Functional Homologous Recombination Assay on FFPE Specimens of Advanced High-Grade Serous Ovarian Cancer Predicts Clinical Outcomes.


Journal

Clinical cancer research : an official journal of the American Association for Cancer Research
ISSN: 1557-3265
Titre abrégé: Clin Cancer Res
Pays: United States
ID NLM: 9502500

Informations de publication

Date de publication:
15 08 2023
Historique:
received: 18 10 2022
revised: 29 12 2022
accepted: 15 02 2023
medline: 16 8 2023
pubmed: 23 2 2023
entrez: 22 2 2023
Statut: ppublish

Résumé

Deficiency in homologous recombination (HR) repair of DNA damage is characteristic of many high-grade serous ovarian cancers (HGSC). It is imperative to identify patients with homologous recombination-deficient (HRD) tumors as they are most likely to benefit from platinum-based chemotherapy and PARP inhibitors (PARPi). Existing methods measure historical, not necessarily current HRD and/or require high tumor cell content, which is not achievable for many patients. We set out to develop a clinically feasible assay for identifying functionally HRD tumors that can predict clinical outcomes. We quantified RAD51, a key HR protein, in immunostained formalin-fixed, paraffin-embedded (FFPE) tumor samples obtained from chemotherapy-naïve and neoadjuvant chemotherapy (NACT)-treated HGSC patients. We defined cutoffs for functional HRD separately for these sample types, classified the patients accordingly as HRD or HR-proficient, and analyzed correlations with clinical outcomes. From the same specimens, genomics-based HRD estimates (HR gene mutations, genomic signatures, and genomic scars) were also determined, and compared with functional HR (fHR) status. fHR status significantly predicted several clinical outcomes, including progression-free survival (PFS) and overall survival (OS), when determined from chemo-naïve (PFS, P < 0.0001; OS, P < 0.0001) as well as NACT-treated (PFS, P < 0.0001; OS, P = 0.0033) tumor specimens. The fHR test also identified as HRD those PARPi-at-recurrence-treated patients with longer OS (P = 0.0188). We developed an fHR assay performed on routine FFPE specimens, obtained from either chemo-naïve or NACT-treated HGSC patients, that can significantly predict real-world platinum-based chemotherapy and PARPi response. See related commentary by Garg and Oza, p. 2957.

Identifiants

pubmed: 36805632
pii: 716666
doi: 10.1158/1078-0432.CCR-22-3156
pmc: PMC10425726
doi:

Substances chimiques

Poly(ADP-ribose) Polymerase Inhibitors 0

Types de publication

Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

3110-3123

Commentaires et corrections

Type : CommentIn

Informations de copyright

©2023 The Authors; Published by the American Association for Cancer Research.

Références

Oncogene. 2003 Oct 20;22(47):7265-79
pubmed: 14576837
Eur J Cancer. 2009 Jan;45(2):228-47
pubmed: 19097774
Lancet Oncol. 2016 Nov;17(11):1579-1589
pubmed: 27617661
Nature. 2005 Apr 14;434(7035):913-7
pubmed: 15829966
Cancers (Basel). 2020 Sep 29;12(10):
pubmed: 33003546
Gynecol Oncol. 2021 Dec;163(3):490-497
pubmed: 34602290
Clin Cancer Res. 2018 Sep 15;24(18):4482-4493
pubmed: 29858219
N Engl J Med. 2018 Dec 27;379(26):2495-2505
pubmed: 30345884
Gynecol Oncol. 2020 Dec;159(3):877-886
pubmed: 32967790
Clin Cancer Res. 2010 Dec 15;16(24):6159-68
pubmed: 20802015
Nucleic Acids Res. 2018 Jan 4;46(D1):D1062-D1067
pubmed: 29165669
Nat Med. 2017 Apr;23(4):517-525
pubmed: 28288110
Nucleic Acids Res. 2019 Jan 8;47(D1):D941-D947
pubmed: 30371878
Ann Oncol. 2018 May 1;29(5):1203-1210
pubmed: 29635390
J Clin Oncol. 2019 Nov 10;37(32):2968-2973
pubmed: 31173551
J Clin Oncol. 2011 Aug 1;29(22):3008-15
pubmed: 21709188
Lancet. 2017 Oct 28;390(10106):1949-1961
pubmed: 28916367
Gynecol Oncol. 2020 Dec;159(3):887-898
pubmed: 33012552
Mod Pathol. 2000 Sep;13(9):962-72
pubmed: 11007036
Clin Cancer Res. 2018 Dec 15;24(24):6277-6287
pubmed: 30139880
EMBO Mol Med. 2021 May 7;13(5):e13366
pubmed: 33709473
Proc Natl Acad Sci U S A. 2010 Sep 28;107(39):16910-5
pubmed: 20837533
NPJ Breast Cancer. 2018 Jul 2;4:16
pubmed: 29978035
Sci Rep. 2020 Feb 17;10(1):2757
pubmed: 32066851
Genome Res. 2010 Sep;20(9):1297-303
pubmed: 20644199
Clin Cancer Res. 2016 Aug 1;22(15):3764-73
pubmed: 26957554
Nat Commun. 2021 May 3;12(1):2487
pubmed: 33941784
Hum Mutat. 2008 Nov;29(11):1282-91
pubmed: 18951446
Nature. 2005 Apr 14;434(7035):917-21
pubmed: 15829967
N Engl J Med. 2016 Dec;375(22):2154-2164
pubmed: 27717299
JAMA Netw Open. 2020 Sep 1;3(9):e2017517
pubmed: 32975569
Mol Cell Biol. 2013 Jan;33(2):387-95
pubmed: 23149936
Expert Rev Mol Diagn. 2022 Feb;22(2):185-199
pubmed: 34913794
Clin Cancer Res. 2014 Feb 1;20(3):764-75
pubmed: 24240112
Cancer Res. 2008 Jun 1;68(11):4311-20
pubmed: 18519691
Gynecol Oncol. 2021 Oct;163(1):11-13
pubmed: 34391577
Nat Commun. 2017 Nov 13;8(1):1470
pubmed: 29133916
Int J Gynecol Cancer. 2011 Feb;21(2):419-23
pubmed: 21270624
Cancer Res. 2022 Apr 15;82(8):1646-1657
pubmed: 35425960
ESMO Open. 2022 Oct;7(5):100585
pubmed: 36156447
Cancers (Basel). 2021 Jun 15;13(12):
pubmed: 34203855
Nature. 2020 Feb;578(7793):94-101
pubmed: 32025018
Mol Cell Biol. 2004 Jul;24(13):5776-87
pubmed: 15199134
NPJ Precis Oncol. 2022 Dec 29;6(1):96
pubmed: 36581696
Ann Oncol. 2020 Sep;31(9):1148-1159
pubmed: 32569725
Cancer Res. 2012 Nov 15;72(22):5675-82
pubmed: 23066035
Cancer Discov. 2015 Nov;5(11):1137-54
pubmed: 26463832
Clin Cancer Res. 2017 Aug 1;23(15):4086-4094
pubmed: 28223274
ESMO Open. 2020 Nov;5(6):e001110
pubmed: 33310779
Nature. 2013 Aug 22;500(7463):415-21
pubmed: 23945592
Clin Cancer Res. 2014 Sep 15;20(18):4816-26
pubmed: 24963051
Ann Oncol. 2020 Dec;31(12):1606-1622
pubmed: 33004253
EMBO Mol Med. 2018 Dec;10(12):
pubmed: 30377213

