Generation of an induced pluripotent stem cell line CSSi015-A (9553), carrying a point mutation c.2915C > T in the human calcium sensing receptor (CasR) gene.


Journal

Stem cell research
ISSN: 1876-7753
Titre abrégé: Stem Cell Res
Pays: England
ID NLM: 101316957

Informations de publication

Date de publication:
03 2023
Historique:
received: 08 10 2022
revised: 12 12 2022
accepted: 05 01 2023
pubmed: 14 1 2023
medline: 3 3 2023
entrez: 13 1 2023
Statut: ppublish

Résumé

Familial Hypocalciuric Hypercalcemia (FHH1) is a rare autosomal dominant disease with low penetrance, caused by inactivating mutations of the calcium-sensing receptor (CaSR) gene, characterized by significant hypercalcemia, inappropriately normal serum PTH levels and a low urinary calcium level. Human induced pluripotent stem cells (hiPSCs) from a patient carrying a previously identified heterozygous mutation, a p.T972M amino acid substitution in cytoplasmic tail of CasR, were produced using a virus, xeno-free and non-integrative protocol.

Identifiants

pubmed: 36638628
pii: S1873-5061(23)00009-0
doi: 10.1016/j.scr.2023.103023
pii:
doi:

Substances chimiques

Receptors, Calcium-Sensing 0
Calcium SY7Q814VUP
CASR protein, human 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

103023

Informations de copyright

Copyright © 2023 The Author(s). Published by Elsevier B.V. All rights reserved.

Déclaration de conflit d'intérêts

Declaration of Competing Interest The authors declare the following financial interests/personal relationships which may be considered as potential competing interests: Jessica Rosati reports financial support was provided by Ministry of Health.

Auteurs

Giovannina Rotundo (G)

Cellular Reprogramming Unit, Fondazione I.R.C.C.S. Casa Sollievo della Sofferenza, Viale dei Cappuccini, San Giovanni Rotondo, Foggia 71013, Italy.

Elisa Maria Turco (EM)

Cellular Reprogramming Unit, Fondazione I.R.C.C.S. Casa Sollievo della Sofferenza, Viale dei Cappuccini, San Giovanni Rotondo, Foggia 71013, Italy.

Giorgia Ruotolo (G)

Cellular Reprogramming Unit, Fondazione I.R.C.C.S. Casa Sollievo della Sofferenza, Viale dei Cappuccini, San Giovanni Rotondo, Foggia 71013, Italy; Biotechnology and Bioscience Department, Bicocca University, Piazza della Scienza 2, Milan 20126, Italy.

Isabella Torrente (I)

Medical Genetics Unit, Fondazione I.R.C.C.S. Casa Sollievo della Sofferenza, Viale dei Cappuccini, San Giovanni Rotondo, Foggia 71013, Italy.

Ornella Candido (O)

Medical Genetics Unit, Fondazione I.R.C.C.S. Casa Sollievo della Sofferenza, Viale dei Cappuccini, San Giovanni Rotondo, Foggia 71013, Italy.

Gianluca Lopez (G)

Department of Clinical and Molecular Medicine, Sapienza University and Sant'Andrea Hospital, Rome, Italy.

Daniela Ferrari (D)

Biotechnology and Bioscience Department, Bicocca University, Piazza della Scienza 2, Milan 20126, Italy.

Caterina Caputi (C)

Child Neurology and Psychiatry Unit Department of Human Neuroscience, Sapienza-University of Rome Via dei Sabelli, 00185, Italy.

Mario Mastrangelo (M)

Child Neurology and Psychiatry Unit Department of Human Neuroscience, Sapienza-University of Rome Via dei Sabelli, 00185, Italy.

Francesco Pisani (F)

Child Neurology and Psychiatry Unit Department of Human Neuroscience, Sapienza-University of Rome Via dei Sabelli, 00185, Italy.

Maurizio Gelati (M)

UPTA Unit Fondazione IRCCS Casa Sollievo della Sofferenza, Viale dei Cappuccini, San Giovanni Rotondo, Foggia 71013, Italy.

Vito Guarnieri (V)

Medical Genetics Unit, Fondazione I.R.C.C.S. Casa Sollievo della Sofferenza, Viale dei Cappuccini, San Giovanni Rotondo, Foggia 71013, Italy.

Angelo Luigi Vescovi (AL)

Cellular Reprogramming Unit, Fondazione I.R.C.C.S. Casa Sollievo della Sofferenza, Viale dei Cappuccini, San Giovanni Rotondo, Foggia 71013, Italy; Biotechnology and Bioscience Department, Bicocca University, Piazza della Scienza 2, Milan 20126, Italy.

Jessica Rosati (J)

Cellular Reprogramming Unit, Fondazione I.R.C.C.S. Casa Sollievo della Sofferenza, Viale dei Cappuccini, San Giovanni Rotondo, Foggia 71013, Italy. Electronic address: j.rosati@css-mendel.it.

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Classifications MeSH