Retinal ganglion cell-specific genetic regulation in primary open-angle glaucoma.

eQTL glaucoma human induced pluripotent stem cells retinal ganglion cells retinal organoids single-cell RNA sequencing transcriptomics

Journal

Cell genomics
ISSN: 2666-979X
Titre abrégé: Cell Genom
Pays: United States
ID NLM: 9918284260106676

Informations de publication

Date de publication:
08 Jun 2022
Historique:
received: 19 09 2020
revised: 08 03 2021
accepted: 11 05 2022
entrez: 13 2 2023
pubmed: 14 2 2023
medline: 14 2 2023
Statut: epublish

Résumé

To assess the transcriptomic profile of disease-specific cell populations, fibroblasts from patients with primary open-angle glaucoma (POAG) were reprogrammed into induced pluripotent stem cells (iPSCs) before being differentiated into retinal organoids and compared with those from healthy individuals. We performed single-cell RNA sequencing of a total of 247,520 cells and identified cluster-specific molecular signatures. Comparing the gene expression profile between cases and controls, we identified novel genetic associations for this blinding disease. Expression quantitative trait mapping identified a total of 4,443 significant loci across all cell types, 312 of which are specific to the retinal ganglion cell subpopulations, which ultimately degenerate in POAG. Transcriptome-wide association analysis identified genes at loci previously associated with POAG, and analysis, conditional on disease status, implicated 97 statistically significant retinal ganglion cell-specific expression quantitative trait loci. This work highlights the power of large-scale iPSC studies to uncover context-specific profiles for a genetically complex disease.

Identifiants

pubmed: 36778138
doi: 10.1016/j.xgen.2022.100142
pii: S2666-979X(22)00075-1
pmc: PMC9903700
doi:

Types de publication

Journal Article

Langues

eng

Pagination

100142

Informations de copyright

© 2022 The Authors.

Déclaration de conflit d'intérêts

The authors declare no competing interests.

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Auteurs

Maciej Daniszewski (M)

Department of Anatomy and Physiology, The University of Melbourne, Parkville, VIC 3010, Australia.
Department of Surgery, The University of Melbourne, Parkville, VIC 3010, Australia.
Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia.

Anne Senabouth (A)

Garvan Weizmann Centre for Cellular Genomics, Garvan Institute of Medical Research, The Kinghorn Cancer Centre, Darlinghurst, NSW 2010, Australia.

Helena H Liang (HH)

Department of Surgery, The University of Melbourne, Parkville, VIC 3010, Australia.
Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia.

Xikun Han (X)

QIMR Berghofer Medical Research Institute, Brisbane, QLD 4006, Australia.

Grace E Lidgerwood (GE)

Department of Anatomy and Physiology, The University of Melbourne, Parkville, VIC 3010, Australia.
Department of Surgery, The University of Melbourne, Parkville, VIC 3010, Australia.
Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia.

Damián Hernández (D)

Department of Anatomy and Physiology, The University of Melbourne, Parkville, VIC 3010, Australia.
Department of Surgery, The University of Melbourne, Parkville, VIC 3010, Australia.
Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia.

Priyadharshini Sivakumaran (P)

Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia.

Jordan E Clarke (JE)

Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia.

Shiang Y Lim (SY)

Department of Surgery, The University of Melbourne, Parkville, VIC 3010, Australia.
O'Brien Institute Department of St Vincent's Institute of Medical Research, Melbourne, Fitzroy, VIC 3065, Australia.

Jarmon G Lees (JG)

O'Brien Institute Department of St Vincent's Institute of Medical Research, Melbourne, Fitzroy, VIC 3065, Australia.
Department of Medicine, St Vincent's Hospital, The University of Melbourne, Parkville, VIC 3010, Australia.

Louise Rooney (L)

Department of Anatomy and Physiology, The University of Melbourne, Parkville, VIC 3010, Australia.
Department of Surgery, The University of Melbourne, Parkville, VIC 3010, Australia.
Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia.

Lerna Gulluyan (L)

Department of Anatomy and Physiology, The University of Melbourne, Parkville, VIC 3010, Australia.
Department of Surgery, The University of Melbourne, Parkville, VIC 3010, Australia.
Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia.

Emmanuelle Souzeau (E)

Department of Ophthalmology, Flinders University, Flinders Medical Centre, Bedford Park, SA 5042, Australia.

Stuart L Graham (SL)

Faculty of Medicine and Health Sciences, Macquarie University, Macquarie Park, NSW 2109, Australia.

Chia-Ling Chan (CL)

Garvan Weizmann Centre for Cellular Genomics, Garvan Institute of Medical Research, The Kinghorn Cancer Centre, Darlinghurst, NSW 2010, Australia.

Uyen Nguyen (U)

Garvan Weizmann Centre for Cellular Genomics, Garvan Institute of Medical Research, The Kinghorn Cancer Centre, Darlinghurst, NSW 2010, Australia.

Nona Farbehi (N)

Garvan Weizmann Centre for Cellular Genomics, Garvan Institute of Medical Research, The Kinghorn Cancer Centre, Darlinghurst, NSW 2010, Australia.

Vikkitharan Gnanasambandapillai (V)

Garvan Weizmann Centre for Cellular Genomics, Garvan Institute of Medical Research, The Kinghorn Cancer Centre, Darlinghurst, NSW 2010, Australia.

Rachael A McCloy (RA)

Garvan Weizmann Centre for Cellular Genomics, Garvan Institute of Medical Research, The Kinghorn Cancer Centre, Darlinghurst, NSW 2010, Australia.

Linda Clarke (L)

Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia.

Lisa S Kearns (LS)

Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia.

David A Mackey (DA)

Lions Eye Institute, Centre for Vision Sciences, University of Western Australia, Crawley, WA 6009, Australia.
School of Medicine, Menzies Institute for Medical Research, University of Tasmania, Hobart, TAS 7005, Australia.

Jamie E Craig (JE)

Department of Ophthalmology, Flinders University, Flinders Medical Centre, Bedford Park, SA 5042, Australia.

Stuart MacGregor (S)

QIMR Berghofer Medical Research Institute, Brisbane, QLD 4006, Australia.

Joseph E Powell (JE)

Garvan Weizmann Centre for Cellular Genomics, Garvan Institute of Medical Research, The Kinghorn Cancer Centre, Darlinghurst, NSW 2010, Australia.
UNSW Cellular Genomics Futures Institute, University of New South Wales, Sydney, NSW 2052, Australia.

Alice Pébay (A)

Department of Anatomy and Physiology, The University of Melbourne, Parkville, VIC 3010, Australia.
Department of Surgery, The University of Melbourne, Parkville, VIC 3010, Australia.
Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia.

Alex W Hewitt (AW)

Department of Surgery, The University of Melbourne, Parkville, VIC 3010, Australia.
Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, VIC 3002, Australia.
School of Medicine, Menzies Institute for Medical Research, University of Tasmania, Hobart, TAS 7005, Australia.

Classifications MeSH