Auteurs

Sanna Pikkusaari (S)

Research Program in Systems Oncology, Research Programs Unit, Faculty of Medicine, University of Helsinki, Helsinki, Finland.

Manuela Tumiati (M)

Research Program in Systems Oncology, Research Programs Unit, Faculty of Medicine, University of Helsinki, Helsinki, Finland.

Anni Virtanen (A)

Department of Pathology, University of Helsinki and HUS Diagnostic Center, Helsinki University Hospital, Helsinki, Finland.

Jaana Oikkonen (J)

Research Program in Systems Oncology, Research Programs Unit, Faculty of Medicine, University of Helsinki, Helsinki, Finland.

Yilin Li (Y)

Research Program in Systems Oncology, Research Programs Unit, Faculty of Medicine, University of Helsinki, Helsinki, Finland.

Fernando Perez-Villatoro (F)

Research Program in Systems Oncology, Research Programs Unit, Faculty of Medicine, University of Helsinki, Helsinki, Finland.

Taru Muranen (T)

Research Program in Systems Oncology, Research Programs Unit, Faculty of Medicine, University of Helsinki, Helsinki, Finland.

Matilda Salko (M)

Research Program in Systems Oncology, Research Programs Unit, Faculty of Medicine, University of Helsinki, Helsinki, Finland.

Kaisa Huhtinen (K)

Research Program in Systems Oncology, Research Programs Unit, Faculty of Medicine, University of Helsinki, Helsinki, Finland.

Anna Kanerva (A)

Department of Obstetrics and Gynecology, Helsinki University Hospital, Helsinki, Finland.

Heidi Koskela (H)

Department of Obstetrics and Gynecology, Turku University Hospital, Turku, Finland.

Johanna Tapper (J)

Department of Obstetrics and Gynecology, Helsinki University Hospital, Helsinki, Finland.

Riitta Koivisto-Korander (R)

Department of Obstetrics and Gynecology, Helsinki University Hospital, Helsinki, Finland.

Titta Joutsiniemi (T)

Department of Obstetrics and Gynecology, Turku University Hospital, Turku, Finland.

Ulla-Maija Haltia (UM)

Department of Obstetrics and Gynecology, Helsinki University Hospital, Helsinki, Finland.

Heini Lassus (H)

Department of Obstetrics and Gynecology, Helsinki University Hospital, Helsinki, Finland.

Sampsa Hautaniemi (S)

Research Program in Systems Oncology, Research Programs Unit, Faculty of Medicine, University of Helsinki, Helsinki, Finland.

Anniina Färkkilä (A)

Research Program in Systems Oncology, Research Programs Unit, Faculty of Medicine, University of Helsinki, Helsinki, Finland.
iCAN digital precision cancer medicine flagship, University of Helsinki and Helsinki University Hospital, Helsinki, Finland.

Johanna Hynninen (J)

Department of Obstetrics and Gynecology, Turku University Hospital, Turku, Finland.

Sakari Hietanen (S)

Department of Obstetrics and Gynecology, Turku University Hospital, Turku, Finland.

Olli Carpén (O)

Research Program in Systems Oncology, Research Programs Unit, Faculty of Medicine, University of Helsinki, Helsinki, Finland.
Department of Pathology, University of Helsinki and HUS Diagnostic Center, Helsinki University Hospital, Helsinki, Finland.

Liisa Kauppi (L)

Research Program in Systems Oncology, Research Programs Unit, Faculty of Medicine, University of Helsinki, Helsinki, Finland.
iCAN digital precision cancer medicine flagship, University of Helsinki and Helsinki University Hospital, Helsinki, Finland.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH