Journal

Case reports in medicine
ISSN: 1687-9627
Titre abrégé: Case Rep Med
Pays: United States
ID NLM: 101512910

Informations de publication

Date de publication:
2023
Historique:
received: 13 11 2022
revised: 02 04 2023
accepted: 12 04 2023
medline: 8 5 2023
pubmed: 8 5 2023
entrez: 8 5 2023
Statut: epublish

Résumé

Primary ciliary dyskinesia (PCD), also known as the immotile-cilia syndrome, is a clinically and genetically heterogeneous syndrome. Improper function of the cilia causes impaired mucociliary clearance. Neonatal respiratory distress, rhinosinusitis, recurrent chest infections, wet cough, and otitis media are respiratory presentations of this disease. It could also manifest as infertility in males as well as laterality defects in both sexes, such as situs abnormalities (Kartagener syndrome). During the past decade, numerous pathogenic variants in 40 genes have been identified as the causatives of primary ciliary dyskinesia. We reported a novel homozygous nonsense variant in

Sections du résumé

Background UNASSIGNED
Primary ciliary dyskinesia (PCD), also known as the immotile-cilia syndrome, is a clinically and genetically heterogeneous syndrome. Improper function of the cilia causes impaired mucociliary clearance. Neonatal respiratory distress, rhinosinusitis, recurrent chest infections, wet cough, and otitis media are respiratory presentations of this disease. It could also manifest as infertility in males as well as laterality defects in both sexes, such as situs abnormalities (Kartagener syndrome). During the past decade, numerous pathogenic variants in 40 genes have been identified as the causatives of primary ciliary dyskinesia.
Conclusion UNASSIGNED
We reported a novel homozygous nonsense variant in

Identifiants

pubmed: 37153356
doi: 10.1155/2023/8436715
pmc: PMC10154638
doi:

Types de publication

Case Reports

Langues

eng

Pagination

8436715

Informations de copyright

Copyright © 2023 Fatemeh Sodeifian et al.

Déclaration de conflit d'intérêts

The authors declare that they have no conflicts of interest.

Références

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Auteurs

Fatemeh Sodeifian (F)

Student Research Committee, School of Medicine, Shahid Beheshti University of Medical Sciences, Tehran, Iran.
Network of Interdisciplinarity in Neonates and Infants (NINI), Universal Scientific Education and Research Network (USERN), Tehran, Iran.
USERN Office, Shahid Beheshti University of Medical Sciences, Tehran, Iran.

Noosha Samieefar (N)

Student Research Committee, School of Medicine, Shahid Beheshti University of Medical Sciences, Tehran, Iran.
Network of Interdisciplinarity in Neonates and Infants (NINI), Universal Scientific Education and Research Network (USERN), Tehran, Iran.
USERN Office, Shahid Beheshti University of Medical Sciences, Tehran, Iran.

Sepideh Shahkarami (S)

Department of Pediatrics, Dr. von Hauner Children's Hospital, University Hospital, Ludwig-Maximilians-Universität München (LMU), Munich, Germany.

Elham Rayzan (E)

International Hematology/Oncology of Pediatric Experts (IHOPE), Universal Scientific Education and Research Network (USERN), Boston, Massachusetts, USA.

Simin Seyedpour (S)

MD-MPH, School of Medicine, Tehran University of Medical Sciences, Tehran, Iran.
Research Center for Immunodeficiencies (RCID), Tehran, Iran.

Meino Rohlfs (M)

Department of Pediatrics, Dr. von Hauner Children's Hospital, University Hospital, Ludwig-Maximilians-Universität München (LMU), Munich, Germany.

Christoph Klein (C)

Department of Pediatrics, Dr. von Hauner Children's Hospital, University Hospital, Ludwig-Maximilians-Universität München (LMU), Munich, Germany.

Delara Babaie (D)

Department of Allergy and Clinical Immunology, Mofid Children Hospital, Shahid Beheshti University of Medical Sciences, Tehran, Iran.

Nima Rezaei (N)

Network of Interdisciplinarity in Neonates and Infants (NINI), Universal Scientific Education and Research Network (USERN), Tehran, Iran.
Research Center for Immunodeficiencies, Pediatrics Center of Excellence, Children's Medical Center, Tehran University of Medical Sciences, Tehran, Iran.

Classifications MeSH