PFS, 31 (58%) reported proportional hazard regression for PFS and OS. Linear regression across trials demonstrated an R PFS provides only a moderate level of surrogacy for OS; An HR We examined the relationship between surrogate endpoints, common outcomes in clinical trials, with survival in urothelial cancer trials. Progression-free survival is moderately correlated, while objective response rate had a poor correlation with survival and should be de-emphasized as a primary endpoint.

Sections du résumé

Background UNASSIGNED
Surrogate endpoints (SEs), such as progression-free survival (PFS) and objective response rate (ORR), are frequently used in clinical trials. The relationship between SEs and overall survival (OS) has not been well described in metastatic urothelial cancer (MUC).
Objective UNASSIGNED
We evaluated trial-level data to assess the relationship between SEs and OS. We hypothesize a moderate surrogacy relationship between both PFS and ORR with OS.
Design setting and participants UNASSIGNED
We systematically reviewed phase 2/3 trials in MUC with two or more treatment arms, and report PFS and/or ORR, and OS.
Outcome measurements and statistical analysis UNASSIGNED
Linear regression was performed, and the coefficient of determination (R
Results and limitations UNASSIGNED
Of 3791 search results, 59 trials and 62 comparisons met the inclusion criteria. Of the 53 trials that reported PFS, 31 (58%) reported proportional hazard regression for PFS and OS. Linear regression across trials demonstrated an R
Conclusions UNASSIGNED
PFS provides only a moderate level of surrogacy for OS; An HR
Patient summary UNASSIGNED
We examined the relationship between surrogate endpoints, common outcomes in clinical trials, with survival in urothelial cancer trials. Progression-free survival is moderately correlated, while objective response rate had a poor correlation with survival and should be de-emphasized as a primary endpoint.

Identifiants

pubmed: 36601043
doi: 10.1016/j.euros.2022.11.003
pii: S2666-1683(22)02684-2
pmc: PMC9806712
doi:

Types de publication

Journal Article

Langues

eng

Pagination

58-64

Informations de copyright

© 2022 The Authors.

Références

J Clin Oncol. 2015 Aug 10;33(23):2563-77
pubmed: 26101248
N Engl J Med. 2021 May 6;384(18):e68
pubmed: 33882220
Br J Cancer. 2020 May;122(11):1707-1714
pubmed: 32214230
J Clin Oncol. 1997 Dec;15(12):3507-14
pubmed: 9396404
J Med Libr Assoc. 2016 Jul;104(3):240-3
pubmed: 27366130
J Clin Oncol. 2007 Nov 20;25(33):5218-24
pubmed: 18024867
CA Cancer J Clin. 2021 Jan;71(1):7-33
pubmed: 33433946
Clin Cancer Res. 2013 May 15;19(10):2607-12
pubmed: 23669420
Ann Oncol. 2018 May 1;29(5):1079-1081
pubmed: 29648572
Ann Transl Med. 2019 Jun;7(11):244
pubmed: 31317014
Ann Oncol. 2015 Mar;26(3):485-96
pubmed: 25057168
Value Health. 2018 Jan;21(1):9-17
pubmed: 29304946
Eur J Cancer. 2009 Jan;45(2):228-47
pubmed: 19097774
Stat Med. 1989 Apr;8(4):431-40
pubmed: 2727467
Am J Cardiol. 2016 Jun 1;117(11):1845-50
pubmed: 27085935
Clin Cancer Res. 2013 May 15;19(10):2613-20
pubmed: 23669421
Clin Cancer Res. 2013 May 15;19(10):2621-8
pubmed: 23669422
Eur J Cancer. 2016 Jul;62:132-7
pubmed: 27189322
J Clin Oncol. 2003 Jul 1;21(13):2574-82
pubmed: 12829678
JAMA Intern Med. 2019 May 1;179(5):642-647
pubmed: 30933235
JAMA Oncol. 2022 May 1;8(5):679-680
pubmed: 35266952
Cancer J. 2009 Sep-Oct;15(5):401-5
pubmed: 19826360
JAMA Intern Med. 2020 Jun 1;180(6):912-914
pubmed: 32338703
JAMA Intern Med. 2015 Aug;175(8):1389-98
pubmed: 26098871
Lancet Oncol. 2017 Mar;18(3):e143-e152
pubmed: 28271869
Cancer. 2013 Aug 15;119(16):3020-6
pubmed: 23720197
Pharm Stat. 2006 Jul-Sep;5(3):173-86
pubmed: 17080751
Cancer J. 2009 Sep-Oct;15(5):386-94
pubmed: 19826358
Int J Clin Oncol. 2009 Apr;14(2):102-11
pubmed: 19390940
Lancet Oncol. 2015 Jan;16(1):e32-42
pubmed: 25638553

Auteurs

Fady Ghali (F)

Department of Urology, University of Washington School of Medicine, Seattle, WA, USA.

Yibai Zhao (Y)

Biostatistics Program, Fred Hutch Cancer Center, Seattle, WA, USA.

Devin Patel (D)

The Urology Clinic of Colorado, Denver, CO, USA.

Teresa Jewell (T)

Library Services, University of Washington School of Medicine, Seattle, WA, USA.

Evan Y Yu (EY)

Department of Medicine, University of Washington School of Medicine, Seattle, WA, USA.

Petros Grivas (P)

Department of Medicine, University of Washington School of Medicine, Seattle, WA, USA.

R Bruce Montgomery (RB)

Department of Medicine, University of Washington School of Medicine, Seattle, WA, USA.

John L Gore (JL)

Department of Urology, University of Washington School of Medicine, Seattle, WA, USA.

Ruth B Etzioni (RB)

Biostatistics Program, Fred Hutch Cancer Center, Seattle, WA, USA.

Jonathan L Wright (JL)

Department of Urology, University of Washington School of Medicine, Seattle, WA, USA.

Classifications MeSH