Intronic


Journal

Journal of neurology, neurosurgery, and psychiatry
ISSN: 1468-330X
Titre abrégé: J Neurol Neurosurg Psychiatry
Pays: England
ID NLM: 2985191R

Informations de publication

Date de publication:
11 Jan 2024
Historique:
received: 15 03 2023
accepted: 25 05 2023
medline: 15 1 2024
pubmed: 3 7 2023
entrez: 3 7 2023
Statut: epublish

Résumé

Intronic GAA repeat expansions in the fibroblast growth factor 14 gene ( We recruited 45 patients negative for biallelic Frequency of GAA-

Sections du résumé

BACKGROUND BACKGROUND
Intronic GAA repeat expansions in the fibroblast growth factor 14 gene (
METHODS METHODS
We recruited 45 patients negative for biallelic
RESULTS RESULTS
Frequency of
CONCLUSIONS CONCLUSIONS
GAA-

Identifiants

pubmed: 37399286
pii: jnnp-2023-331490
doi: 10.1136/jnnp-2023-331490
pmc: PMC10850669
doi:

Substances chimiques

fibroblast growth factor 14 0

Types de publication

Journal Article

Langues

eng

Sous-ensembles de citation

IM

Pagination

175-179

Subventions

Organisme : Wellcome Trust
Pays : United Kingdom
Organisme : Medical Research Council
ID : MR/N028767/1
Pays : United Kingdom
Organisme : Medical Research Council
ID : MR/S01165X/1
Pays : United Kingdom
Organisme : Medical Research Council
ID : MR/T001712/1
Pays : United Kingdom

Informations de copyright

© Author(s) (or their employer(s)) 2024. Re-use permitted under CC BY. Published by BMJ.

Déclaration de conflit d'intérêts

Competing interests: DP reports no disclosures. CW reports no disclosures. AT reports no disclosures. SN reports no disclosures. RC reports no disclosures. M-JD reports no disclosures. HG-M reports no disclosures. MA has received consultancy honoraria from Merz, Ipsen Pharmaceuticals, Orkyn, AbbVie, Reata, Ever Pharma, all unrelated to the present manuscript. TW has received consultancy honoraria from Ipsen Pharmaceuticals and AbbVie, all unrelated to the present manuscript. JF reports no disclosures. DT reports no disclosures. CD reports no disclosures. DR has received grant/research support from Janssen and Lundbeck; he has served as a consultant or on advisory boards for AC Immune, Janssen, Roche and Rovi and he has served on speakers bureaus of Janssen and Pharmagenetix. He also received honoraria from Gerot Lannacher, Janssen and Pharmagenetix, and travel support from Angelini and Janssen, all unrelated to the present manuscript. JG reports no disclosures. MMR reports no disclosures. PG reports no disclosures. BB reports no disclosures. HH reports no disclosures. LS reports no disclosures. MSt reports no disclosures. AC reports no disclosures. MSy has received consultancy honoraria from Janssen, Ionis, Orphazyme, Servier, Reata, GenOrph and AviadoBio, all unrelated to the present manuscript.

Références

Front Neurol. 2016 Apr 20;7:58
pubmed: 27148159
Sci Rep. 2023 Jun 15;13(1):9737
pubmed: 37322040
Nat Genet. 2019 Apr;51(4):649-658
pubmed: 30926972
J Neurol Neurosurg Psychiatry. 2003 Oct;74(10):1403-6
pubmed: 14570834
Brain. 2021 Jun 22;144(5):1542-1550
pubmed: 33969391
Neurology. 2021 Mar 2;96(9):e1369-e1382
pubmed: 33495376
Cerebellum Ataxias. 2020 May 28;7:6
pubmed: 32514364
Int Arch Otorhinolaryngol. 2017 Jan;21(1):79-85
pubmed: 28050212
Lancet Neurol. 2010 Jan;9(1):94-104
pubmed: 20083040
Brain. 2022 Jun 30;145(6):2121-2132
pubmed: 34927205
Brain. 2020 Feb 1;143(2):480-490
pubmed: 32040566
Neurology. 2016 Nov 1;87(18):1892-1898
pubmed: 27683845
Brain. 2023 Oct 3;146(10):4144-4157
pubmed: 37165652
Neurology. 2020 Nov 24;95(21):e2912-e2923
pubmed: 32873692
Neurol Clin Pract. 2016 Feb;6(1):61-68
pubmed: 26918204
Arch Neurol. 1998 Oct;55(10):1353-7
pubmed: 9779665
J Neurol. 1999 Sep;246(9):789-97
pubmed: 10525976
Neurol Genet. 2022 Aug 29;8(5):e200016
pubmed: 36046423
N Engl J Med. 2023 Jan 12;388(2):128-141
pubmed: 36516086
Am J Hum Genet. 2023 Jun 1;110(6):1018
pubmed: 37267898
Brain. 2022 Apr 29;145(3):e6-e9
pubmed: 35230382

Auteurs

David Pellerin (D)

Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology and The National Hospital for Neurology and Neurosurgery, University College London, London, UK matthis.synofzik@uni-tuebingen.de david.pellerin.21@ucl.ac.uk.
Department of Neurology and Neurosurgery, Montreal Neurological Hospital and Institute, McGill University, Montreal, QC, Canada.

