Circulating indian hedgehog is a marker of the hepatocyte-TAZ pathway in experimental NASH and is elevated in humans with NASH.

Biomarker Fibrosis IHH NAFLD NASH TAZ

Journal

JHEP reports : innovation in hepatology
ISSN: 2589-5559
Titre abrégé: JHEP Rep
Pays: Netherlands
ID NLM: 101761237

Informations de publication

Date de publication:
May 2023
Historique:
received: 01 11 2022
revised: 08 02 2023
accepted: 11 02 2023
medline: 11 4 2023
entrez: 10 4 2023
pubmed: 11 4 2023
Statut: epublish

Résumé

Non-alcoholic steatohepatitis (NASH)-induced liver fibrosis is emerging as the most common cause of liver disease. For evaluation of therapies, there is a pressing need to identify non-invasive, mechanism-based biomarkers. A pro-fibrotic process relevant to human NASH involves a pathway in which a transcriptional regulator called TAZ (WWTR1) in hepatocytes induces the secretion of pro-fibrotic Indian hedgehog (IHH). We therefore reasoned that circulating IHH may be a useful mechanism-based marker to assess changes in NASH fibrosis. Circulating IHH was assessed in wild-type and hepatocyte-TAZ-silenced NASH mice and in three separate cohorts of patients with mild-moderate NASH. Circulating IHH was elevated in mice with diet-induced NASH compared with chow-fed mice or with NASH mice in which hepatocyte TAZ was silenced, which is an effective means to decrease NASH fibrosis. In patients with fatty liver disease with or without NASH, NASH fibrosis was associated with increased concentrations of circulating IHH. The results of these analyses support further investigation to determine whether circulating IHH may be useful as a mechanism-based indicator of target engagement in anticipated future clinical trials testing NASH fibrosis therapies that block the IHH pathway. Non-alcoholic steatohepatitis (NASH)-induced liver fibrosis is a common cause of liver disease. Circulating biomarkers that reflect liver fibrosis in NASH would be very useful to evaluate therapies. One mechanism of NASH fibrosis with potential as a therapeutic target involves a liver-secreted protein called Indian hedgehog (IHH). We report that circulating levels of IHH in experimental and human NASH associates with NASH and NASH-associated liver fibrosis, providing the premise for further investigation into using circulating IHH to evaluate anticipated future NASH therapies that block the IHH pathway in liver.

Sections du résumé

Background & Aims UNASSIGNED
Non-alcoholic steatohepatitis (NASH)-induced liver fibrosis is emerging as the most common cause of liver disease. For evaluation of therapies, there is a pressing need to identify non-invasive, mechanism-based biomarkers. A pro-fibrotic process relevant to human NASH involves a pathway in which a transcriptional regulator called TAZ (WWTR1) in hepatocytes induces the secretion of pro-fibrotic Indian hedgehog (IHH). We therefore reasoned that circulating IHH may be a useful mechanism-based marker to assess changes in NASH fibrosis.
Methods UNASSIGNED
Circulating IHH was assessed in wild-type and hepatocyte-TAZ-silenced NASH mice and in three separate cohorts of patients with mild-moderate NASH.
Results UNASSIGNED
Circulating IHH was elevated in mice with diet-induced NASH compared with chow-fed mice or with NASH mice in which hepatocyte TAZ was silenced, which is an effective means to decrease NASH fibrosis. In patients with fatty liver disease with or without NASH, NASH fibrosis was associated with increased concentrations of circulating IHH.
Conclusions UNASSIGNED
The results of these analyses support further investigation to determine whether circulating IHH may be useful as a mechanism-based indicator of target engagement in anticipated future clinical trials testing NASH fibrosis therapies that block the IHH pathway.
Impact and implications UNASSIGNED
Non-alcoholic steatohepatitis (NASH)-induced liver fibrosis is a common cause of liver disease. Circulating biomarkers that reflect liver fibrosis in NASH would be very useful to evaluate therapies. One mechanism of NASH fibrosis with potential as a therapeutic target involves a liver-secreted protein called Indian hedgehog (IHH). We report that circulating levels of IHH in experimental and human NASH associates with NASH and NASH-associated liver fibrosis, providing the premise for further investigation into using circulating IHH to evaluate anticipated future NASH therapies that block the IHH pathway in liver.

Identifiants

pubmed: 37035456
doi: 10.1016/j.jhepr.2023.100716
pii: S2589-5559(23)00047-2
pmc: PMC10074197
doi:

Types de publication

Journal Article

Langues

eng

Pagination

100716

Informations de copyright

© 2023 The Author(s).

Déclaration de conflit d'intérêts

IT and XW have received research funding (unrestricted) from Takeda Pharmaceuticals. LV has been an invited speaker for MSD, Gilead, AlfaSigma, and AbbVie; consults for Gilead, Pfizer, Astra Zeneca, Novo Nordisk, Intercept pharmaceuticals, Diatech Pharmacogenetics, IONIS, Viatris, and Boehringer Ingelheim; and has received research funding (unrestricted) from Gilead. Please refer to the accompanying ICMJE disclosure forms for further details.

