Brolucizumab in Neovascular Age-Related Macular Degeneration and Diabetic Macular Edema: Ophthalmology and Diabetology Treatment Aspects.

Brolucizumab Diabetic macular edema (DME) Intraocular inflammation (IOI) Neovascular age-related macular degeneration (nAMD) Retinal vascular occlusion Retinal vasculitis Side effects Steroid-induced diabetes Treatment

Journal

Ophthalmology and therapy
ISSN: 2193-8245
Titre abrégé: Ophthalmol Ther
Pays: England
ID NLM: 101634502

Informations de publication

Date de publication:
Apr 2023
Historique:
received: 21 11 2022
accepted: 03 01 2023
pubmed: 13 1 2023
medline: 13 1 2023
entrez: 12 1 2023
Statut: ppublish

Résumé

Anti-vascular endothelial growth factor (anti-VEGF) therapies have become the standard of care in the treatment of neovascular age-related macular degeneration (nAMD) and diabetic macular edema (DME), resulting in a remarkable decrease in disease-related vision loss. However, the need for regular injections places a significant burden on patients, caregivers, and the healthcare system and improvements in vision may not be maintained long term. As a result of its drying potency and duration of action, brolucizumab, an intravitreal anti-VEGF therapy approved for the treatment of nAMD and DME, could decrease injection frequency for patients and provide an efficacious treatment; however, balancing its benefits and risks can be challenging. There have been reports of intraocular inflammation (IOI) in patients treated with brolucizumab, which, if left untreated, may result in severe vision loss. Recent evidence, however, indicates that early recognition of IOI and prompt and aggressive systemic corticosteroid treatment in response to posterior segment involvement can lead to favorable outcomes in these relatively rare but severe cases. A series of consensus meetings were conducted in 2022 between Swiss medical retina experts and diabetologists, discussing the current data for brolucizumab and exploring various challenges to its use, including the associated risk of IOI. The outcome is a collation of practical insights and guidance for ophthalmologists on the use of brolucizumab in patients with nAMD and DME, including patient selection and assessment, treatment regimen and monitoring, and the recognition and management of adverse events.

Identifiants

pubmed: 36633780
doi: 10.1007/s40123-023-00647-7
pii: 10.1007/s40123-023-00647-7
pmc: PMC10011261
doi:

Types de publication

Journal Article

Langues

eng

Pagination

639-655

Informations de copyright

© 2023. The Author(s).

