Case report: Novel frameshift mutation in

case report congenital muscular dystrophy type 1A exome sequencing laminin subunit alpha 2 LAMA2 mutation rare diseases sequence analysis

Journal

Frontiers in genetics
ISSN: 1664-8021
Titre abrégé: Front Genet
Pays: Switzerland
ID NLM: 101560621

Informations de publication

Date de publication:
2023
Historique:
received: 03 02 2023
accepted: 06 06 2023
medline: 7 7 2023
pubmed: 7 7 2023
entrez: 7 7 2023
Statut: epublish

Résumé

Congenital muscular dystrophy type 1A (CMD1A) is a rare autosomal recessive disorder caused by mutations in the

Identifiants

pubmed: 37415604
doi: 10.3389/fgene.2023.1158350
pii: 1158350
pmc: PMC10319579
doi:

Types de publication

Case Reports

Langues

eng

Pagination

1158350

Informations de copyright

Copyright © 2023 Diaz-Lombana, Diaz-Ordoñez, Gutierrez-Medina and Pachajoa.

Déclaration de conflit d'intérêts

The authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.

Références

Acta Myol. 2019 Jun 01;38(1):21-24
pubmed: 31309178
Hum Mutat. 2018 Oct;39(10):1314-1337
pubmed: 30055037
Arch Dis Child. 1999 Jun;80(6):542-7
pubmed: 10332004
Neurology. 2001 Oct 9;57(7):1319-22
pubmed: 11591858
Bioinformatics. 2017 Jul 15;33(14):i389-i398
pubmed: 28882004
J Spine Surg. 2016 Sep;2(3):185-194
pubmed: 27757431
Ann Neurol. 2016 Jul;80(1):101-11
pubmed: 27159402
Neuromuscul Disord. 2019 May;29(5):376-380
pubmed: 31040037
Case Rep Genet. 2018 Jul 25;2018:3028145
pubmed: 30147969
Cell Adh Migr. 2013 Jan-Feb;7(1):111-21
pubmed: 23154401
Appl Clin Genet. 2019 Jul 03;12:113-130
pubmed: 31308722
Neuromuscul Disord. 2010 Apr;20(4):241-50
pubmed: 20207543
Iran Biomed J. 2018 Apr 30;22(6):408-14
pubmed: 29707938
Curr Top Membr. 2015;76:1-30
pubmed: 26610910
PLoS One. 2017 Feb 27;12(2):e0172648
pubmed: 28241031
Mol Cell Probes. 2014 Aug;28(4):118-22
pubmed: 24225367
Biomed Rep. 2017 Aug;7(2):193-196
pubmed: 28804634
Clin Genet. 2008 Dec;74(6):502-12
pubmed: 18700894

Auteurs

Natalia Diaz-Lombana (N)

Centro de Investigaciones en Anomalías Congénitas y Enfermedades Raras (CIACER), Universidad Icesi, Cali, Colombia.

Lorena Diaz-Ordoñez (L)

Centro de Investigaciones en Anomalías Congénitas y Enfermedades Raras (CIACER), Universidad Icesi, Cali, Colombia.
Departamento de Ciencias Básicas Médicas, Facultad de Salud, Universidad Icesi, Cali, Colombia.

Juan David Gutierrez-Medina (JD)

Centro de Investigaciones en Anomalías Congénitas y Enfermedades Raras (CIACER), Universidad Icesi, Cali, Colombia.
Centro de Investigaciones Clínicas, Fundación Valle del Lili, Cali, Colombia.

Harry Pachajoa (H)

Centro de Investigaciones en Anomalías Congénitas y Enfermedades Raras (CIACER), Universidad Icesi, Cali, Colombia.
Departamento de Ciencias Básicas Médicas, Facultad de Salud, Universidad Icesi, Cali, Colombia.
Genetic Division, Fundación Valle del Lili, Cali, Colombia.

Classifications MeSH