Transplantation in paediatric patients with MMA requires multidisciplinary approach for achievement of good clinical outcomes.


Journal

Pediatric nephrology (Berlin, Germany)
ISSN: 1432-198X
Titre abrégé: Pediatr Nephrol
Pays: Germany
ID NLM: 8708728

Informations de publication

Date de publication:
08 2023
Historique:
received: 28 11 2022
accepted: 06 02 2023
revised: 06 02 2023
medline: 4 8 2023
pubmed: 26 2 2023
entrez: 25 2 2023
Statut: ppublish

Résumé

As modern medicine is advancing, younger, small, and more complex children are becoming multi-organ transplant candidates. This brings up new challenges in all aspects of their care. We describe the first report of a small child receiving a simultaneous liver and kidney transplant and abdominal rectus sheath fascia transplant on the background of Williams syndrome and methylmalonic acidaemia. At the time of transplantation, the child was 3 years old, weighed 14.0 kg, had chronic kidney disease stage V, and had not yet started any other form of kidney replacement therapy. There were many anaesthetic, medical, metabolic, and surgical challenges to consider in this case. A long general anaesthetic time increased the risk of cardiac complications and metabolic decompensation. Additionally, the small size of the patient and the organ size mis-match meant that primary abdominal closure was not possible. The patient's recovery was further complicated by sepsis, transient CNI toxicity, and de novo DSAs. Through a multidisciplinary approach between 9 specialties in 4 hospitals across England and Wales, and detailed pre-operative planning, a good outcome was achieved for this child. An hour by hour management protocol was drafted to facilitate transplant and included five domains: 1. management at the time of organ offer; 2. before the admission; 3. at admission and before theatre time; 4. intra-operative management; and 5. post-operative management in the first 24 h. Importantly, gaining a clear and in depth understanding of the metabolic state of the patient pre- and peri-operatively was crucial in avoiding metabolic decompensation. Furthermore, an abdominal rectus sheath fascia transplant was required to achieve abdominal closure, which to our knowledge, had never been done before for this indication. Using our experience of this complex case, as well as our experience in transplanting other children with MMA, and through a literature review, we propose a new perioperative management pathway for this complex cohort of transplant recipients.

Sections du résumé

BACKGROUND
As modern medicine is advancing, younger, small, and more complex children are becoming multi-organ transplant candidates. This brings up new challenges in all aspects of their care.
METHODS
We describe the first report of a small child receiving a simultaneous liver and kidney transplant and abdominal rectus sheath fascia transplant on the background of Williams syndrome and methylmalonic acidaemia. At the time of transplantation, the child was 3 years old, weighed 14.0 kg, had chronic kidney disease stage V, and had not yet started any other form of kidney replacement therapy.
RESULTS
There were many anaesthetic, medical, metabolic, and surgical challenges to consider in this case. A long general anaesthetic time increased the risk of cardiac complications and metabolic decompensation. Additionally, the small size of the patient and the organ size mis-match meant that primary abdominal closure was not possible. The patient's recovery was further complicated by sepsis, transient CNI toxicity, and de novo DSAs.
CONCLUSIONS
Through a multidisciplinary approach between 9 specialties in 4 hospitals across England and Wales, and detailed pre-operative planning, a good outcome was achieved for this child. An hour by hour management protocol was drafted to facilitate transplant and included five domains: 1. management at the time of organ offer; 2. before the admission; 3. at admission and before theatre time; 4. intra-operative management; and 5. post-operative management in the first 24 h. Importantly, gaining a clear and in depth understanding of the metabolic state of the patient pre- and peri-operatively was crucial in avoiding metabolic decompensation. Furthermore, an abdominal rectus sheath fascia transplant was required to achieve abdominal closure, which to our knowledge, had never been done before for this indication. Using our experience of this complex case, as well as our experience in transplanting other children with MMA, and through a literature review, we propose a new perioperative management pathway for this complex cohort of transplant recipients.

Identifiants

pubmed: 36840752
doi: 10.1007/s00467-023-05906-0
pii: 10.1007/s00467-023-05906-0
pmc: PMC10393894
doi:

Types de publication

Review Journal Article Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Pagination

2887-2896

Informations de copyright

© 2023. The Author(s).