Références

GBD 2019 Blindness and Vision Impairment Collaborators. Causes of blindness and vision impairment in 2020 and trends over 30 years, and prevalence of avoidable blindness in relation to VISION 2020: the Right to Sight: an analysis for the Global Burden of Disease Study. Lancet Glob Health. 2021;9(2):e144–60.
doi: 10.1016/S2214-109X(20)30489-7
World Health Organization. Blindness and vision impairment. 2022. https://www.who.int/news-room/fact-sheets/detail/blindness-and-visual-impairment . Accessed 18 Nov 2022.
Gehrs KM, Anderson DH, Johnson LV, Hageman GS. Age-related macular degeneration–emerging pathogenetic and therapeutic concepts. Am Med. 2000;38(7):450–71.
Finger RP, Dennis N, Freitas R, et al. Comparative efficacy of brolucizumab in the treatment of neovascular age-related macular degeneration: a systematic literature review and network meta-analysis. Adv Ther. 2022;39(8):3425–48.
pubmed: 35678996 pmcid: 9309118 doi: 10.1007/s12325-022-02193-3
Starr MR, Xu D, Boucher N, et al. Characterizing progression to neovascular AMD in fellow eyes of patients treated with intravitreal anti-VEGF injections. Ophthalmic Surg Lasers Imaging Retina. 2021;52(3):123–8.
pubmed: 34038686 doi: 10.3928/23258160-20210302-02
Yau JWY, Rogers SL, Kawasaki R, et al. Global prevalence and major risk factors of diabetic retinopathy. Diabetes Care. 2012;35:556–64.
pubmed: 22301125 pmcid: 3322721 doi: 10.2337/dc11-1909
Schmidt-Erfurth U, Garcia-Arumi J, Bandello F, et al. Guidelines for the management of diabetic macular Edema by the European Society of Retina Specialists (EURETINA). Ophthalmologica. 2017;237:185–222.
pubmed: 28423385 doi: 10.1159/000458539
Teo ZL, Tham Y, Yu M, et al. Global prevalence of diabetic retinopathy and projection of burden through 2045, systematic review and meta-analysis. Ophthalmology. 2021;128(11):1580–91.
pubmed: 33940045 doi: 10.1016/j.ophtha.2021.04.027
Kim LA, D’Amore PA. A brief history of anti-VEGF for the treatment of ocular angiogenesis. Am J Clin Pathol. 2012;181(2):376–9.
doi: 10.1016/j.ajpath.2012.06.006
Wirkkala J, Kubin AM, Ohtonen P, Yisela J, Siik T, Hautala N. Visual outcomes of observation, macular laser and anti-VEGF in diabetic macular edema in type 1 diabetes: a real-world study. BMC Ophthalmol. 2022;22:258.
pubmed: 35681133 pmcid: 9178825 doi: 10.1186/s12886-022-02482-z
Zirpel J, Pfister IB, Gerhardt C, Garweg JG. Long-term outcomes of intravitreal therapy for symptomatic diabetic macular oedema in a real-world setting in Switzerland. Graefes Arch Clin Exp Ophthalmol. 2021;259:3569–78.
pubmed: 33942162 pmcid: 8589751 doi: 10.1007/s00417-021-05187-z
Peto T, Akerele T, Sagkriotis A, Zappacosta S, Clemens A, Chakravarthy U. Treatment patterns and persistence rates with anti-vascular endothelial growth factor treatment for diabetic macular oedema in the UK: a real-world study. Diabet Med. 2022;39: e14746.
pubmed: 34796985 doi: 10.1111/dme.14746
Virgili G, Parravano M, Evans JR, Gordon I, Lucenteforte E. Anti-vascular endothelial growth factor for diabetic macular oedema: a network meta-analysis. Cochrane Database Syst Rev. 2018. https://doi.org/10.1002/14651858.CD007419.pub6 .
doi: 10.1002/14651858.CD007419.pub6 pubmed: 30325017 pmcid: 6517139
Gale RP, Mahmood S, Devonport H. Action on neovascular age-related macular degeneration (nAMD): recommendations for management and service provision in the UK hospital eye service. Eye. 2019;33(Suppl 1):1–21.
pubmed: 30926932 pmcid: 6474281 doi: 10.1038/s41433-018-0300-3
Ebneter A, Michels S, Pruente C, et al. Two-year outcomes of intravitreal aflibercept in a Swiss routine treat and extend regimen for patients with neovascular age-related macular degeneration. Sci Rep. 2020;10:20256.
pubmed: 33219242 pmcid: 7680100 doi: 10.1038/s41598-020-76354-1
Garweg JG, Gerhardt C. Disease stability and extended dosing under anti-VEGF treatment of exudative age-related macular degeneration (AMD)—a meta-analysis. Graefes Arch Clin Exp Ophthalmol. 2021;259:2181–92.
pubmed: 33528645 pmcid: 8352813 doi: 10.1007/s00417-020-05048-1
