Live Birth of a Healthy Child in a Couple with Identical mtDNA Carrying a Pathogenic c.471_477delTTTAAAAinsG Variant in the


Journal

Genes
ISSN: 2073-4425
Titre abrégé: Genes (Basel)
Pays: Switzerland
ID NLM: 101551097

Informations de publication

Date de publication:
15 03 2023
Historique:
received: 11 02 2023
revised: 04 03 2023
accepted: 13 03 2023
medline: 30 3 2023
entrez: 29 3 2023
pubmed: 30 3 2023
Statut: epublish

Résumé

Molybdenum cofactor deficiency type B (MOCODB; #252160) is an autosomal recessive metabolic disorder that has only been described in 37 affected patients. In this report, we describe the presence of an in-frame homozygous variant (c.471_477delTTTAAAAinsG) in the

Identifiants

pubmed: 36980992
pii: genes14030720
doi: 10.3390/genes14030720
pmc: PMC10048300
pii:
doi:

Substances chimiques

DNA, Mitochondrial 0

Types de publication

Case Reports Research Support, Non-U.S. Gov't

Langues

eng

Sous-ensembles de citation

IM

Déclaration de conflit d'intérêts

The authors declare no conflict of interest.

Références

Genet Med. 2011 Sep;13(9):841-7
pubmed: 21555946
Nature. 2017 Sep 28;549(7673):519-522
pubmed: 28959963
Eur J Obstet Gynecol Reprod Biol. 2019 Jan;232:87-96
pubmed: 30502592
Diagnostics (Basel). 2020 Oct 14;10(10):
pubmed: 33066491
Nature. 2021 Aug;596(7873):583-589
pubmed: 34265844
Hum Mutat. 2003 Jun;21(6):569-76
pubmed: 12754701
J Inherit Metab Dis. 2022 May;45(3):456-469
pubmed: 35192225
Eur J Hum Genet. 2011 Dec;19(12):1226-9
pubmed: 21712854
Pediatr Neurol. 2012 Nov;47(5):317-23
pubmed: 23044011

Auteurs

Maria Tofilo (M)

Center for Molecular and Cellular Biology, Skolkovo Institute of Science and Technology, 121205 Moscow, Russia.
Medical Genomics, 170100 Tver, Russia.

Natalia Voronova (N)

Center for Molecular and Cellular Biology, Skolkovo Institute of Science and Technology, 121205 Moscow, Russia.

Leila Nigmatullina (L)

Center for Molecular and Cellular Biology, Skolkovo Institute of Science and Technology, 121205 Moscow, Russia.
Medical Genomics, 170100 Tver, Russia.
Fomin Clinics, 119192 Moscow, Russia.

Elena Kuznetsova (E)

Fomin Clinics, 119192 Moscow, Russia.

Valeria Timonina (V)

School of Life Sciences, Ecole Polytechnique Fédérale de Lausanne, 1015 Lausanne, Switzerland.

Bogdan Efimenko (B)

Center for Mitochondrial Functional Genomics, Immanuel Kant Baltic Federal University, 236041 Kaliningrad, Russia.

Oybek Turgunkhujaev (O)

Neurology Department, Semeynaya Clinic, 121059 Moscow, Russia.
A.I. Burnazyan Federal Medical and Biophysical Center, 123098 Moscow, Russia.

Svetlana Avdeichik (S)

Medical Genomics, 170100 Tver, Russia.
Fomin Clinics, 119192 Moscow, Russia.

Muhammad Ansar (M)

Department of Ophthalmology, Jules Gonin Eye Hospital, Fondation Asile Des Aveugles, University of Lausanne, 1015 Lausanne, Switzerland.
Advanced Molecular Genetics and Genomics Disease Research and Treatment Centre, Dow University of Health Sciences, Karachi 74200, Pakistan.

Konstantin Popadin (K)

School of Life Sciences, Ecole Polytechnique Fédérale de Lausanne, 1015 Lausanne, Switzerland.
Center for Mitochondrial Functional Genomics, Immanuel Kant Baltic Federal University, 236041 Kaliningrad, Russia.
Swiss Institute of Bioinformatics, 1015 Lausanne, Switzerland.

Anastasia Kirillova (A)

Center for Molecular and Cellular Biology, Skolkovo Institute of Science and Technology, 121205 Moscow, Russia.
Fomin Clinics, 119192 Moscow, Russia.

Ilya Mazunin (I)

Center for Molecular and Cellular Biology, Skolkovo Institute of Science and Technology, 121205 Moscow, Russia.

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Classifications MeSH