Journal

bioRxiv : the preprint server for biology
Titre abrégé: bioRxiv
Pays: United States
ID NLM: 101680187

Informations de publication

Date de publication:
12 Jun 2023
Historique:
medline: 3 7 2023
pubmed: 3 7 2023
entrez: 3 7 2023
Statut: epublish

Résumé

The RGD (Arg-Gly-Asp)-binding integrins αvβ6 and αvβ8 are clinically validated cancer and fibrosis targets of considerable therapeutic importance. Compounds that can discriminate between the two closely related integrin proteins and other RGD integrins, stabilize specific conformational states, and have sufficient stability enabling tissue restricted administration could have considerable therapeutic utility. Existing small molecules and antibody inhibitors do not have all of these properties, and hence there is a need for new approaches. Here we describe a method for computationally designing hyperstable RGD-containing miniproteins that are highly selective for a single RGD integrin heterodimer and conformational state, and use this strategy to design inhibitors of αvβ6 and αvβ8 with high selectivity. The αvβ6 and αvβ8 inhibitors have picomolar affinities for their targets, and >1000-fold selectivity over other RGD integrins. CryoEM structures are within 0.6-0.7Å root-mean-square deviation (RMSD) to the computational design models; the designed αvβ6 inhibitor and native ligand stabilize the open conformation in contrast to the therapeutic anti-αvβ6 antibody BG00011 that stabilizes the bent-closed conformation and caused on-target toxicity in patients with lung fibrosis, and the αvβ8 inhibitor maintains the constitutively fixed extended-closed αvβ8 conformation. In a mouse model of bleomycin-induced lung fibrosis, the αvβ6 inhibitor potently reduced fibrotic burden and improved overall lung mechanics when delivered via oropharyngeal administration mimicking inhalation, demonstrating the therapeutic potential of

Identifiants

pubmed: 37398153
doi: 10.1101/2023.06.12.544624
pmc: PMC10312613
pii:
doi:

Types de publication

Preprint

Langues

eng

Subventions

Organisme : NIAMS NIH HHS
ID : R01 AR067288
Pays : United States
Organisme : NIGMS NIH HHS
ID : R35 GM147414
Pays : United States
Organisme : NIDDK NIH HHS
ID : K01 DK124443
Pays : United States
Organisme : NIGMS NIH HHS
ID : T32 GM008268
Pays : United States
Organisme : NCI NIH HHS
ID : P30 CA015704
Pays : United States
Organisme : NIGMS NIH HHS
ID : R01 GM092802
Pays : United States

Commentaires et corrections

Type : UpdateIn

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Auteurs

Anindya Roy (A)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Lei Shi (L)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.
Current Address: Encodia Inc, 5785 Oberlin Drive, San Diego, CA 92121.

Ashley Chang (A)

Department of Chemistry and Biochemistry, Brigham Young University, Provo, UT 84602, USA.

Xianchi Dong (X)

Program in Cellular and Molecular Medicine, Children's Hospital Boston, and Departments of Biological Chemistry and Molecular Pharmacology and of Medicine, Harvard Medical School, Boston, United States.
Current address: State Key Laboratory of Pharmaceutical Biotechnology, School of Life Sciences, Nanjing University, Nanjing, China; Engineering Research Center of Protein and Peptide Medicine,Ministry of Education.

Andres Fernandez (A)

Division of Basic Sciences, Fred Hutchinson Cancer Center, Seattle, WA 98109, USA.

John C Kraft (JC)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Jing Li (J)

Program in Cellular and Molecular Medicine, Children's Hospital Boston, and Departments of Biological Chemistry and Molecular Pharmacology and of Medicine, Harvard Medical School, Boston, United States.

Viet Q Le (VQ)

Program in Cellular and Molecular Medicine, Children's Hospital Boston, and Departments of Biological Chemistry and Molecular Pharmacology and of Medicine, Harvard Medical School, Boston, United States.

Rebecca Viazzo Winegar (RV)

Department of Chemistry and Biochemistry, Brigham Young University, Provo, UT 84602, USA.