Références

Elife. 2016 May 17;5:
pubmed: 27185526
Hepatology. 2007 Oct;46(4):1081-90
pubmed: 17654743
Endocrinol Diabetes Metab. 2021 Oct;4(4):e00296
pubmed: 34505423
J Hepatol. 2009 Apr;50(4):789-96
pubmed: 19231010
Gastroenterology. 2020 May;158(7):1913-1928
pubmed: 32044315
N Engl J Med. 2017 Jan 5;376(1):41-51
pubmed: 27959715
J Am Chem Soc. 2014 Dec 10;136(49):16958-61
pubmed: 25434769
Am J Gastroenterol. 2017 Apr;112(4):581-587
pubmed: 28195177
J Blood Med. 2018 Aug 22;9:135-140
pubmed: 30174468
J Lipid Res. 2001 Nov;42(11):1801-11
pubmed: 11714849
Endocr Pract. 2022 May;28(5):528-562
pubmed: 35569886
J Am Soc Nephrol. 2017 Feb;28(2):494-503
pubmed: 27432743
Clin Gastroenterol Hepatol. 2015 Apr;13(4):643-54.e1-9; quiz e39-40
pubmed: 24768810
J Hepatol. 2019 Mar;70(3):531-544
pubmed: 30414863
Cell Metab. 2020 May 5;31(5):969-986.e7
pubmed: 32259482
Hepatol Commun. 2019 Jul 23;3(9):1221-1234
pubmed: 31497743
Trends Endocrinol Metab. 2016 Feb;27(2):84-95
pubmed: 26703097
Physiol Rev. 2008 Jan;88(1):125-72
pubmed: 18195085
Cell Metab. 2016 Dec 13;24(6):848-862
pubmed: 28068223
Cochrane Database Syst Rev. 2017 Mar 30;3:CD011640
pubmed: 28358980
Gastroenterology. 2015 Aug;149(2):389-97.e10
pubmed: 25935633
Proc Natl Acad Sci U S A. 1985 Dec;82(24):8681-5
pubmed: 3909149
Hepatology. 2022 Nov;76(5):1452-1465
pubmed: 35000203
ACS Chem Biol. 2015 May 15;10(5):1181-7
pubmed: 25730476
Nat Med. 2018 Jul;24(7):908-922
pubmed: 29967350
Adv Drug Deliv Rev. 2016 Sep 1;104:61-77
pubmed: 27352638
J Hepatol. 2022 Apr;76(4):910-920
pubmed: 34902531

Auteurs

Mary Patricia Moore (MP)

Department of Medicine, Columbia University Irving Medical Center, New York, NY, USA.

Xiaobo Wang (X)

Department of Medicine, Columbia University Irving Medical Center, New York, NY, USA.

Hongxue Shi (H)

Department of Medicine, Columbia University Irving Medical Center, New York, NY, USA.

Marica Meroni (M)

General Medicine and Metabolic Diseases, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Alessandro Cherubini (A)

Precision Medicine Lab, Biological Resource Center, Department of Transfusion Medicine, Fondazione Ca' Granda Ospedale Maggiore Policlinico Milano, Milan, Italy.

Luisa Ronzoni (L)

Precision Medicine Lab, Biological Resource Center, Department of Transfusion Medicine, Fondazione Ca' Granda Ospedale Maggiore Policlinico Milano, Milan, Italy.

Elizabeth J Parks (EJ)

Division of Gastroenterology and Hepatology, University of Missouri, Columbia, MO, USA.
Department of Nutrition and Exercise Physiology, School of Medicine, University of Missouri, Columbia, MO, USA.

Jamal A Ibdah (JA)

Division of Gastroenterology and Hepatology, University of Missouri, Columbia, MO, USA.
Research Service, Harry S Truman Memorial Veterans Medical Center, Columbia, MO, USA.
Department of Medical Pharmacology and Physiology, School of Medicine, University of Missouri, Columbia, MO, USA.

R Scott Rector (RS)

Division of Gastroenterology and Hepatology, University of Missouri, Columbia, MO, USA.
Department of Nutrition and Exercise Physiology, School of Medicine, University of Missouri, Columbia, MO, USA.
Research Service, Harry S Truman Memorial Veterans Medical Center, Columbia, MO, USA.

Luca Valenti (L)

Precision Medicine Lab, Biological Resource Center, Department of Transfusion Medicine, Fondazione Ca' Granda Ospedale Maggiore Policlinico Milano, Milan, Italy.
Department of Pathophysiology and Transplantation, Universitádegli Studi di Milano, Milan, Italy.

Paola Dongiovanni (P)

General Medicine and Metabolic Diseases, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan, Italy.

Ira Tabas (I)

Department of Medicine, Columbia University Irving Medical Center, New York, NY, USA.
Department of Pathology and Cell Biology, Columbia University Irving Medical Center, New York, NY, USA.
Department of Physiology and Cellular Biophysics, Columbia University Irving Medical Center, New York, NY, USA.

Classifications MeSH