PSMA-positive Circulating Tumor Cell Detection and Outcomes with Abiraterone or Enzalutamide Treatment in Men with Metastatic Castrate-resistant Prostate Cancer.


Journal

Clinical cancer research : an official journal of the American Association for Cancer Research
ISSN: 1557-3265
Titre abrégé: Clin Cancer Res
Pays: United States
ID NLM: 9502500

Informations de publication

Date de publication:
15 05 2023
Historique:
received: 11 11 2022
revised: 24 01 2023
accepted: 28 02 2023
medline: 16 5 2023
pubmed: 11 3 2023
entrez: 10 3 2023
Statut: ppublish

Résumé

In men with metastatic castration-resistant prostate cancer (mCRPC), prostate-specific membrane antigen (PSMA)-targeted radioligand therapy has drastically improved clinical outcomes. A liquid biopsy characterizing PSMA expression could be useful in guiding optimal therapy. We conducted a retrospective analysis of the prospective multicenter PROPHECY (Prospective CiRculating PrOstate Cancer Predictors in HighEr Risk mCRPC StudY) trial of men with mCRPC (n = 118) treated with abiraterone (abi) or enzalutamide (enza). Circulating tumor cells (CTC) were enriched (CTC/mL) and characterized for PSMA protein expression/heterogeneity at baseline and progression. We utilized proportional hazards modeling of the association between PSMA-positive (PSMA+) CTC enumeration with overall survival (OS) and progression-free survival (PFS). Overall, 97 men with mCRPC had evaluable blood samples for baseline CTC PSMA detection; 78 men (80%) had detectable CTCs. Of these, 55% (43/78) of men had any PSMA CTC detection, 21% (16/78) had ≥2 PSMA+ CTCs/mL, and 19% (8/43) were 100% PSMA+. At progression on abi/enza, 88% (50/57) of men had detectable CTCs, 68% (34/50) had any PSMA CTCs, and 12% (4/34) had 100% PSMA+ CTCs. Among paired cases (n = 57), PSMA+ CTC detection increased slightly after abi/enza progression. Using an optimal cutoff of ≥2 PSMA+ CTCs/mL, median OS was 26, 21, and 11 months for men without CTCs, PSMA- CTCs, and PSMA+ CTCs. Adjusting for prior abi/enza therapy, Halabi clinical risk score, and CTC enumeration, the HRs for OS and PFS for PSMA+ CTC+ were 3.0 [95% confidence interval (CI) = 1.1-7.8] and 2.3 (95% CI = 0.9-5.8). We observed PSMA CTC heterogeneity between and within patients with mCRPC over time during abi/enza progression. CTC PSMA enumeration was adversely prognostic independent of clinical factors and disease burden. Further validation is warranted in the context of PSMA-targeted therapies.

Identifiants

pubmed: 36897758
pii: 718681
doi: 10.1158/1078-0432.CCR-22-3233
pmc: PMC10192124
mid: NIHMS1890682
doi:

Substances chimiques

abiraterone G819A456D0
enzalutamide 93T0T9GKNU
Biomarkers, Tumor 0

Types de publication

Multicenter Study Journal Article Research Support, N.I.H., Extramural Research Support, U.S. Gov't, Non-P.H.S.

Langues

eng

Sous-ensembles de citation

IM

Pagination

1929-1937

Subventions

Organisme : NCI NIH HHS
ID : R01 CA233585
Pays : United States
Organisme : NCI NIH HHS
ID : P30 CA008748
Pays : United States
Organisme : NCI NIH HHS
ID : P30 CA014236
Pays : United States

Informations de copyright

©2023 American Association for Cancer Research.

Références

Endocr Relat Cancer. 2018 Oct 1;26(2):131-146
pubmed: 30400059
Nat Rev Cancer. 2014 Sep;14(9):623-31
pubmed: 25154812
Eur Urol. 2019 Oct;76(4):469-478
pubmed: 31345636
JCO Precis Oncol. 2020 Oct 28;4:
pubmed: 33154984
JAMA Oncol. 2018 Oct 1;4(10):1344-1351
pubmed: 29978216
Lancet Oncol. 2021 Aug;22(8):1115-1125
pubmed: 34246328
Prostate. 2000 May 1;43(2):150-7
pubmed: 10754531
Eur J Cancer. 2021 Jun;150:83-94
pubmed: 33894633
J Clin Oncol. 2008 Mar 1;26(7):1148-59
pubmed: 18309951
Clin Cancer Res. 2020 Jun 1;26(11):2654-2663
pubmed: 31911548
J Natl Cancer Inst. 2013 Nov 20;105(22):1729-37
pubmed: 24136890
Clin Cancer Res. 2021 Jul 15;27(14):4077-4088
pubmed: 33820782
J Clin Oncol. 2019 May 1;37(13):1120-1129
pubmed: 30865549
N Engl J Med. 2021 Sep 16;385(12):1091-1103
pubmed: 34161051
Mol Cancer Res. 2021 Jun;19(6):1040-1050
pubmed: 33771885
J Exp Med. 2018 Jan 2;215(1):159-175
pubmed: 29141866

Auteurs

Santosh Gupta (S)

Epic Sciences, San Diego, California.

Susan Halabi (S)

Department of Biostatistics and Bioinformatics, Duke University, Durham, North Carolina.

Qian Yang (Q)

Department of Biostatistics and Bioinformatics, Duke University, Durham, North Carolina.

Akash Roy (A)

Department of Biostatistics and Bioinformatics, Duke University, Durham, North Carolina.

Alisa Tubbs (A)

Epic Sciences, San Diego, California.

Yamini Gore (Y)

Epic Sciences, San Diego, California.

Daniel J George (DJ)

Duke Cancer Institute Center for Prostate and Urologic Cancers, Duke University, Durham, North Carolina.

David M Nanus (DM)

Weill Cornell Medical College, New York, New York.

Emmanuel S Antonarakis (ES)

Masonic Cancer Center, University of Minnesota, Minneapolis, Minnesota.

Daniel C Danila (DC)

Weill Cornell Medical College, New York, New York.

Russell Z Szmulewitz (RZ)

University of Chicago, Chicago, Illinois.

Richard Wenstrup (R)

Epic Sciences, San Diego, California.

Andrew J Armstrong (AJ)

Duke Cancer Institute Center for Prostate and Urologic Cancers, Duke University, Durham, North Carolina.

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Classifications MeSH