Modelling renal defects in Bardet-Biedl syndrome patients using human iPS cells.

Bardet-Biedl syndrome CRISPR ciliopathy iPSC (induced pluripotent stem cell) kidney

Journal

Frontiers in cell and developmental biology
ISSN: 2296-634X
Titre abrégé: Front Cell Dev Biol
Pays: Switzerland
ID NLM: 101630250

Informations de publication

Date de publication:
2023
Historique:
received: 11 02 2023
accepted: 19 05 2023
medline: 19 6 2023
pubmed: 19 6 2023
entrez: 19 6 2023
Statut: epublish

Résumé

Bardet-Biedl syndrome (BBS) is a ciliopathy with pleiotropic effects on multiple tissues, including the kidney. Here we have compared renal differentiation of iPS cells from healthy and BBS donors. High content image analysis of WT1-expressing kidney progenitors showed that cell proliferation, differentiation and cell shape were similar in healthy,

Identifiants

pubmed: 37333983
doi: 10.3389/fcell.2023.1163825
pii: 1163825
pmc: PMC10272764
doi:

Types de publication

Journal Article

Langues

eng

Pagination

1163825

Informations de copyright

Copyright © 2023 Williams, Hurling, Munir, Harley, Machado, Cujba, Alvarez-Fallas, Danovi, Lieberam, Sancho, Beales and Watt.

Déclaration de conflit d'intérêts

The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.

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Auteurs

James Williams (J)

Centre for Gene Therapy and Regenerative Medicine, King's College London, Guy's Hospital, London, United Kingdom.

Chloe Hurling (C)

Centre for Gene Therapy and Regenerative Medicine, King's College London, Guy's Hospital, London, United Kingdom.

Sabrina Munir (S)

Centre for Gene Therapy and Regenerative Medicine, King's College London, Guy's Hospital, London, United Kingdom.

Peter Harley (P)

Centre for Gene Therapy and Regenerative Medicine, King's College London, Guy's Hospital, London, United Kingdom.

Carolina Barcellos Machado (CB)

Centre for Gene Therapy and Regenerative Medicine, King's College London, Guy's Hospital, London, United Kingdom.

Ana-Maria Cujba (AM)

Centre for Gene Therapy and Regenerative Medicine, King's College London, Guy's Hospital, London, United Kingdom.

Mario Alvarez-Fallas (M)

Centre for Gene Therapy and Regenerative Medicine, King's College London, Guy's Hospital, London, United Kingdom.

Davide Danovi (D)

Centre for Gene Therapy and Regenerative Medicine, King's College London, Guy's Hospital, London, United Kingdom.
Bit.bio, Babraham Research Campus, Cambridge, United Kingdom.

Ivo Lieberam (I)

Centre for Gene Therapy and Regenerative Medicine, King's College London, Guy's Hospital, London, United Kingdom.
Centre for Developmental Neurobiology and MRC Centre for Neurodevelopmental Disorders, King's College London, London, United Kingdom.

Rocio Sancho (R)

Centre for Gene Therapy and Regenerative Medicine, King's College London, Guy's Hospital, London, United Kingdom.

Philip Beales (P)

Institute of Child Health, Genetic and Genomic Medicine, University College London, London, United Kingdom.

Fiona M Watt (FM)

Centre for Gene Therapy and Regenerative Medicine, King's College London, Guy's Hospital, London, United Kingdom.

Classifications MeSH