Khanani AM, Skelly A, Bezlyak V, et al. SIERRA-AMD: a retrospective, real-world evidence study of patients with neovascular age-related macular degeneration in the United States. Ophthalmol Retina. 2020;4(2):122–33.
pubmed: 31812631 doi: 10.1016/j.oret.2019.09.009
Giannakaki-Zimmermann H, Behrndt A, Hoffman L, et al. Predictors for 2-year functional and morphological outcomes of a treat-and-extend regimen with ranibizumab in patients with diabetic macular edema. Ophthalmic Res. 2021;64:465–75.
pubmed: 33498045 doi: 10.1159/000514721
Prenner JL, Halperin LS, Rycroft C, Hogue S, Liu ZW, Seibert R. Disease burden in the treatment of age-related macular degeneration: findings from a time-and-motion study. Am J Ophthalmol. 2015;160(4):725–31.
pubmed: 26142721 doi: 10.1016/j.ajo.2015.06.023
Adams M, Holekamp N, Jackson T, et al. PCR61 Burden and impacts associated with caring for neovascular age-related macular degeneration and diabetic macular edema patients: a multinational caregiver survey. Value Health. 2022;25(7):S552.
doi: 10.1016/j.jval.2022.04.1406
Spooner KL, Mhlanga CT, Hong TH, Broadhead GK, Chang AA. The burden of neovascular age-related macular degeneration: a patient’s perspective. Clin Ophthalmol. 2018;12:2483–91.
pubmed: 30584267 pmcid: 6287411 doi: 10.2147/OPTH.S185052
NHS England and NHS Improvement. Transforming NHS Outpatient Care. 2020. https://www.locsu.co.uk/wp-content/uploads/2020/11/NHSEI-NOC-2020-25112020.pdf . Accessed 18 Nov 2022.
Kiss S, Chandwani HS, Cole AL, Patel VD, Lunacsek OE, Dugel PU. Comorbidity and health care visit burden in working-age commercially insured patients with diabetic macular edema. Clin Ophthalmol. 2016;10:2443–53.
pubmed: 27994438 pmcid: 5153291 doi: 10.2147/OPTH.S114006
Skelly A, Ferreira A, Bezlyak V, Jaffe D. PSS13 The economic and humanistic burden of patients on treatment for neovascular age-related macular degeneration. Value Health. 2017;20:A399–811.
doi: 10.1016/j.jval.2017.08.2391
Jansen ME, Krambeer CJ, Kermany DS, et al. Appointment compliance in patients with diabetic macular edema and exudative macular degeneration. Ophthalmic Surg Lasers Imaging Retina. 2018;49:186–90.
pubmed: 29554386 doi: 10.3928/23258160-20180221-06
Holz FG, Tadayoni R, Beatty S, et al. Multi-country real-life experience of anti-vascular endothelial growth factor therapy for wet age-related macular degeneration. Br J Ophthalmol. 2015;99:220–6.
pubmed: 25193672 doi: 10.1136/bjophthalmol-2014-305327
Brynskov T, Munch IC, Larsen TM, Erngaard L, Sorensen TL. Real-world 10-year experiences with intravitreal treatment with ranibizumab and aflibercept for neovascular age-related macular degeneration. Acta Ophthalmol. 2020;98:132–8.
pubmed: 31282617 doi: 10.1111/aos.14183
Chandra S, Arpa C, Menon D, et al. Ten-year outcomes of antivascular endothelial growth factor therapy in neovascular age-related macular degeneration. Eye. 2020;34:1888–96.
pubmed: 31980748 pmcid: 7608465 doi: 10.1038/s41433-020-0764-9
Nguyen CL, Gillies MC, Nguyen V, et al. Characterization of poor visual outcomes of neovascular age-related macular degeneration treated with anti-vascular endothelial growth factor agents. Ophthalmology. 2019;126:735–42.
pubmed: 30529685 doi: 10.1016/j.ophtha.2018.11.036
Rodríguez FJ, Wu L, Bordon AF, et al. Intravitreal aflibercept for the treatment of patients with diabetic macular edema in routine clinical practice in Latin America: the AQUILA study. Int J Retin Vitr. 2022. https://doi.org/10.1186/s40942-022-00425-w .
doi: 10.1186/s40942-022-00425-w
Angermann R, Hofer M, Huber AL, et al. The impact of compliance among patients with diabetic macular oedema treated with intravitreal aflibercept: a 48-month follow-up study. Acta Ophthalmol. 2022;100:e546–52.
pubmed: 34145756 doi: 10.1111/aos.14946
Swiss Public Assessment Report – Beovu. 2020. https://www.swissmedic.ch/dam/swissmedic/de/dokumente/zulassung/swisspar/67244-beovu-01-swisspar-20200306.pdf.download.pdf/SwissPAR%20%E2%80%93%20Beovu.pdf . Accessed 18 Nov 2022.
Swiss Public Assessment Report, extension of therapeutic indication – Beovu. https://www.swissmedic.ch/dam/swissmedic/fr/dokumente/zulassung/swisspar/67244-beovu-02-swisspar-20220803.pdf.download.pdf/SwissPAR_final.pdf . Accessed 18 Nov 2022.
