Long-Term
NCALD
SMA
SMN2
antisense oligonucleotide
genetic modifier
hiPSCs
neuromuscular disorder
therapy
Journal
International journal of molecular sciences
ISSN: 1422-0067
Titre abrégé: Int J Mol Sci
Pays: Switzerland
ID NLM: 101092791
Informations de publication
Date de publication:
20 Feb 2023
20 Feb 2023
Historique:
received:
30
01
2023
revised:
17
02
2023
accepted:
19
02
2023
entrez:
25
2
2023
pubmed:
26
2
2023
medline:
3
3
2023
Statut:
epublish
Résumé
For SMA patients with only two
Identifiants
pubmed: 36835624
pii: ijms24044198
doi: 10.3390/ijms24044198
pmc: PMC9961752
pii:
doi:
Substances chimiques
Neurocalcin
0
Oligonucleotides
0
Survival of Motor Neuron 1 Protein
0
NCALD protein, human
0
Ncald protein, mouse
0
Types de publication
Journal Article
Langues
eng
Sous-ensembles de citation
IM
Subventions
Organisme : Deutsche Forschungsgemeinschaft
ID : Wi 945/17-1 (project 398410809)
Organisme : Deutsche Forschungsgemeinschaft
ID : GRK1960 (project ID 233886668)]
Organisme : Deutsche Forschungsgemeinschaft
ID : SFB1451 (project 431549029 - A01)
Organisme : European Union
ID : Horizon 2020 Marie Skłodowska-Curie (project 956185; SMABEYOND)
Organisme : Center for Molecular Medicine Cologne
ID : C18
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