Detection of

ATXN2 gene CAA interruption Parkinson's disease repeat expansions whole exome sequencing

Journal

Movement disorders clinical practice
ISSN: 2330-1619
Titre abrégé: Mov Disord Clin Pract
Pays: United States
ID NLM: 101630279

Informations de publication

Date de publication:
Apr 2023
Historique:
received: 13 12 2022
revised: 23 01 2023
accepted: 05 02 2023
medline: 19 4 2023
entrez: 18 4 2023
pubmed: 19 4 2023
Statut: epublish

Résumé

CAG-repeat expansions in To identify We explored WES data from a cohort of 477 index cases with PD using ExpansionHunter (Illumina DRAGEN Bio-IT Platform, San Diego, CA). Putative expansions were confirmed by combining polymerase chain reaction and fragment length analysis followed by sub-cloning and sequencing methods. Using ExpansionHunter, we identified three patients from two families with AD PD carrying either These findings demonstrate the usefulness of WES to detect pathogenic CAG repeat expansions, which were found in 1.7% of AD PD in the

Sections du résumé

Background UNASSIGNED
CAG-repeat expansions in
Objectives UNASSIGNED
To identify
Methods UNASSIGNED
We explored WES data from a cohort of 477 index cases with PD using ExpansionHunter (Illumina DRAGEN Bio-IT Platform, San Diego, CA). Putative expansions were confirmed by combining polymerase chain reaction and fragment length analysis followed by sub-cloning and sequencing methods.
Results UNASSIGNED
Using ExpansionHunter, we identified three patients from two families with AD PD carrying either
Conclusion UNASSIGNED
These findings demonstrate the usefulness of WES to detect pathogenic CAG repeat expansions, which were found in 1.7% of AD PD in the

Identifiants

pubmed: 37070044
doi: 10.1002/mdc3.13699
pii: MDC313699
pmc: PMC10105108
doi:

Types de publication

Journal Article

Langues

eng

Pagination

664-669

Informations de copyright

© 2023 The Authors. Movement Disorders Clinical Practice published by Wiley Periodicals LLC on behalf of International Parkinson and Movement Disorder Society.

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Auteurs

Fanny Casse (F)

Sorbonne Université, Institut du Cerveau - Paris Brain Institute - ICM, Institut National de la Recherche Médicale-U1127, Centre National de la Recherche Scientifique-UMR7225 Paris France.

Thomas Courtin (T)

Sorbonne Université, Institut du Cerveau - Paris Brain Institute - ICM, Institut National de la Recherche Médicale-U1127, Centre National de la Recherche Scientifique-UMR7225 Paris France.
AP-HP, Hôpital de la Pitié Salpêtrière, U.F. de Neurogénétique Moléculaire et Cellulaire Paris France.

Christelle Tesson (C)

Sorbonne Université, Institut du Cerveau - Paris Brain Institute - ICM, Institut National de la Recherche Médicale-U1127, Centre National de la Recherche Scientifique-UMR7225 Paris France.

Mélanie Ferrien (M)

Sorbonne Université, Institut du Cerveau - Paris Brain Institute - ICM, Institut National de la Recherche Médicale-U1127, Centre National de la Recherche Scientifique-UMR7225 Paris France.

Sandrine Noël (S)

AP-HP, Hôpital de la Pitié Salpêtrière, U.F. de Neurogénétique Moléculaire et Cellulaire Paris France.

Anne-Laure Fauret-Amsellem (AL)

AP-HP, Hôpital de la Pitié Salpêtrière, U.F. de Neurogénétique Moléculaire et Cellulaire Paris France.

Thomas Gareau (T)

Sorbonne Université, Institut du Cerveau - Paris Brain Institute - ICM, Institut National de la Recherche Médicale-U1127, Centre National de la Recherche Scientifique-UMR7225 Paris France.

Justine Guegan (J)

Sorbonne Université, Institut du Cerveau - Paris Brain Institute - ICM, Institut National de la Recherche Médicale-U1127, Centre National de la Recherche Scientifique-UMR7225 Paris France.

Mathieu Anheim (M)

Service de Neurologie Hôpitaux Universitaires de Strasbourg Strasbourg France.
Institut de Génétique et de Biologie Moléculaire et Cellulaire, Institut National de la Santé Et de la Recherche Médicale-U964/Centre National de la Recherche Scientifique-UMR7104/Université de Strasbourg Illkirch-Graffenstaden France.
Université de Strasbourg, Fédération de Médecine Translationnelle de Strasbourg Strasbourg France.

Louise-Laure Mariani (LL)

Sorbonne Université, Institut du Cerveau - Paris Brain Institute - ICM, Institut National de la Recherche Médicale-U1127, Centre National de la Recherche Scientifique-UMR7225 Paris France.
Département de Neurologie AP-HP, Hôpital de la Pitié Salpêtrière Paris France.

Nadine Le Forestier (N)

Département de Neurologie AP-HP, Hôpital de la Pitié Salpêtrière Paris France.

Christine Tranchant (C)

Service de Neurologie Hôpitaux Universitaires de Strasbourg Strasbourg France.
Institut de Génétique et de Biologie Moléculaire et Cellulaire, Institut National de la Santé Et de la Recherche Médicale-U964/Centre National de la Recherche Scientifique-UMR7104/Université de Strasbourg Illkirch-Graffenstaden France.
Université de Strasbourg, Fédération de Médecine Translationnelle de Strasbourg Strasbourg France.

Jean-Christophe Corvol (JC)

Sorbonne Université, Institut du Cerveau - Paris Brain Institute - ICM, Institut National de la Recherche Médicale-U1127, Centre National de la Recherche Scientifique-UMR7225 Paris France.
Département de Neurologie AP-HP, Hôpital de la Pitié Salpêtrière Paris France.

Suzanne Lesage (S)

Sorbonne Université, Institut du Cerveau - Paris Brain Institute - ICM, Institut National de la Recherche Médicale-U1127, Centre National de la Recherche Scientifique-UMR7225 Paris France.

Alexis Brice (A)

Sorbonne Université, Institut du Cerveau - Paris Brain Institute - ICM, Institut National de la Recherche Médicale-U1127, Centre National de la Recherche Scientifique-UMR7225 Paris France.

Classifications MeSH