Specific
CRISPRi
MT: RNA/DNA Editing
gene silencing
gene therapy
myotonic dystrophy type 1
neuromuscular disease
Journal
Molecular therapy. Nucleic acids
ISSN: 2162-2531
Titre abrégé: Mol Ther Nucleic Acids
Pays: United States
ID NLM: 101581621
Informations de publication
Date de publication:
13 Jun 2023
13 Jun 2023
Historique:
received:
26
08
2022
accepted:
10
05
2023
medline:
5
6
2023
pubmed:
5
6
2023
entrez:
5
6
2023
Statut:
epublish
Résumé
Myotonic dystrophy type 1 (DM1) is a neuromuscular disease that originates from an expansion of CTG microsatellites in the 3' untranslated region of the
Identifiants
pubmed: 37273786
doi: 10.1016/j.omtn.2023.05.007
pii: S2162-2531(23)00124-5
pmc: PMC10238591
doi:
Types de publication
Journal Article
Langues
eng
Pagination
857-871Informations de copyright
© 2023 The Authors.
Déclaration de conflit d'intérêts
The authors declare no competing interests.
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