Gerald Maxwell Cherf (GM)

Department of Bioengineering, Stanford University, Stanford CA 94305.
Current Address: Denali Therapeutics, South San Francisco, CA, USA.

Dean Slocum (D)

Department of Chemistry and Biochemistry, Brigham Young University, Provo, UT 84602, USA.

P Daniel Poulson (P)

Department of Chemistry and Biochemistry, Brigham Young University, Provo, UT 84602, USA.

Garrett E Casper (GE)

Department of Chemistry and Biochemistry, Brigham Young University, Provo, UT 84602, USA.

Mary L Vallecillo-Zúniga (ML)

Department of Chemistry and Biochemistry, Brigham Young University, Provo, UT 84602, USA.

Jonard Corpuz Valdoz (JC)

Department of Chemistry and Biochemistry, Brigham Young University, Provo, UT 84602, USA.

Marcos C Miranda (MC)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.
Current Address: Department of Medicine Solna, Division of Immunology and Allergy, Karolinska Institutet and Karolinska University Hospital, Stockholm, Sweden.

Hua Bai (H)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Yakov Kipnis (Y)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.
Division of Pulmonary, Critical Care and Sleep Medicine, Department of Medicine, University of Washington, Seattle, Washington.

Audrey Olshefsky (A)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.
Department of Bioengineering, University of Washington, Seattle, WA 98195, USA.

Tanu Priya (T)

Department of Materials Science and Engineering, University of Washington, Seattle, WA 98195, USA.
Current Address: Department of Pharmacology, Northwestern University Feinberg School of Medicine; Chicago, IL 60611, USA.

Lauren Carter (L)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Rashmi Ravichandran (R)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Cameron M Chow (CM)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Max R Johnson (MR)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Suna Cheng (S)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

McKaela Smith (M)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Catherine Overed-Sayer (C)

Research and Early Development, Respiratory and Immunology, BioPharmaceuticals R&D, AstraZeneca, Cambridge, United Kingdom.
Current Address: Bioscience COPD/IPF, Research and Early Development, Respiratory and Immunology, BioPharmaceuticals R&D, AstraZeneca, Cambridge, UK.

Donna K Finch (DK)

Research and Early Development, Respiratory and Immunology, BioPharmaceuticals R&D, AstraZeneca, Cambridge, United Kingdom.
Current Address: Alchemab Therapeutics Ltd, Cambridge, United Kingdom.

David Lowe (D)

Research and Early Development, Respiratory and Immunology, BioPharmaceuticals R&D, AstraZeneca, Cambridge, United Kingdom.
Current Address: Evox Therapeutics Limited, Oxford Science Park, Medawar Centre, East Building, Robert Robinson Avenue, Oxford, OX4 4HG.

Asim K Bera (AK)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Gustavo Matute-Bello (G)

Center for Lung Biology, Division of Pulmonary, Critical Care and Sleep Medicine, University of Washington.

Timothy P Birkland (TP)

Division of Pulmonary, Critical Care and Sleep Medicine, Department of Medicine, University of Washington, Seattle, Washington.

Frank DiMaio (F)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Ganesh Raghu (G)

Division of Pulmonary, Critical Care and Sleep Medicine, Department of Medicine, University of Washington, Seattle, Washington.

Jennifer R Cochran (JR)

Department of Bioengineering, Stanford University, Stanford CA 94305.

Lance J Stewart (LJ)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.

Melody G Campbell (MG)

Division of Basic Sciences, Fred Hutchinson Cancer Center, Seattle, WA 98109, USA.

Pam M Van Ry (PM)

Department of Chemistry and Biochemistry, Brigham Young University, Provo, UT 84602, USA.

Timothy Springer (T)

Program in Cellular and Molecular Medicine, Children's Hospital Boston, and Departments of Biological Chemistry and Molecular Pharmacology and of Medicine, Harvard Medical School, Boston, United States.

David Baker (D)

Department of Biochemistry and Institute for Protein Design, University of Washington, Seattle, WA 98195, USA.
Howard Hughes Medical Institute, University of Washington, Seattle, WA 98195, USA.

Classifications MeSH