Dugel PU, Singh RP, Koh A, et al. HAWK and HARRIER ninety-six-week outcomes from the phase 3 trials of brolucizumab for neovascular age-related macular degeneration. Ophthalmology. 2021;128(1):89–99.
pubmed: 32574761 doi: 10.1016/j.ophtha.2020.06.028
Dugel PU, Koh A, Ogura Y, et al. HAWK and HARRIER: phase 3, multicenter, randomized, double-masked trials of brolucizumab for neovascular age-related macular degeneration. Ophthalmology. 2020;127(1):72–84.
pubmed: 30986442 doi: 10.1016/j.ophtha.2019.04.017
Jhaveri C, Wykoff CC, Khanani AM, et al. Early residual fluid-free status and long-term BCVA outcomes: a treatment agnostic, post hoc analysis of pooled HAWK and HARRIER data. Am J Ophthalmol. 2022;236:12–9.
pubmed: 34695400 doi: 10.1016/j.ajo.2021.10.017
Singh RP, Jhaveri C, Wykoff C, et al. Efficacy outcomes of brolucizumab versus aflibercept in neovascular age-related macular degeneration patients with early residual fluid. Ophthalmol Retina. 2022;6(5):377–86.
pubmed: 34968756 doi: 10.1016/j.oret.2021.12.014
Schmidt-Erfurth U, Mulyukov Z, Gerendas BS, et al. Therapeutic response in the HAWK and HARRIER trials using deep learning in retinal fluid volume and compartment analysis. Eye. 2022. https://doi.org/10.1038/s41433-022-02077-4 .
doi: 10.1038/s41433-022-02077-4 pubmed: 36577804 pmcid: 8873196
Monés J, Srivastava SK, Jaffe GJ, et al. Risk of inflammation, retinal vasculitis, and retinal occlusion-related events with brolucizumab: post hoc review of HAWK and HARRIER. Ophthalmology. 2021;128:1050–9.
pubmed: 33207259 doi: 10.1016/j.ophtha.2020.11.011
Regillo C, Kertes P, Kaiser PK, et al. TALON, a phase IIIb study of brolucizumab versus aflibercept in a matched (treat-and-extend) regimen in patients with neovascular age-related macular degeneration: 32-week primary outcomes. Presented at American Society of Retina Specialists, New York, July 13–16, 2022.
Boltz A, Radunksy K, Weingessel B, Vécsei-Marlovits VP. Brolucizumab for pre-treated patients with choroidal neovascularization and signs of tachyphylaxis to aflibercept and bevacizumab. Graefes Arch Clin Exp Ophthalmol. 2022;260(8):2561–6.
pubmed: 35348844
Bulirsch LM, Sassmannshausen S, Nadal J, Liegl R, Thiele S, Holz FG. Short-term real-world outcomes following intravitreal brolucizumab for neovascular AMD: SHIFT study. Br J Ophthalmol. 2022;106:1288–94.
pubmed: 33846161 doi: 10.1136/bjophthalmol-2020-318672
Giunta M, Meunier LG, Nixon D, Steeves J, Noble J. Early Canadian real-world experience with brolucizumab in anti-vascular endothelial growth factor-experienced patients with neovascular age-related macular degeneration: a retrospective chart review. Clin Ophthalmol. 2022;16:28852894.
doi: 10.2147/OPTH.S376199
Khanani AM, Zarbin MA, Barakat MR, et al. Safety outcomes of brolucizumab in neovascular age-related macular degeneration. JAMA Ophthalmol. 2022;140:20–8.
pubmed: 34817566 doi: 10.1001/jamaophthalmol.2021.4585
Khanani AM, Brown DM, Jaffe GJ, et al. MERLIN: phase 3a, multicenter, randomized, double-masked trial of brolucizumab in participants with neovascular age-related macular degeneration and persistent retinal fluid. Ophthalmology. 2022;129:974–85.
pubmed: 35537533 doi: 10.1016/j.ophtha.2022.04.028
Novartis. Novartis reports one year results of phase III MERLIN study evaluating Beovu
Swiss Medic Info. Beovu (Brolucizumab) product information. 2022. https://www.swissmedicinfo.ch/Default.aspx . Accessed 18 Nov 2022.
Schmouder RL, Maciejewski B, Karle A, et al. Immunologic features of Beovu
Bilgic A, Kodjikian L, March de Ribot F, et al. Real-world experience with brolucizumab in wet age-related macular degeneration: the REBA study. J Clin Med. 2021;10(13):2758.
pubmed: 34201729 pmcid: 8268719 doi: 10.3390/jcm10132758
Barchichat I, Thiel M, Job O, Schmid M. Bilateral blindness after uneventful brolucizumab injection for macular degeneration. BMC Ophthalmol. 2022;22:80.
pubmed: 35172763 pmcid: 8848976 doi: 10.1186/s12886-022-02305-1