Références

J Inherit Metab Dis. 2022 Mar;45(2):132-143
pubmed: 35038174
Pediatr Nephrol. 2021 Feb;36(2):245-257
pubmed: 31932959
Pediatr Nephrol. 2004 Oct;19(10):1071-4
pubmed: 15293040
Indian J Anaesth. 2017 Dec;61(12):1018-1020
pubmed: 29307912
Mol Genet Metab. 2022 Nov;137(3):265-272
pubmed: 36240580
Liver Transpl. 2018 Sep;24(9):1260-1270
pubmed: 30080956
Transplant Rev (Orlando). 2021 Dec;35(4):100634
pubmed: 34147948
Am J Transplant. 2007 Dec;7(12):2782-7
pubmed: 17908273
JCI Insight. 2018 Dec 6;3(23):
pubmed: 30518688
Pediatr Transplant. 2014 Feb;18(1):6-15
pubmed: 24283623
Pediatrics. 2015 Jul;136(1):e252-6
pubmed: 26077484
Pediatr Transplant. 2016 Dec;20(8):1081-1086
pubmed: 27670840
Pediatr Transplant. 2019 Aug;23(5):e13473
pubmed: 31124589
Masui. 2003 Aug;52(8):876-8
pubmed: 13677282
J Pediatr. 2015 Jun;166(6):1346-50
pubmed: 25882873
Ann Card Anaesth. 2010 Jan-Apr;13(1):44-8
pubmed: 20075535
J Inherit Metab Dis. 2020 Mar;43(2):234-243
pubmed: 31525265
J Inherit Metab Dis. 2021 May;44(3):593-605
pubmed: 32996606
Adv Ther. 2020 May;37(5):1866-1896
pubmed: 32270363
Mol Genet Metab. 2013 Sep-Oct;110(1-2):106-10
pubmed: 23751327
Transplantation. 2009 Sep 15;88(5):711-5
pubmed: 19741470
Pediatr Transplant. 2006 Dec;10(8):943-7
pubmed: 17096763
J Pediatr. 2015 Jun;166(6):1455-61.e1
pubmed: 25771389
Paediatr Anaesth. 2019 May;29(5):483-490
pubmed: 30811742
Am J Transplant. 2005 Nov;5(11):2754-63
pubmed: 16212637
World J Gastroenterol. 2018 Dec 21;24(47):5312-5321
pubmed: 30598576
Orphanet J Rare Dis. 2014 Sep 02;9:130
pubmed: 25205257

Auteurs

Alicia Paessler (A)

Great Ormond Street Hospital for Children NHS Foundation Trust, Great Ormond Street, WC1N 3JH, London, UK.
University College London Great Ormond Street Institute of Child Health, London, UK.

Miriam Cortes-Cerisuelo (M)

King's College Hospital NHS Foundation Trust, London, UK.

Wayel Jassem (W)

King's College Hospital NHS Foundation Trust, London, UK.

Hector Vilca-Melendez (H)

King's College Hospital NHS Foundation Trust, London, UK.

Akash Deep (A)

King's College Hospital NHS Foundation Trust, London, UK.

Vandana Jain (V)

King's College Hospital NHS Foundation Trust, London, UK.

Andrew Pool (A)

King's College Hospital NHS Foundation Trust, London, UK.

Stephanie Grunewald (S)

Great Ormond Street Hospital for Children NHS Foundation Trust, Great Ormond Street, WC1N 3JH, London, UK.

Nicos Kessaris (N)

Guys and St Thomas' NHS Foundation Trust, London, UK.

Jelena Stojanovic (J)

Great Ormond Street Hospital for Children NHS Foundation Trust, Great Ormond Street, WC1N 3JH, London, UK. jelena.stojanovic@gosh.nhs.uk.

Articles similaires

[Redispensing of expensive oral anticancer medicines: a practical application].

Lisanne N van Merendonk, Kübra Akgöl, Bastiaan Nuijen
1.00
Humans Antineoplastic Agents Administration, Oral Drug Costs Counterfeit Drugs

Smoking Cessation and Incident Cardiovascular Disease.

Jun Hwan Cho, Seung Yong Shin, Hoseob Kim et al.
1.00
Humans Male Smoking Cessation Cardiovascular Diseases Female
Humans United States Aged Cross-Sectional Studies Medicare Part C
1.00
Humans Yoga Low Back Pain Female Male

Classifications MeSH