Thromboembolic toxicity observed with concurrent trametinib and lenalidomide therapy.


Journal

Pediatric blood & cancer
ISSN: 1545-5017
Titre abrégé: Pediatr Blood Cancer
Pays: United States
ID NLM: 101186624

Informations de publication

Date de publication:
03 2023
Historique:
revised: 12 12 2022
received: 18 05 2022
accepted: 13 12 2022
pmc-release: 01 03 2024
pubmed: 6 1 2023
medline: 27 1 2023
entrez: 5 1 2023
Statut: ppublish

Résumé

The event-free survival of pediatric low-grade gliomas is poor, and patients often require multiple treatment strategies. While MEK and RAF inhibitors are efficacious in early-phase trials, not all patients respond, and many experience progression following completion of therapy. Evaluating combination therapies that may enhance efficacy or prolong disease stabilization is warranted. We report our institutional experience using concurrent trametinib and lenalidomide in the treatment of primary pediatric central and peripheral nervous system tumors. Two of four patients using this combination therapy experienced severe thromboembolic events, necessitating discontinuation of therapy. This combination requires further investigation, and we urge caution if used.

Identifiants

pubmed: 36602034
doi: 10.1002/pbc.30190
pmc: PMC10519171
mid: NIHMS1928592
doi:

Substances chimiques

Lenalidomide F0P408N6V4
trametinib 33E86K87QN
Pyridones 0
Pyrimidinones 0
Proto-Oncogene Proteins B-raf EC 2.7.11.1

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

e30190

Subventions

Organisme : NINDS NIH HHS
ID : K08 NS121592
Pays : United States

Informations de copyright

© 2023 Wiley Periodicals LLC.

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Auteurs

Priya P Chan (PP)

Department of Pediatrics, University of Utah, Salt Lake City, Utah, USA.

Ashley Sabus (A)

Department of Pharmacy, Children's Hospital Colorado, University of Colorado Anschutz Medical Campus, Aurora, Colorado, USA.

Molly S Hemenway (MS)

Department of Pediatrics, Children's Hospital Colorado, University of Colorado Anschutz Medical Campus, Aurora, Colorado, USA.

Kathryn C Chatfield (KC)

Department of Pediatrics, Children's Hospital Colorado, University of Colorado Anschutz Medical Campus, Aurora, Colorado, USA.

Christina J White (CJ)

Department of Radiology, Children's Hospital Colorado, University of Colorado Anschutz Medical Campus, Aurora, Colorado, USA.

David M Mirsky (DM)

Department of Radiology, Children's Hospital Colorado, University of Colorado Anschutz Medical Campus, Aurora, Colorado, USA.

Nicholas K Foreman (NK)

Department of Pediatrics, Children's Hospital Colorado, University of Colorado Anschutz Medical Campus, Aurora, Colorado, USA.

Nathan A Dahl (NA)

Department of Pediatrics, Children's Hospital Colorado, University of Colorado Anschutz Medical Campus, Aurora, Colorado, USA.

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Classifications MeSH