Chromatographic Scalable Method to Isolate Engineered Extracellular Vesicles Derived from Mesenchymal Stem Cells for the Treatment of Liver Fibrosis in Mice.


Journal

International journal of molecular sciences
ISSN: 1422-0067
Titre abrégé: Int J Mol Sci
Pays: Switzerland
ID NLM: 101092791

Informations de publication

Date de publication:
31 May 2023
Historique:
received: 06 05 2023
revised: 25 05 2023
accepted: 27 05 2023
medline: 12 6 2023
pubmed: 10 6 2023
entrez: 10 6 2023
Statut: epublish

Résumé

New therapeutic options for liver cirrhosis are needed. Mesenchymal stem cell (MSC)-derived extracellular vesicles (EVs) have emerged as a promising tool for delivering therapeutic factors in regenerative medicine. Our aim is to establish a new therapeutic tool that employs EVs derived from MSCs to deliver therapeutic factors for liver fibrosis. EVs were isolated from supernatants of adipose tissue MSCs, induced-pluripotent-stem-cell-derived MSCs, and umbilical cord perivascular cells (HUCPVC-EVs) by ion exchange chromatography (IEC). To produce engineered EVs, HUCPVCs were transduced with adenoviruses that code for insulin-like growth factor 1 (AdhIGF-I-HUCPVC-EVs) or green fluorescent protein. EVs were characterized by electron microscopy, flow cytometry, ELISA, and proteomic analysis. We evaluated EVs' antifibrotic effect in thioacetamide-induced liver fibrosis in mice and on hepatic stellate cells in vitro. We found that IEC-isolated HUCPVC-EVs have an analogous phenotype and antifibrotic activity to those isolated by ultracentrifugation. EVs derived from the three MSCs sources showed a similar phenotype and antifibrotic potential. EVs derived from AdhIGF-I-HUCPVC carried IGF-1 and showed a higher therapeutic effect in vitro and in vivo. Remarkably, proteomic analysis revealed that HUCPVC-EVs carry key proteins involved in their antifibrotic process. This scalable MSC-derived EV manufacturing strategy is a promising therapeutic tool for liver fibrosis.

Identifiants

pubmed: 37298538
pii: ijms24119586
doi: 10.3390/ijms24119586
pmc: PMC10253331
pii:
doi:

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Subventions

Organisme : Agencia Nacional de Promoción Científica y Tecnológica (ANPCyT), CONICET (PIBAA 2022-2023), and Universidad Austral.
ID : PICT 2021 GRF-TI N° 00397, PICT-2021-I-A N° 975, PICT 2021-CAT-II N° 123 PICT 2019 N° 3282; PICT 2018 N° 4053

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Auteurs

Luciana M Domínguez (LM)

Laboratorio de Terapia Génica, Instituto de Investigaciones en Medicina Traslacional (IIMT), Universidad Austral-CONICET, Pilar B1629, Buenos Aires, Argentina.

Bárbara Bueloni (B)

Laboratorio de Terapia Génica, Instituto de Investigaciones en Medicina Traslacional (IIMT), Universidad Austral-CONICET, Pilar B1629, Buenos Aires, Argentina.

Ma José Cantero (MJ)

Laboratorio de Terapia Génica, Instituto de Investigaciones en Medicina Traslacional (IIMT), Universidad Austral-CONICET, Pilar B1629, Buenos Aires, Argentina.

Milagros Albornoz (M)

Laboratorio de Terapia Génica, Instituto de Investigaciones en Medicina Traslacional (IIMT), Universidad Austral-CONICET, Pilar B1629, Buenos Aires, Argentina.

Natalia Pacienza (N)

Instituto de Medicina Traslacional, Trasplante y Bioingeniería (IMeTTyB), Universidad Favaloro-CONICET, Ciudad Autónoma de Buenos Aires C1078, Argentina.

Celeste Biani (C)

LIAN-CONICET, Fleni, Belén de Escobar B1625, Buenos Aires, Argentina.

Carlos Luzzani (C)

LIAN-CONICET, Fleni, Belén de Escobar B1625, Buenos Aires, Argentina.

Santiago Miriuka (S)

LIAN-CONICET, Fleni, Belén de Escobar B1625, Buenos Aires, Argentina.

Mariana García (M)

Laboratorio de Terapia Génica, Instituto de Investigaciones en Medicina Traslacional (IIMT), Universidad Austral-CONICET, Pilar B1629, Buenos Aires, Argentina.

Catalina Atorrasagasti (C)

Laboratorio de Terapia Génica, Instituto de Investigaciones en Medicina Traslacional (IIMT), Universidad Austral-CONICET, Pilar B1629, Buenos Aires, Argentina.

Gustavo Yannarelli (G)

Instituto de Medicina Traslacional, Trasplante y Bioingeniería (IMeTTyB), Universidad Favaloro-CONICET, Ciudad Autónoma de Buenos Aires C1078, Argentina.

Juan Bayo (J)

Laboratorio de Terapia Génica, Instituto de Investigaciones en Medicina Traslacional (IIMT), Universidad Austral-CONICET, Pilar B1629, Buenos Aires, Argentina.

Esteban Fiore (E)

Laboratorio de Terapia Génica, Instituto de Investigaciones en Medicina Traslacional (IIMT), Universidad Austral-CONICET, Pilar B1629, Buenos Aires, Argentina.

Guillermo Mazzolini (G)

Laboratorio de Terapia Génica, Instituto de Investigaciones en Medicina Traslacional (IIMT), Universidad Austral-CONICET, Pilar B1629, Buenos Aires, Argentina.
Liver Unit, Hospital Universitario Austral, Universidad Austral-CONICET, Pilar B1629, Buenos Aires, Argentina.

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Classifications MeSH