Growth patterns in patients with mucopolysaccharidosis VII.
Growth
Height
MPS VII
Weight, BMI
Journal
Molecular genetics and metabolism reports
ISSN: 2214-4269
Titre abrégé: Mol Genet Metab Rep
Pays: United States
ID NLM: 101624422
Informations de publication
Date de publication:
Sep 2023
Sep 2023
Historique:
received:
13
06
2023
accepted:
14
06
2023
medline:
7
7
2023
pubmed:
7
7
2023
entrez:
7
7
2023
Statut:
epublish
Résumé
This study assessed growth patterns in patients with mucopolysaccharidosis (MPS) VII before enzyme replacement therapy. Height, weight, and body mass index (BMI) measurements and Among 20 enrolled patients with MPS VII, height In patients with MPS VII, declines in height
Identifiants
pubmed: 37415957
doi: 10.1016/j.ymgmr.2023.100987
pii: S2214-4269(23)00033-2
pmc: PMC10320588
doi:
Banques de données
ClinicalTrials.gov
['NCT02230566', 'NCT02432144', 'NCT02418455']
Types de publication
Journal Article
Langues
eng
Pagination
100987Informations de copyright
© 2023 The Authors. Published by Elsevier Inc.
Déclaration de conflit d'intérêts
Adriana M. Montaño has received research support from 10.13039/100013220Ultragenyx Pharmaceutical Inc. Agnieszka Różdżyńska-Świątkowska declares no conflicts of interest. Agnieszka Jurecka, Antonio Nino Ramirez, Lin Zhang, and Deborah Marsden are employees of and own stock in Ultragenyx Pharmaceutical Inc. Raymond Y. Wang has received research support from Ultragenyx Pharmaceutical Inc. Paul Harmatz has received research and consulting support from Ultragenyx Pharmaceutical Inc.
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