Brown DM, Bandello AE, Bandello F, et al. KESTREL and KITE: 52-week results from two phase III pivotal trials of brolucizumab for diabetic macular edema 2022. Am J Ophthalmol. 2022;238:157–72.
pubmed: 35038415 doi: 10.1016/j.ajo.2022.01.004
Wykoff CC, Garweg JG, Regillo C, et al. Brolucizumab for treatment of diabetic macular edema (DME): 100-week results from the KESTREL and KITE studies. Invest Ophthalmol Vis Sci. 2022;63(7):3849.
Chakraborty D, Sheth JU, Boral S, Sinha TK. Off-label intravitreal brolucizumab for recalcitrant diabetic macular edema: a real-world case series. Am J Ophthalmol Case Rep. 2021;24: 101197.
pubmed: 34504981 pmcid: 8414050 doi: 10.1016/j.ajoc.2021.101197
Pearce I, Amoaku W, Bailey C, et al. The changing landscape for the management of patients with neovascular AMD: brolucizumab in clinical practice. Eye. 2022;36:1725–34.
pubmed: 35314774 pmcid: 8936380 doi: 10.1038/s41433-022-02008-3
Holz FG, Iida T, Maruko I, Sadda SR. A consensus on risk mitigation for brolucizumab in neovascular age-related macular degeneration - patient selection, evaluation, and treatment. Retina. 2022;42:1629–37.
pubmed: 35994582 pmcid: 9387760 doi: 10.1097/IAE.0000000000003556
Fonollosa A, Gallego-Pinazo R, Sararols L, Adan A, Lopez-Galvez M, Figueroa MS. Guidance on brolucizumab management recommendations. Arch Soc Esp Oftalmol. 2022. https://doi.org/10.1016/j.oftale.2022.05.006 .
doi: 10.1016/j.oftale.2022.05.006 pubmed: 35882576
Sharma A, Kumar N, Parachuri N, et al. Brolucizumab—early real-world experience: BREW study. Eye. 2021;5:1045–7.
doi: 10.1038/s41433-020-1111-x
Aziz AA, Khanani AM, London N, et al. Real world efficacy and safety of brolucizumab in neovascular AMD: The REBEL study. Invest Ophthalmol Vis Sci. 2021;62(8):451.
Haensli C, Pfister IB, Garweg JG. Switching to brolucizumab in neovascular age-related macular degeneration incompletely responsive to ranibizumab or aflibercept: real-life 6-month outcomes. J Clin Med. 2021;10:2666.
pubmed: 34204266 pmcid: 8235134 doi: 10.3390/jcm10122666
Khanani A, Sadda SR, Sarraf D, et al. Comparative assessment of the maximum thickness of pigment epithelial detachments and sub-RPE fluid in patients treated with brolucizumab versus aflibercept in the HAWK & HARRIER studies. Presented at EURETINA Virtual Meeting, September 2021.
Maruko I, Okada AA, Iida T, et al. Brolucizumab-related intraocular inflammation in Japanese patients with age-related macular degeneration: a short-term multicenter study. Graefes Arch Clin Exp Ophthalmol. 2021;259:2857–9.
pubmed: 33723637 pmcid: 8380561 doi: 10.1007/s00417-021-05136-w
Lanzetta P, Loewenstein A. Fundamental principles of an anti-VEGF treatment regimen: optimal application of intravitreal anti-vascular endothelial growth factor therapy of macular diseases. Arch Clin Exp Ophthalmol. 2017;255:1259–73.
doi: 10.1007/s00417-017-3647-4
National Institute for Health and Care Excellence (NICE). NICE guideline 82. Age-related macular degeneration. 2018. https://www.nice.org.uk/guidance/ng82 . Accessed 18 Nov 2022.
Holz FG, Heinz C, Wolf A, Hoerauf H, Pleyer U. Intraocular inflammation when using brolucizumab. Ophthalmologist. 2021;118(3):248–56.
doi: 10.1007/s00347-021-01321-8
Garweg JG, Hänsli C. Pitfalls in the interpretation of intraocular inflammation in response to intravitreal brolucizumab injection. Ocul Immunol Inflamm. 2021. https://doi.org/10.1080/09273948.2021.1976220 .
doi: 10.1080/09273948.2021.1976220 pubmed: 34637659
Tervaert CJW. Translational mini-review series on immunology of vascular disease: accelerated atherosclerosis in vasculitis. Clin Exp Immunol. 2009;156(3):377–85.
pubmed: 19309350 pmcid: 2691964 doi: 10.1111/j.1365-2249.2009.03885.x
Scherler L, Haas NA, Tengler A, Pattathu J, Mandilaras G, Jakob A. Acute phase of Kawasaki disease: a review of national guideline recommendations. Eur J Ped. 2022;181:2563–73.
doi: 10.1007/s00431-022-04458-z
Li J, Cummins CL. Fresh insights into glucocorticoid-induced diabetes mellitus and new therapeutic directions. Nat Rev Endocrinol. 2022;18:540–57.
pubmed: 35585199 pmcid: 9116713 doi: 10.1038/s41574-022-00683-6

