Bayesian Statistics for Medical Devices: Progress Since 2010.

Bayesian adaptive designs Benefit-risk decision analysis Diagnostic test accuracy Hierarchical Bayesian modeling Prior Information Real-world evidence

Journal

Therapeutic innovation & regulatory science
ISSN: 2168-4804
Titre abrégé: Ther Innov Regul Sci
Pays: Switzerland
ID NLM: 101597411

Informations de publication

Date de publication:
05 2023
Historique:
received: 08 09 2022
accepted: 24 12 2022
medline: 28 4 2023
pubmed: 4 3 2023
entrez: 3 3 2023
Statut: ppublish

Résumé

The use of Bayesian statistics to support regulatory evaluation of medical devices began in the late 1990s. We review the literature, focusing on recent developments of Bayesian methods, including hierarchical modeling of studies and subgroups, borrowing strength from prior data, effective sample size, Bayesian adaptive designs, pediatric extrapolation, benefit-risk decision analysis, use of real-world evidence, and diagnostic device evaluation. We illustrate how these developments were utilized in recent medical device evaluations. In Supplementary Material, we provide a list of medical devices for which Bayesian statistics were used to support approval by the US Food and Drug Administration (FDA), including those since 2010, the year the FDA published their guidance on Bayesian statistics for medical devices. We conclude with a discussion of current and future challenges and opportunities for Bayesian statistics, including artificial intelligence/machine learning (AI/ML) Bayesian modeling, uncertainty quantification, Bayesian approaches using propensity scores, and computational challenges for high dimensional data and models.

Identifiants

pubmed: 36869194
doi: 10.1007/s43441-022-00495-w
pii: 10.1007/s43441-022-00495-w
pmc: PMC9984131
doi:

Types de publication

Journal Article Review

Langues

eng

Sous-ensembles de citation

IM

Pagination

453-463

Informations de copyright

© 2023. The Author(s), under exclusive licence to The Drug Information Association, Inc.

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Auteurs

Gregory Campbell (G)

GCStat Consulting LLC, 14605 Sandy Ridge Road, Silver Spring, MD, 20905, USA. GCStat@verizon.net.
Quantitative Sciences Consulting, Statistics and Decision Sciences, The Janssen Pharmaceutical Companies of Johnson & Johnson, 1125 Trenton-Harbourton Road, Titusville, NJ, 08560, USA. GCStat@verizon.net.

Telba Irony (T)

Quantitative Sciences Consulting, Statistics and Decision Sciences, The Janssen Pharmaceutical Companies of Johnson & Johnson, 1125 Trenton-Harbourton Road, Titusville, NJ, 08560, USA.

Gene Pennello (G)

Center for Devices and Radiological Health, U.S. Food and Drug Administration, Silver Spring, MD, 20993, USA.

Laura Thompson (L)

Center for Biologics Evaluation and Research, U.S. Food and Drug Administration, 10903 New Hampshire Avenue, Silver Spring, MD, 20993, USA.

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