Discovery and Characterization of PROTACs Targeting Tissue Transglutaminase (TG2).


Journal

Journal of medicinal chemistry
ISSN: 1520-4804
Titre abrégé: J Med Chem
Pays: United States
ID NLM: 9716531

Informations de publication

Date de publication:
27 07 2023
Historique:
medline: 28 7 2023
pubmed: 14 7 2023
entrez: 14 7 2023
Statut: ppublish

Résumé

Tissue transglutaminase (TG2) is a multifunctional enzyme involved in the cross-linking of extracellular matrix proteins, formation of complexes with fibronectin (FN) and integrins, and GTP hydrolysis. TG2 is activated in several pathological conditions, including cancer. We recently described a novel series of ligands that bind to TG2 and inhibit its interaction with FN. Because TG2 acts via multiple mechanisms, we set out to pursue a targeted protein degradation strategy to abolish TG2's myriad functions. Here, we report the synthesis and characterization of a series of VHL-based degraders that reduce TG2 in ovarian cancer cells in a proteasome-dependent manner. Degradation of TG2 resulted in significantly reduced cancer cell adhesion and migration

Identifiants

pubmed: 37449845
doi: 10.1021/acs.jmedchem.2c01859
pmc: PMC10388319
doi:

Substances chimiques

Protein Glutamine gamma Glutamyltransferase 2 EC 2.3.2.13
Transglutaminases EC 2.3.2.13
Proteolysis Targeting Chimera 0
GTP-Binding Proteins EC 3.6.1.-

Types de publication

Journal Article Research Support, U.S. Gov't, Non-P.H.S.

Langues

eng

Sous-ensembles de citation

IM

Pagination

9445-9465

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Auteurs

Andres Valdivia (A)

Department of Obstetrics and Gynecology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois 60611, United States.

Purav P Vagadia (PP)

Department of Chemistry, Northwestern University, Evanston, Illinois 60208, United States.

Guangxu Guo (G)

WuXi AppTec, Shanghai 200131, People's Republic of China.

Eilidh O'Brien (E)

Department of Obstetrics and Gynecology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois 60611, United States.

Daniela Matei (D)

Department of Obstetrics and Gynecology, Feinberg School of Medicine, Northwestern University, Chicago, Illinois 60611, United States.
Robert H. Lurie Comprehensive Cancer Center, Feinberg School of Medicine, Northwestern University, Chicago, Illinois 60611, United States.
Jesse Brown VA Medical Center, Chicago, Illinois 60612, United States.

Gary E Schiltz (GE)

Department of Chemistry, Northwestern University, Evanston, Illinois 60208, United States.
Robert H. Lurie Comprehensive Cancer Center, Feinberg School of Medicine, Northwestern University, Chicago, Illinois 60611, United States.
Department of Pharmacology, Northwestern University Feinberg School of Medicine, Chicago, Illinois 60611, United States.

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Classifications MeSH