Auteurs

Justus G Garweg (JG)

Berner Augenklinik, Zieglerstrasse 29 (Y), 3012, Bern, Switzerland. justus.garweg@augenklinik-bern.ch.
Department of Ophthalmology, Inselspital, University of Bern, Bern, Switzerland. justus.garweg@augenklinik-bern.ch.
Swiss Eye Institute, Luzernerstrasse 1, 6343, Rotkreuz, Switzerland. justus.garweg@augenklinik-bern.ch.

Claudine A Blum (CA)

University of Basel, Basel, Switzerland.
Medical University Clinic, Kantonsspital Aarau, Aarau, Switzerland.

René-Pierre Copt (RP)

Centre Ophtalmologique du Valais, 1950, Sion, Switzerland.

Chiara M Eandi (CM)

Department of Ophthalmology, University of Lausanne, Jules-Gonin Eye Hospital - Fondation Asile des Aveugles, Lausanne, Switzerland.
Department of Surgical Science, Eye Clinic, University of Torino, Turin, Italy.

Katja Hatz (K)

University of Basel, Basel, Switzerland.
Department of Ophthalmology, Vista Augenklinik, Binningen, Switzerland.

Christian F Prünte (CF)

Department of Ophthalmology, University Clinic, Basel, Switzerland.
Institute of Molecular and Clinical Ophthalmology (IOB), Basel, Switzerland.

Eleonora Seelig (E)

Departments of Endocrinology, Diabetology and Metabolism, University Hospital Basel, Petersgraben 4, 4031, Basel, Switzerland.
University Clinic of Medicine, Cantonal Hospital Baselland, Liestal, Switzerland.

Gábor M Somfai (GM)

Department of Ophthalmology, Stadtspital Zürich, 8063, Zurich, Switzerland.
Spross Research Institute, 8063, Zurich, Switzerland.
Department of Ophthalmology, Faculty of Medicine, Semmelweis University, 1085, Budapest, Hungary.

Classifications MeSH