Hematopoietic stem and progenitors cells gene editing: Beyond blood disorders.
TALEN and CRISPR/Cas9
ZFN
base editing
gene editing
hematopoietic stem and progenitor cells
inherited disorders
prime editing
Journal
Frontiers in genome editing
ISSN: 2673-3439
Titre abrégé: Front Genome Ed
Pays: Switzerland
ID NLM: 101775540
Informations de publication
Date de publication:
2022
2022
Historique:
received:
18
07
2022
accepted:
19
12
2022
entrez:
26
1
2023
pubmed:
27
1
2023
medline:
27
1
2023
Statut:
epublish
Résumé
Lessons learned from decades-long practice in the transplantation of hematopoietic stem and progenitor cells (HSPCs) to treat severe inherited disorders or cancer, have set the stage for the current
Identifiants
pubmed: 36698790
doi: 10.3389/fgeed.2022.997142
pii: 997142
pmc: PMC9868335
doi:
Types de publication
Journal Article
Review
Langues
eng
Pagination
997142Informations de copyright
Copyright © 2023 Buffa, Alvarez Vargas, Galy, Spinozzi and Rocca.
Déclaration de conflit d'intérêts
Authors VB, JA, AG, SS and CR were employed by the company Genethon.
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