Therapeutic potential of extracellular vesicles derived from cardiac progenitor cells in rodent models of chemotherapy-induced cardiomyopathy.

cardiac strain cardio-oncology cardiovascular progenitor chemotherapy-induced cardiomyopathy extracellular vesicles regenerative medicine

Journal

Frontiers in cardiovascular medicine
ISSN: 2297-055X
Titre abrégé: Front Cardiovasc Med
Pays: Switzerland
ID NLM: 101653388

Informations de publication

Date de publication:
2023
Historique:
received: 15 04 2023
accepted: 13 06 2023
medline: 24 7 2023
pubmed: 24 7 2023
entrez: 24 7 2023
Statut: epublish

Résumé

Current treatments of chemotherapy-induced cardiomyopathy (CCM) are of limited efficacy. We assessed whether repeated intravenous injections of human extracellular vesicles from cardiac progenitor cells (EV-CPC) could represent a new therapeutic option and whether EV manufacturing according to a Good Manufacturing Practices (GMP)-compatible process did not impair their bioactivity. Immuno-competent mice received intra-peritoneal injections (IP) of doxorubicin (DOX) (4 mg/kg each; cumulative dose: 12 mg/kg) and were then intravenously (IV) injected three times with EV-CPC (total dose: 30 billion). Cardiac function was assessed 9-11 weeks later by cardiac magnetic resonance imaging (CMR) using strain as the primary end point. Then, immuno-competent rats received 5 IP injections of DOX (3 mg/kg each; cumulative dose 15 mg/kg) followed by 3 equal IV injections of GMP-EV (total dose: 100 billion). Cardiac function was assessed by two dimensional-echocardiography. In the chronic mouse model of CCM, DOX + placebo-injected hearts incurred a significant decline in basal (global, epi- and endocardial) circumferential strain compared with sham DOX-untreated mice ( Intravenously-injected extracellular vesicles derived from CPC have cardio-protective effects which may make them an attractive user-friendly option for the treatment of CCM.

Sections du résumé

Background UNASSIGNED
Current treatments of chemotherapy-induced cardiomyopathy (CCM) are of limited efficacy. We assessed whether repeated intravenous injections of human extracellular vesicles from cardiac progenitor cells (EV-CPC) could represent a new therapeutic option and whether EV manufacturing according to a Good Manufacturing Practices (GMP)-compatible process did not impair their bioactivity.
Methods UNASSIGNED
Immuno-competent mice received intra-peritoneal injections (IP) of doxorubicin (DOX) (4 mg/kg each; cumulative dose: 12 mg/kg) and were then intravenously (IV) injected three times with EV-CPC (total dose: 30 billion). Cardiac function was assessed 9-11 weeks later by cardiac magnetic resonance imaging (CMR) using strain as the primary end point. Then, immuno-competent rats received 5 IP injections of DOX (3 mg/kg each; cumulative dose 15 mg/kg) followed by 3 equal IV injections of GMP-EV (total dose: 100 billion). Cardiac function was assessed by two dimensional-echocardiography.
Results UNASSIGNED
In the chronic mouse model of CCM, DOX + placebo-injected hearts incurred a significant decline in basal (global, epi- and endocardial) circumferential strain compared with sham DOX-untreated mice (
Conclusions UNASSIGNED
Intravenously-injected extracellular vesicles derived from CPC have cardio-protective effects which may make them an attractive user-friendly option for the treatment of CCM.

Identifiants

pubmed: 37485274
doi: 10.3389/fcvm.2023.1206279
pmc: PMC10360184
doi:

Types de publication

Journal Article

Langues

eng

Pagination

1206279

Informations de copyright

© 2023 Desgres, Lima Correa, Petrusca, Autret, Pezzana, Marigny, Guillas, Bellamy, Vilar, Perier, Dingli, Loew, Humbert, Larghero, Churlaud, Renault, Croisille, Hagège, Silvestre and Menasché.

Déclaration de conflit d'intérêts

NR is a full time employee of FUJIFILM Cellular Dynamics, Inc. PM is a member of the Strategic Advisory Board of FUJIFILM Cellular Dynamics, Inc. All other authors have reported that they have no relationships relevant to the contents of this paper to disclose. The remaining authors declare that the research was conducted in the absence of any commercial or financial relationships that could be construed as a potential conflict of interest.

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Auteurs

Manon Desgres (M)

Université Paris Cité, Inserm, PARCC, Paris, France.

Bruna Lima Correa (B)

Université Paris Cité, Inserm, PARCC, Paris, France.

Lorena Petrusca (L)

Université de Lyon, INSA, Université Claude Bernard Lyon 1, UJM-Saint-Etienne, CNRS UMR 5520, INSERM U1206, CREATIS, Saint-Etienne, France.

Gwennhael Autret (G)

Université Paris Cité, Inserm, PARCC, Paris, France.
Plateforme Imageries du Vivant, Université Paris Cité, UFR de médecine, Paris, France.

Chloé Pezzana (C)

Université Paris Cité, Inserm, PARCC, Paris, France.

Céline Marigny (C)

Université Paris Cité, Inserm, PARCC, Paris, France.

Chloé Guillas (C)

Université Paris Cité, Inserm, PARCC, Paris, France.

Valérie Bellamy (V)

Université Paris Cité, Inserm, PARCC, Paris, France.

José Vilar (J)

Université Paris Cité, Inserm, PARCC, Paris, France.

Marie-Cécile Perier (MC)

Université Paris Cité, Inserm, PARCC, Paris, France.

Florent Dingli (F)

Institut Curie, PSL Research University, Centre de Recherche, Curie CoreTech Mass Spectrometry Proteomics, Paris, France.

Damarys Loew (D)

Institut Curie, PSL Research University, Centre de Recherche, Curie CoreTech Mass Spectrometry Proteomics, Paris, France.

Camille Humbert (C)

MEARY Cell and Gene Therapy Center, AP-HP, Hôpital Saint-Louis, Paris, France.

Jérôme Larghero (J)

Université Paris Cité, AP-HP, Hôpital Saint-Louis, MEARY Cell and Gene Therapy Center, Hôpital Saint Louis, INSERM CIC-BT CBT501, Paris, France.

Guillaume Churlaud (G)

MEARY Cell and Gene Therapy Center, AP-HP, Hôpital Saint-Louis, Paris, France.

Nisa Renault (N)

FUJIFILM Cellular Dynamics, Inc., Madison, WI, United States.

Pierre Croisille (P)

Université de Lyon, INSA, Université Claude Bernard Lyon 1, UJM-Saint-Etienne, CNRS UMR 5520, INSERM U1206, CREATIS, Saint-Etienne, France.

Albert Hagège (A)

Université Paris Cité, Inserm, PARCC, Paris, France.
Department of Cardiology, AP-HP, Hôpital Européen Georges Pompidou, Paris, France.

Jean-Sébastien Silvestre (JS)

Université Paris Cité, Inserm, PARCC, Paris, France.

Philippe Menasché (P)

Université Paris Cité, Inserm, PARCC, Paris, France.
Department of Cardiovascular Surgery, AP-HP, Hôpital Européen Georges Pompidou, Paris, France.

Classifications MeSH