Carlo Wilke (C)

Research Division Translational Genomics of Neurodegenerative Diseases, Hertie-Institute for Clinical Brain Research and Center of Neurology, University of Tübingen, Tübingen, Germany.
German Center for Neurodegenerative Diseases (DZNE), Tübingen, Germany.

Andreas Traschütz (A)

Research Division Translational Genomics of Neurodegenerative Diseases, Hertie-Institute for Clinical Brain Research and Center of Neurology, University of Tübingen, Tübingen, Germany.
German Center for Neurodegenerative Diseases (DZNE), Tübingen, Germany.

Sara Nagy (S)

Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology and The National Hospital for Neurology and Neurosurgery, University College London, London, UK.
Department of Neurology, University Hospital Basel, University of Basel, Basel, Switzerland.

Riccardo Currò (R)

Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology and The National Hospital for Neurology and Neurosurgery, University College London, London, UK.
Department of Brain and Behavioral Sciences, University of Pavia, Pavia, Italy.

Marie-Josée Dicaire (MJ)

Department of Neurology and Neurosurgery, Montreal Neurological Hospital and Institute, McGill University, Montreal, QC, Canada.

Hector Garcia-Moreno (H)

Ataxia Centre, UCL Queen Square Institute of Neurology, University College London, London, UK.
National Hospital for Neurology and Neurosurgery, University College London Hospitals NHS Foundation Trust, London, UK.

Mathieu Anheim (M)

Service de Neurologie, Hôpitaux Universitaires de Strasbourg, Hôpital de Hautepierre, Strasbourg, France.
Fédération de Médecine Translationnelle de Strasbourg (FMTS), Université de Strasbourg, Strasbourg, France.

Thomas Wirth (T)

Service de Neurologie, Hôpitaux Universitaires de Strasbourg, Hôpital de Hautepierre, Strasbourg, France.
Fédération de Médecine Translationnelle de Strasbourg (FMTS), Université de Strasbourg, Strasbourg, France.

Jennifer Faber (J)

Department of Neurology, University Hospital Bonn, Bonn, Germany.
German Center for Neurodegenerative Diseases (DZNE), Bonn, Germany.

Dagmar Timmann (D)

Department of Neurology and Center for Translational Neuro- and Behavioral Sciences (C-TNBS), Essen University Hospital, University of Duisburg-Essen, Essen, Germany.

Christel Depienne (C)

Institute of Human Genetics, Essen University Hospital, University of Duisburg-Essen, Essen, Germany.

Dan Rujescu (D)

Department of Psychiatry and Psychotherapy, Comprehensive Center for Clinical Neurosciences and Mental Health, Medical University of Vienna, Vienna, Austria.

José Gazulla (J)

Department of Neurology, Hospital Universitario Miguel Servet, Zaragoza, Spain.

Mary M Reilly (MM)

Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology and The National Hospital for Neurology and Neurosurgery, University College London, London, UK.

Paola Giunti (P)

Ataxia Centre, UCL Queen Square Institute of Neurology, University College London, London, UK.
National Hospital for Neurology and Neurosurgery, University College London Hospitals NHS Foundation Trust, London, UK.

Bernard Brais (B)

Department of Neurology and Neurosurgery, Montreal Neurological Hospital and Institute, McGill University, Montreal, QC, Canada.
Department of Human Genetics, McGill University, Montreal, QC, Canada.
Centre de Réadaptation Lucie-Bruneau, Montreal, QC, Canada.

Henry Houlden (H)

Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology and The National Hospital for Neurology and Neurosurgery, University College London, London, UK.

Ludger Schöls (L)

German Center for Neurodegenerative Diseases (DZNE), Tübingen, Germany.
Department of Neurodegenerative Diseases, Hertie-Institute for Clinical Brain Research and Center of Neurology, University of Tübingen, Tübingen, Germany.

Michael Strupp (M)

Department of Neurology and German Center for Vertigo and Balance Disorders, LMU University Hospital, LMU Munich, Munich, Germany.

Andrea Cortese (A)

Department of Neuromuscular Diseases, UCL Queen Square Institute of Neurology and The National Hospital for Neurology and Neurosurgery, University College London, London, UK.
Department of Brain and Behavioral Sciences, University of Pavia, Pavia, Italy.

Matthis Synofzik (M)

Research Division Translational Genomics of Neurodegenerative Diseases, Hertie-Institute for Clinical Brain Research and Center of Neurology, University of Tübingen, Tübingen, Germany matthis.synofzik@uni-tuebingen.de david.pellerin.21@ucl.ac.uk.
German Center for Neurodegenerative Diseases (DZNE), Tübingen, Germany.

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Classifications MeSH